FDA-Approved Treatments
Drugs with orphan designation or indications for rare diseases — 970 total
Drug information is sourced from FDA labels and prescribing information. Always verify current prescribing information with your pharmacist or prescriber before starting, stopping, or changing any medication.
Nithiodote
sodium nitrite and sodium thiosulfate
Hope Pharmaceuticals
1 INDICATIONS AND USAGE NITHIODOTE is indicated for the treatment of acute cyanide poisoning that is judged to be serious or life-threatening. When th…
Lumryz
sodium oxybate
Flamel Ireland Limited dba Avadel Ireland
1 INDICATIONS AND USAGE LUMRYZ is indicated for the treatment of cataplexy or excessive daytime sleepiness (EDS) in patients 7 years of age and older …
Sodium Phenylacetate And Sodium Benzoate
SODIUM PHENYLACETATE AND SODIUM BENZOATE
Zydus Pharmaceuticals USA Inc.
1 INDICATIONS AND USAGE Sodium Phenylacetate and Sodium Benzoate Injection is a nitrogen binding agent indicated as adjunctive therapy for the treatme…
Sodium Phenylbutyrate
SODIUM PHENYLBUTYRATE
GLENMARK PHARMACEUTICALS INC., USA
INDICATIONS AND USAGE Sodium phenylbutyrate tablets are indicated as adjunctive therapy in the chronic management of patients with urea cycle disorder…
Relyvrio
sodium phenylbutyrate and taurursodiol
Amylyx Pharmaceuticals, Inc.
Treatment of amyotrophic lateral sclerosis (ALS) in adults…
Sodium Phenylbutyrate
SODIUM PHENYLBUTYRATE TABLETS, 500 MG
ENDO USA, Inc.
INDICATIONS AND USAGE Sodium Phenylbutyrate Tablets is indicated as adjunctive therapy in the chronic management of patients with urea cycle disorders…
SUPREP Bowel Prep Kit
sodium sulfate, potassium sulfate, and magnesium sulfate
Braintree Laboratories, Inc.
1 INDICATIONS & USAGE Sodium sulfate, potassium sulfate and magnesium sulfate oral solution is indicated for cleansing of the colon as a preparation f…
Pedmark
sodium thiosulfate
Fennec Pharmaceuticals, Inc.
1 INDICATIONS AND USAGE PEDMARK is indicated to reduce the risk of ototoxicity associated with cisplatin in pediatric patients 1 month of age and olde…
Sovaldi
sofosbuvir
Gilead Sciences, Inc.
1 INDICATIONS AND USAGE SOVALDI is a hepatitis C virus (HCV) nucleotide analog NS5B polymerase inhibitor indicated for the treatment of: Adult patient…
Epclusa
sofosbuvir and velpatasvir
Gilead Sciences, Inc.
1 INDICATIONS AND USAGE EPCLUSA is indicated for the treatment of adults and pediatric patients 3 years of age and older with chronic hepatitis C viru…
Sunosi
Solriamfetol
Axsome Malta, Ltd.
1 INDICATIONS AND USAGE SUNOSI is indicated to improve wakefulness in adult patients with excessive daytime sleepiness associated with narcolepsy or o…
Sogroya
somapacitan-beco
Novo Nordisk Pharmaceuticals
1 INDICATIONS AND USAGE SOGROYA is indicated for the treatment of pediatric patients aged 2.5 years and older with: • Growth failure due to inadequate…
Ngenla
somatrogon-ghla
Pfizer Ireland Pharmaceuticals
1 INDICATIONS AND USAGE NGENLA is indicated for the treatment of pediatric patients aged 3 years and older who have growth failure due to an inadequat…
Norditropin
SOMATROPIN
Novo Nordisk
1 INDICATIONS AND USAGE NORDITROPIN is a recombinant human growth hormone indicated for: • Pediatric : Treatment of pediatric patients with growth fai…
Zorbtive
Somatropin (r-DNA)
EMD Serono, Inc.
Treatment of short bowel syndrome in patients receiving specialized nutritional support…
Nutropin Depot
Somatropin (rDNA origin)
Genentech, Inc.
Long-term treatment of growth failure due to a lack of adequate endogenous growth hormone secetion for once- or twice-a-month administration.…
Serostim
Somatropin for injection
EMD Serono, Inc.
1 INDICATIONS AND USAGE SEROSTIM (somatropin) is indicated for the treatment of HIV patients with wasting or cachexia to increase lean body mass and b…
Nexavar
sorafenib
Bayer HealthCare Pharmaceuticals, Inc.
1 INDICATIONS AND USAGE NEXAVAR is a kinase inhibitor indicated for the treatment of • Unresectable hepatocellular carcinoma ( 1.1 ) • Advanced renal …
So-Aqueous
sotalol (IV)
AltaThera Pharmaceuticals LLC
For use as a substitute for oral sotalol in patients who are unable to take sotalol orally [oral sotalol is indicated for maintenance of normal sinus …
Betapace
Sotalol HCl
Berlex Laboratories, Inc.
1 INDICATIONS AND USAGE Betapace/Betapace AF is an antiarrhythmic indicated for: the treatment of life-threatening ventricular arrhythmias ( 1.1 ) the…
WINREVAIR
SOTATERCEPT-CSRK
Merck Sharp & Dohme LLC
1 INDICATIONS AND USAGE WINREVAIR™ is indicated for the treatment of adults with pulmonary arterial hypertension (PAH, Group 1 pulmonary hypertension)…
Lumakras
sotorasib
Amgen Inc.
1 INDICATIONS AND USAGE LUMAKRAS is an inhibitor of the RAS GTPase family indicated for: KRAS G12C-mutated Locally Advanced or Metastatic Non-Small Ce…
Filspari
sparsentan
Travere Therapeutics
1 INDICATIONS AND USAGE FILSPARI is indicated to slow kidney function decline in adults with primary immunoglobulin A nephropathy (IgAN) who are at ri…
Spevigo
spesolimab-sbzo
Boehringer Ingelheim Pharmaceuticals, Inc. (BI)
1 INDICATIONS AND USAGE SPEVIGO is indicated for the treatment of generalized pustular psoriasis (GPP) in adults and pediatric patients 12 years of ag…
Steritalc
Sterile talc
Novatech SA
1.INDICATIONS AND USAGE 1.INDICATIONS AND USAGE 1.1 Malignant Pleural Effusion STERITALC is indicated to decrease the recurrence of malignant pleural …
Sclerosol Intrapleural Aerosol
Sterile talc powder
Sciarra Laboratories, Inc.
Prevention of recurrence of malignant pleural effusions in symptomatic patients.…
Diacomit
stiripentol
Biocodex
Treatment of seizures associated with Dravet syndrome (DS) in patients taking clobazam who are 6 months of age and older and weighing 7 kg or more |||…