Advocacy Hub

Built for patient advocacy organizations. Stop manually compiling disease intelligence — live FDA tracking, financial assistance programs, clinical trials, and specialist networks aggregated for every rare disease, updated daily.

Featured diseases

Pulmonary arterial hypertension

7 foundations · 26 programs

Duchenne muscular dystrophy

7 foundations · 32 programs

Sickle cell disease

7 foundations · 27 programs

Cystic fibrosis

7 foundations · 21 programs

Gaucher disease

7 foundations · 26 programs

Spinal Muscular Atrophy

7 foundations · 24 programs

Fabry disease

7 foundations · 17 programs

Hereditary angioedema

6 foundations · 22 programs

Phenylketonuria

6 foundations · 9 programs

Amyotrophic lateral sclerosis

6 foundations · 34 programs

Alpha-1-antitrypsin deficiency

5 foundations · 6 programs

Huntington disease

4 foundations · 6 programs

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