Thoracic malformation

Last reviewed

🖨 Print for my doctorAdvocacy Hub →
ORPHA:182108
Who is this for?
Show terms as
13Active trials50Specialists8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
Report missing data

Overview

Thoracic malformation is a broad term used to describe a group of rare birth defects that affect the shape and structure of the chest (thorax). This includes abnormalities of the ribs, sternum (breastbone), spine in the chest area, and the overall chest wall. These malformations can range from mild cosmetic differences to severe structural problems that affect how the lungs and heart work. Common examples include pectus excavatum (sunken chest), pectus carinatum (pigeon chest), and more complex rib or sternal abnormalities. Some thoracic malformations occur on their own, while others are part of broader genetic syndromes. Symptoms depend on the type and severity of the malformation. Mild cases may only cause a visible difference in chest shape, while more severe cases can lead to breathing difficulties, reduced exercise tolerance, and heart problems due to compression of organs inside the chest. In newborns, severe thoracic malformations can cause life-threatening breathing problems that require immediate medical attention. Treatment varies widely depending on the specific type and severity. Mild cases may only need monitoring, while moderate to severe cases may require surgery to reshape the chest wall, bracing, or other supportive treatments such as respiratory therapy. In some cases, multiple surgeries over time may be needed as the child grows. Early diagnosis and a team-based approach involving several specialists are important for the best outcomes.

Key symptoms:

Abnormal chest shapeSunken or protruding breastboneBreathing difficultiesShortness of breath during exerciseReduced stamina or exercise intoleranceAsymmetric chest wallMissing or extra ribsChest pain or discomfortFrequent respiratory infectionsPoor weight gain in infantsRapid breathing in newbornsVisible rib abnormalitiesCurved spine in the chest areaHeart palpitations or irregular heartbeat

Inheritance

Variable

Can be inherited in different ways depending on the underlying gene

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗NORD ↗

FDA & Trial Timeline

10 events
Dec 2025Effectiveness of Cardiopulmonary Exercises for Children With Pectus Excavatum

Ankara Etlik City Hospital — NA

TrialRECRUITING
Jul 2025Synergic Effects of Schroth Method With and Without Core Stabilization Exercises in Idiopathic Scoliosis Patients

University of Lahore — NA

TrialRECRUITING
Jun 2025Percutaneous Intercostal Cryoneuromodulation Onset Timing.

Papa Giovanni XXIII Hospital

TrialRECRUITING
Apr 2025Effectiveness of One-Minute Versus Two-Minute Cryoanalgesia in Nuss Surgery

Children's Memorial Health Institute, Poland — NA

TrialRECRUITING
Mar 2025Sagittal Spine Balance in Patients With Chest Wall Deformity

Pomeranian Medical University Szczecin

TrialACTIVE NOT RECRUITING
Feb 2025Evaluating the Clinical Effectiveness of "Endotracheal Tube Position Anomaly Alerting System"

Kaohsiung Medical University Chung-Ho Memorial Hospital — NA

TrialNOT YET RECRUITING
Jan 2025Artificial Intelligence-assisted Diagnosis

China National Center for Cardiovascular Diseases

TrialACTIVE NOT RECRUITING
Dec 2024Comparative Analysis Of Modified Vs. Classical Nuss Technique In The Surgical Correction Of Pectus Excavatum "

University Hospital, Strasbourg, France

TrialRECRUITING
Nov 2024Intraoperative Cryoanalgesia Versus Thoracic Epidural Block in MIRPE (Minimally Invasive Repair of Pectus Excavatum)

University of Sao Paulo — NA

TrialRECRUITING
Oct 2024Investigation of the Effectiveness of Telerehabilitation Training in Pectus Excavatum Deformity

Eastern Mediterranean University — NA

TrialNOT YET RECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

No FDA-approved treatments are currently listed for Thoracic malformation.

13 clinical trialsare actively recruiting — trials can provide access to cutting-edge therapies.

View clinical trials →

Clinical Trials

13 recruitingView all trials with filters →
N/A7 trials
Intraoperative Cryoanalgesia Versus Thoracic Epidural Block in MIRPE (Minimally Invasive Repair of Pectus Excavatum)
N/A
Actively Recruiting
· Sites: São Paulo, São Paulo · Age: 1399 yrs
ES Catheter vs Cryoablation After Pectus Surgery
N/A
Actively Recruiting
PI: Charlotte Walter, MD (Children's Hospital Medical Center, Cincinnati) · Sites: Cincinnati, Ohio · Age: 1221 yrs
Physiological Assessments During Non Operative Treatment on the Chest Wall Deformities
N/A
Actively Recruiting
PI: Manuel LOPEZ, MD (CHU de SAINT-ETIENNE) · Sites: Saint-Etienne · Age: 1030 yrs
Effectiveness of One-Minute Versus Two-Minute Cryoanalgesia in Nuss Surgery
N/A
Actively Recruiting
· Sites: Warsaw, Wybierz Województwo · Age: 1218 yrs
Effectiveness of Cardiopulmonary Exercises for Children With Pectus Excavatum
N/A
Actively Recruiting
· Sites: Ankara, Yenimahalle · Age: 518 yrs
Pectus Excavatum Camouflage (IT)
N/A
Active
PI: Flavio Facchini, Dr (Unit of Paediatric Surgery and Burn Center - Meyer) · Sites: Florence, Italy · Age: 1499 yrs
Pectus Excavatum Camouflage
N/A
Active
PI: Michael Wagels, Dr (Department of Plastic & Reconstructive Surgery Pri) · Sites: Brisbane, Queensland · Age: 1854 yrs
Other6 trials
Sagittal Spine Balance in Patients With Chest Wall Deformity
Active
· Sites: Szczecin · Age: 1018 yrs
Percutaneous Intercostal Cryoneuromodulation Onset Timing.
Actively Recruiting
· Sites: Bergamo, BG · Age: 1240 yrs
Reconstructions of Chest Wall Defects: a Retrospective Study
Actively Recruiting
PI: Marco Pignatti, MD (IRCCS Azienda Ospedaliero-Universitaria di Bologna) · Sites: Bologna · Age: 1899 yrs
Serratus Anterior Plane Block and Transthoracic Plane Block in Pectus Surgery
Actively Recruiting
· Sites: Istanbul, İ̇stanbul · Age: 1599 yrs
Comparative Analysis Of Modified Vs. Classical Nuss Technique In The Surgical Correction Of Pectus Excavatum "
Actively Recruiting
· Sites: Strasbourg · Age: 1118 yrs
Field-test and Psychometric Validation of the Pectus Excavatum Evaluation Questionnaire in the Dutch Pectus Excavatum Population
Actively Recruiting
· Sites: Heerlen · Age: 1218 yrs

Specialists

Showing 25 of 50View all specialists →
YM
Yuan Shi, M.D
Specialist
PI on 2 active trials
SM
Surya Narayanasamy, MD
CINCINNATI, OH
Specialist
PI on 1 active trial
CM
Charlotte Walter, MD
Specialist
PI on 1 active trial
SM
Scott O Trerotola, MD
PHILADELPHIA, PA
Specialist
PI on 1 active trial
AP
Annamaria Colao, MD, PhD
Specialist
PI on 3 active trials
DM
Deborah P Merke, M.D.
BETHESDA, MD
Specialist
PI on 7 active trials
MM
Mary Norton, MD
Specialist
PI on 3 active trials
MM
Michael R DeBaun, MD, MPH
NASHVILLE, TN
Specialist
PI on 4 active trials
MM
Mary Ann McLaughlin, MD, MPH
Specialist
PI on 2 active trials
AP
Alshimaa Azab, PhD
Specialist
PI on 6 active trials
MS
Muhammad Shoaib Nabi, Professor of Thoracic Surgery
Specialist
PI on 2 active trials13 Thoracic malformation publications
MD
Mohammad Ali Tabibi, Dr
Specialist
PI on 3 active trials
BP
Bernard Maitre, MD, PhD
Specialist
PI on 1 active trial
MH
Margaret Hodson
BUFFALO, NY
Specialist
PI on 1 active trial4 Thoracic malformation publications
LM
Luisa Veronese, MD
Specialist
PI on 1 active trial1 Thoracic malformation publication
EM
Eva-Corina Caragounis, MD
Specialist
PI on 1 active trial
DM
DOMINIC S CAROLLO, MD
NEW ORLEANS, LA
Specialist
PI on 1 active trial
HP
Hans Granhed, MD PhD
Specialist
PI on 1 active trial
HA
Hatem A Emara, A.Prof
Specialist
PI on 1 active trial
BM
Babu Naidu, MBBS
Specialist
PI on 1 active trial
EB
Ezio Bonanomi
Specialist
PI on 1 active trial
NC
Nicole Chandler
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Thoracic malformation.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Thoracic malformationForum →

No community posts yet. Be the first to share your experience with Thoracic malformation.

Start the conversation →

Latest news about Thoracic malformation

Disease timeline:

New recruiting trial: Intraoperative Cryoanalgesia Versus Thoracic Epidural Block in MIRPE (Minimally Invasive Repair of Pectus Excavatum)

A new clinical trial is recruiting patients for Thoracic malformation

New recruiting trial: Effectiveness of Cardiopulmonary Exercises for Children With Pectus Excavatum

A new clinical trial is recruiting patients for Thoracic malformation

New recruiting trial: Reconstructions of Chest Wall Defects: a Retrospective Study

A new clinical trial is recruiting patients for Thoracic malformation

New recruiting trial: Clariance ErYs Registry

A new clinical trial is recruiting patients for Thoracic malformation

New recruiting trial: Field-test and Psychometric Validation of the Pectus Excavatum Evaluation Questionnaire in the Dutch Pectus Excavatum Population

A new clinical trial is recruiting patients for Thoracic malformation

New recruiting trial: Synergic Effects of Schroth Method With and Without Core Stabilization Exercises in Idiopathic Scoliosis Patients

A new clinical trial is recruiting patients for Thoracic malformation

New recruiting trial: Effectiveness of One-Minute Versus Two-Minute Cryoanalgesia in Nuss Surgery

A new clinical trial is recruiting patients for Thoracic malformation

New recruiting trial: Effects of AD on VI in Patients With CF

A new clinical trial is recruiting patients for Thoracic malformation

New recruiting trial: Comparative Analysis Of Modified Vs. Classical Nuss Technique In The Surgical Correction Of Pectus Excavatum "

A new clinical trial is recruiting patients for Thoracic malformation

New recruiting trial: ES Catheter vs Cryoablation After Pectus Surgery

A new clinical trial is recruiting patients for Thoracic malformation

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What specific type of thoracic malformation does my child have, and how severe is it?,Is this malformation part of a genetic syndrome, and should we pursue genetic testing?,Will my child need surgery, and if so, when is the best time to do it?,How will this affect my child's breathing, heart function, and ability to exercise?,What non-surgical treatment options are available?,How often will my child need follow-up visits and imaging?,Are there any activity restrictions my child should follow?

Common questions about Thoracic malformation

What is Thoracic malformation?

Thoracic malformation is a broad term used to describe a group of rare birth defects that affect the shape and structure of the chest (thorax). This includes abnormalities of the ribs, sternum (breastbone), spine in the chest area, and the overall chest wall. These malformations can range from mild cosmetic differences to severe structural problems that affect how the lungs and heart work. Common examples include pectus excavatum (sunken chest), pectus carinatum (pigeon chest), and more complex rib or sternal abnormalities. Some thoracic malformations occur on their own, while others are part

At what age does Thoracic malformation typically begin?

Typical onset of Thoracic malformation is neonatal. Age of onset can vary across affected individuals.

Are there clinical trials for Thoracic malformation?

Yes — 13 recruiting clinical trials are currently listed for Thoracic malformation on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.

Which specialists treat Thoracic malformation?

25 specialists and care centers treating Thoracic malformation are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.