46,XX disorder of gonadal development

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ORPHA:325055
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17Specialists8Treatment centers

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UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

46,XX disorder of gonadal development, also known as 46,XX gonadal dysgenesis or XX female gonadal dysgenesis, is a rare condition in which a person has typical female chromosomes (46,XX) but their ovaries do not develop properly. Instead of normal, functioning ovaries, the gonads may be underdeveloped (streak gonads) or partially developed, meaning they cannot produce eggs or adequate amounts of female hormones like estrogen and progesterone. This condition falls under the broader category of disorders of sex development (DSD). The most common signs include delayed puberty, absent or irregular menstrual periods (primary amenorrhea), and infertility. Because the ovaries do not produce enough estrogen, affected individuals may also experience underdeveloped secondary sexual characteristics such as breast development and body hair. Some forms of this condition can be associated with other health issues depending on the underlying genetic cause, such as hearing loss (in Perrault syndrome) or adrenal problems. Treatment focuses on hormone replacement therapy (HRT) to induce puberty, maintain bone health, and support overall well-being. Estrogen and progesterone are typically prescribed to mimic the natural hormonal cycle. Fertility options are limited, but assisted reproductive technologies such as egg donation with in vitro fertilization (IVF) may be possible. Psychological support is also an important part of care, as the diagnosis can have emotional and social impacts. Early diagnosis and ongoing management by a team of specialists can greatly improve quality of life.

Key symptoms:

Delayed pubertyAbsent menstrual periods (primary amenorrhea)Underdeveloped breastsInfertilitySmall or streak ovariesLow estrogen levelsSparse body or pubic hairShort stature in some casesWeak or thin bones (osteoporosis) if untreatedPossible hearing loss (in certain genetic forms)Possible learning difficulties in some forms

Inheritance

Variable

Can be inherited in different ways depending on the underlying gene

Age of Onset

Juvenile

Begins in the teen years

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for 46,XX disorder of gonadal development.

View clinical trials →

No actively recruiting trials found for 46,XX disorder of gonadal development at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the 46,XX disorder of gonadal development community →

Specialists

17 foundView all specialists →
DM
Deborah P Merke, M.D.
BETHESDA, MD
Specialist
PI on 7 active trials
RM
Randal D Robinson, MD
Specialist
PI on 1 active trial
CM
Christine M Burt Solorzano, MD
Specialist
PI on 1 active trial
RM
Richard S. Legro, M.D.
HERSHEY, PA
Specialist
PI on 1 active trial
CM
Christine Burt Solorzano, MD
Specialist
PI on 3 active trials
MM
Manuel Luque-Ramírez, PhD, MD
Specialist
PI on 1 active trial
HM
Héctor F Escobar-Morreale, PhD, MD
Specialist
PI on 1 active trial
MM
Ming I Hsu, MD
LOS ANGELES, CA
Specialist
PI on 2 active trials
DP
David E Sandberg, PhD
Specialist
PI on 1 active trial
JP
John C. Marshall, MD, PhD
Specialist
PI on 1 active trial
MP
Melek Yildiz, Associate Professor
Specialist
PI on 1 active trial1 46,XX disorder of gonadal development publication
MP
Manuel Luque Ramírez, M.D., Ph.D.
Specialist
PI on 1 active trial
MM
Maya B Lodish, M.D.
BETHESDA, MD
Specialist
PI on 2 active trials
RM
R. Jeffrey Chang, MD
HOOVER, AL
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to 46,XX disorder of gonadal development.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about 46,XX disorder of gonadal development

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What is the specific genetic cause of my condition, and should my family members be tested?,When should hormone replacement therapy be started, and what can I expect?,How will this condition affect my bone health, and how often should I have bone density tests?,What are my options for having children in the future?,Are there any other health problems I should be screened for based on my specific diagnosis?,Can you refer me to a psychologist or counselor who has experience with disorders of sex development?,How long will I need to take hormone replacement therapy?

Common questions about 46,XX disorder of gonadal development

What is 46,XX disorder of gonadal development?

46,XX disorder of gonadal development, also known as 46,XX gonadal dysgenesis or XX female gonadal dysgenesis, is a rare condition in which a person has typical female chromosomes (46,XX) but their ovaries do not develop properly. Instead of normal, functioning ovaries, the gonads may be underdeveloped (streak gonads) or partially developed, meaning they cannot produce eggs or adequate amounts of female hormones like estrogen and progesterone. This condition falls under the broader category of disorders of sex development (DSD). The most common signs include delayed puberty, absent or irregul

At what age does 46,XX disorder of gonadal development typically begin?

Typical onset of 46,XX disorder of gonadal development is juvenile. Age of onset can vary across affected individuals.

Which specialists treat 46,XX disorder of gonadal development?

17 specialists and care centers treating 46,XX disorder of gonadal development are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.