Becker muscular dystrophy

Last reviewed

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ORPHA:98895OMIM:159050G71.0
Who is this for?
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8Active trials81Specialists8Treatment centers

Where are you in your journey?

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UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Also known as:

BMDBecker dystrophinopathy

Clinical phenotype terms— hover any for plain English:

MyoglobinuriaHP:0002913Abnormal urinary colorHP:0012086
Orphanet ↗OMIM ↗NORD ↗

FDA & Trial Timeline

10 events
Apr 2026Registry for Duchenne and Becker Muscular Dystrophy

Dr. Andreas Ziegler

TrialNOT YET RECRUITING
Mar 2026Romosozumab Effects on Bone Density, Muscle Mass, and Spine Surgery Outcomes

Nitin Agarwal — PHASE2

TrialNOT YET RECRUITING
Feb 2026Contribution of Bone to Urine Citrate

University of Texas Southwestern Medical Center

TrialENROLLING BY INVITATION
Feb 2026EFFECTS OF SUPERVISED PHYSICAL EXERCISE AFTER BARIATRIC SURGERY ON MUSCLE MASS AND BONE DENSITY (OBEFIT STUDY)

Hospitales Universitarios Virgen del Rocío — NA

TrialRECRUITING
Jan 2026Multiparametric Ultrafast Ultrasound Biomarkers for Duchenne and Becker Muscular Dystrophies

Nantes University Hospital

TrialNOT YET RECRUITING
Jan 2026Bone Health in Postmenopausal Women: The Effect of Exercise With or Without Medication for Osteoporosis

Loughborough University — NA

TrialNOT YET RECRUITING
Nov 2025The Effect of REgulation of PArathyroId hoRmone in Patients With Chronic Kidney Disease to Investigate the Change in Bone Mineral Density

Herlev Hospital — NA

TrialRECRUITING
Nov 2025Effect of Local Application of 1% Metformin Gel on Implant Stability and Peri-implant Bone Density: A Randomized Controlled Study

University of Baghdad — NA

TrialRECRUITING
Oct 2025Effectiveness of Whole Body Vibration on Health Outcomes in Older Adults With Dynapenic Abdominal Obesity

Dalin Tzu Chi General Hospital — NA

TrialNOT YET RECRUITING
Sep 2025Transition to Adulthood in People With Muscular Dystrophy

IRCCS Eugenio Medea — NA

TrialNOT YET RECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

No FDA-approved treatments are currently listed for Becker muscular dystrophy.

8 clinical trialsare actively recruiting — trials can provide access to cutting-edge therapies.

View clinical trials →

Clinical Trials

8 recruitingView all trials with filters →
Phase 23 trials
Vasodilator and Exercise Study for DMD (VASO-REx)
Phase 2
Actively Recruiting
PI: Tanja Taivassalo, Ph.D. (University of Florida, College of Medicine, Depart) · Sites: Gainesville, Florida · Age: 6–99 yrs
View on ClinicalTrials.gov ↗I'm interested →
Open-Label Extension of EDG-5506 in Participants With Becker Muscular Dystrophy
Phase 2
Enrolling by Invitation
PI: Joanne M. Donovan, MD, PhD (Edgewise Therapeutics, Inc.) · Sites: Little Rock, Arkansas; La Jolla, California +44 more
View on ClinicalTrials.gov ↗I'm interested →
Phase 2 Study of EDG-5506 in Becker Muscular Dystrophy (GRAND CANYON)
Phase 2
Active
PI: Joanne Donovan, MD, PhD (Edgewise Therapeutics, Inc.) · Sites: Little Rock, Arkansas; La Jolla, California +49 more · Age: 12–50 yrs
View on ClinicalTrials.gov ↗I'm interested →
Other5 trials
Characterization of Clinical Skeletal and Cardiac Impairment in Carriers of DMD and BMD
Active
PI: May Ling Mah, MD (PI) · Sites: Columbus, Ohio · Age: 18–99 yrs
View on ClinicalTrials.gov ↗I'm interested →
Biomarker Development for Muscular Dystrophies
Actively Recruiting
PI: Thurman M. Wheeler, MD (Massachusetts General Hospital) · Sites: Boston, Massachusetts; Boston, Massachusetts +3 more · Age: 5–99 yrs
View on ClinicalTrials.gov ↗I'm interested →
The Duchenne Registry
Actively Recruiting
· Sites: Washington D.C., District of Columbia
View on ClinicalTrials.gov ↗I'm interested →
Defining Endpoints in Becker Muscular Dystrophy
Active
PI: Nicholas E. Johnson, MD (Virginia Commonwealth University) · Sites: Orange, California; Aurora, Colorado +9 more · Age: 6–99 yrs
View on ClinicalTrials.gov ↗I'm interested →
Molecular Analysis of Patients With Neuromuscular Disease
Actively Recruiting
PI: Louis M Kunkel, PhD (Boston Children's Hospital/Harvard Medical School) · Sites: Boston, Massachusetts · Age: 0–100 yrs
View on ClinicalTrials.gov ↗I'm interested →

Specialists

Showing 25 of 81View all specialists →
TM
Tsuyoshi Matsumura
Specialist
3 Becker muscular dystrophy publications
KO
Katsuhisa Ogata
Specialist
2 Becker muscular dystrophy publications
YT
Yasuhiro Takeshima
Specialist
2 Becker muscular dystrophy publications
DV
Daniele Velardo
Specialist
4 Becker muscular dystrophy publications
TF
Tatsuya Fujii
Specialist
2 Becker muscular dystrophy publications
KK
Koichi Kimura
Specialist
2 Becker muscular dystrophy publications
TT
Toshiaki Takahashi
HONOLULU, HI
Specialist
2 Becker muscular dystrophy publications
KS
Kazuma Sugie
Specialist
2 Becker muscular dystrophy publications
HA
Hajime Arahata
Specialist
2 Becker muscular dystrophy publications
FM
Francesca Magri
Specialist
4 Becker muscular dystrophy publications
MK
Michio Kobayashi
Specialist
2 Becker muscular dystrophy publications
AN
Akinori Nakamura
Specialist
3 Becker muscular dystrophy publications
ET
Eri Takeshita
Specialist
2 Becker muscular dystrophy publications
MM
Madoka Mori-Yoshimura
Specialist
3 Becker muscular dystrophy publications
HA
Hiroyuki Awano
Specialist
2 Becker muscular dystrophy publications
GL
Global Clinical Leader
Specialist
PI on 44 active trials4 Becker muscular dystrophy publications
JM
Jerry R Mendell, MD
COLUMBUS, OH
Specialist
PI on 4 active trials
MP
Marika Pane
Bosisio Parini, Lc
Specialist

Rare Disease Specialist

PI on 2 active trials28 Becker muscular dystrophy publications
CM
Craig McDonald, MD
Phoenix, Arizona
Specialist

Rare Disease Specialist

PI on 4 active trials
TM
Thurman M. Wheeler, MD
ROCHESTER, NY
Specialist
PI on 3 active trials
LM
Laurent Servais, MD
Specialist
PI on 6 active trials1 Becker muscular dystrophy publication
EM
Elizabeth A Lawson, MD
Specialist
PI on 2 active trials
GM
Giuseppe Vita, MD
NORTH BRANFORD, CT
Specialist
PI on 1 active trial
RM
Ronald G Victor, MD
Specialist
PI on 5 active trials
SO
Satellos Chief Medical Officer
Los Angeles, California
Specialist

Rare Disease Specialist

PI on 1 active trial1 Becker muscular dystrophy publication

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center ↗

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center ↗

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program ↗

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site ↗

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site ↗

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site ↗

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine ↗

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program ↗

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Becker muscular dystrophy.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Becker muscular dystrophy

2 articles
NewsRSSApr 22, 2026
Exploring other mobility devices when a walker is no longer sufficient
A person with facioscapulohumeral muscular dystrophy (FSHD) is finding it harder to move around their home with a walker and is exploring other mobility options…
AdvocacyRSSApr 22, 2026
Collaboration aims to improve design of FSHD clinical trials
Three organizations that work with facioscapulohumeral muscular dystrophy (FSHD) patients are joining together to make clinical trials better. FSHD is a rare mu…
See all news about Becker muscular dystrophy →

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Common questions about Becker muscular dystrophy

Are there clinical trials for Becker muscular dystrophy?

Yes — 8 recruiting clinical trials are currently listed for Becker muscular dystrophy on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.

Which specialists treat Becker muscular dystrophy?

25 specialists and care centers treating Becker muscular dystrophy are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.