Overview
Duchenne and Becker Muscular Dystrophy is treated with 3 medications in our database, including Deflazacort, DEFLAZACORT, Vyondys 53, JAYTHARI Oral Suspension. 2 of these have manufacturer assistance programs available to help reduce out-of-pocket costs. Medications are manufactured by PTC Therapeutics, Sarepta, Amneal. Patients and caregivers can find copay cards, patient assistance programs, and travel grants for Duchenne and Becker Muscular Dystrophy treatment below.
Also known as:
X-linked recessive
Carried on the X chromosome; typically affects males more than females
Childhood
Begins in childhood, roughly ages 1 to 12
FDA & Trial Timeline
1 eventDUVYZAT: FDA approved
treatment of Duchenne muscular dystrophy (DMD) in patients 6 years of age and older
Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.
Treatments
4 availableDUVYZAT
treatment of Duchenne muscular dystrophy (DMD) in patients 6 years of age and older
Deflazacort, DEFLAZACORT
* Patient Copay Amount: Not Publicly Available * Maximum Annual Benefit Limit: Not Publicly Available * Core Eligibility Restrictions: Not Publicly Available * RxBIN, PCN, and Group numbers: Not Publi
Vyondys 53
* Patient Copay Amount: Not Publicly Available * Maximum Annual Benefit Limit: Not Publicly Available * Core Eligibility Restrictions: Not Publicly Available * RxBIN, PCN, and Group numbers: Not Publi
JAYTHARI Oral Suspension
• Patient Copay Amount: As little as $0 per prescription • Maximum Annual Benefit Limit: Not Publicly Available (Maximum value per prescription and annual fill limits apply but specific amounts are no
Clinical Trials
View all trials with filters →No actively recruiting trials found for Duchenne and Becker muscular dystrophy at this time.
New trials open frequently. Follow this disease to get notified.
Rare Disease Specialist
Rare Disease Specialist
Treatment Centers
8 centersBaylor College of Medicine Rare Disease Center ↗
Baylor College of Medicine
📍 Houston, TX
🏥 NORDStanford Medicine Rare Disease Center ↗
Stanford Medicine
📍 Stanford, CA
🔬 UDNNIH Clinical Center Undiagnosed Diseases Program ↗
National Institutes of Health
📍 Bethesda, MD
🔬 UDNUCLA UDN Clinical Site ↗
UCLA Health
📍 Los Angeles, CA
🔬 UDNBaylor College of Medicine UDN Clinical Site ↗
Baylor College of Medicine
📍 Houston, TX
🔬 UDNHarvard/MGH UDN Clinical Site ↗
Massachusetts General Hospital
📍 Boston, MA
🏥 NORDMayo Clinic Center for Individualized Medicine ↗
Mayo Clinic
📍 Rochester, MN
👤 Mayo Clinic Center for Individualized Medicine
🏥 NORDUCLA Rare Disease Day Program ↗
UCLA Health
📍 Los Angeles, CA
Travel Grants
No travel grants are currently matched to Duchenne and Becker muscular dystrophy.
Community
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Start the conversation →Latest news about Duchenne and Becker muscular dystrophy
No recent news articles for Duchenne and Becker muscular dystrophy.
Follow this condition to be notified when news becomes available.
Caregiver Resources
NORD Caregiver Resources
Support, advocacy, and financial assistance for caregivers of rare disease patients.
Mental Health Support
Rare disease caregiving can be isolating. Connect with counseling and peer support.
Family & Caregiver Grants
Financial assistance programs specifically for caregivers of rare disease patients.
Social Security Disability
Learn how rare disease patients may qualify for SSDI/SSI benefits.
Common questions about Duchenne and Becker muscular dystrophy
What is Duchenne and Becker muscular dystrophy?
Duchenne and Becker Muscular Dystrophy is treated with 3 medications in our database, including Deflazacort, DEFLAZACORT, Vyondys 53, JAYTHARI Oral Suspension. 2 of these have manufacturer assistance programs available to help reduce out-of-pocket costs. Medications are manufactured by PTC Therapeutics, Sarepta, Amneal. Patients and caregivers can find copay cards, patient assistance programs, and travel grants for Duchenne and Becker Muscular Dystrophy treatment below.
How is Duchenne and Becker muscular dystrophy inherited?
Duchenne and Becker muscular dystrophy follows a x-linked recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.
At what age does Duchenne and Becker muscular dystrophy typically begin?
Typical onset of Duchenne and Becker muscular dystrophy is childhood. Age of onset can vary across affected individuals.
Which specialists treat Duchenne and Becker muscular dystrophy?
10 specialists and care centers treating Duchenne and Becker muscular dystrophy are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.
What treatment and support options exist for Duchenne and Becker muscular dystrophy?
3 FDA-approved treatments are currently tracked on UniteRare for Duchenne and Becker muscular dystrophy. See the treatments and support programs sections for copay assistance, eligibility, and contact details.