Rare anemia

Last reviewed

🖨 Print for my doctorAdvocacy Hub →
ORPHA:108997
Who is this for?
Show terms as
17Specialists8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
Report missing data

Overview

Orphanet ↗NORD ↗

FDA & Trial Timeline

2 events
Jan 2026Luspatercept in Patients Affected With Rare Inherited Anemias

EuroBloodNet Association — PHASE2

TrialNOT YET RECRUITING
Mar 2020Observational Study for Patients With Hemoglobinopathies and Rare Inherited Anemia and Covid 19

Società Italiana Talassemie ed Emoglobinopatie

TrialRECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

No FDA-approved treatments are currently listed for Rare anemia.

View clinical trials →

No actively recruiting trials found for Rare anemia at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Rare anemia community →

Specialists

17 foundView all specialists →
PP
Prof. Antonio Piga
Specialist
PI on 1 active trial
PG
Prof. Renzo Galanello
Specialist
PI on 1 active trial
DB
Dr. Yves Bertrand
Specialist
PI on 1 active trial
DF
Dr. Gianluca Forni
Specialist
PI on 1 active trial
TM
Tammuella Chrisentery-Singleton, MD
Phoenix, Arizona
Specialist

Rare Disease Specialist

PI on 2 active trials
MM
Michael Recht, MD, PhD, MBA
CLEVELAND, OH
Specialist
PI on 1 active trial
MP
María del Mar Mañú Pereira, PhD
Specialist
PI on 1 active trial
PM
Pablo Velasco Puyó, MD
Specialist
PI on 1 active trial
ND
Nathalie ALADJIDI, Dr
Specialist
PI on 1 active trial
GF
Gian Luca Forni
Specialist
PI on 1 active trial16 Rare anemia publications
LM
Liza-Marie Johnson, MD, MPH, MSB
MEMPHIS, TN
Specialist
PI on 1 active trial
GC
Gary A Connor
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Rare anemia.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Rare anemiaForum →

No community posts yet. Be the first to share your experience with Rare anemia.

Start the conversation →

Latest news about Rare anemia

Disease timeline:

New recruiting trial: Observational Study for Patients With Hemoglobinopathies and Rare Inherited Anemia and Covid 19

A new clinical trial is recruiting patients for Rare anemia

New recruiting trial: Gene Therapy Communication: Use of a Needs Assessment to Drive Decision-AIDS for Gene Therapy for Rare Diseases (GENETX)

A new clinical trial is recruiting patients for Rare anemia

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Common questions about Rare anemia

Which specialists treat Rare anemia?

17 specialists and care centers treating Rare anemia are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.