Rare hematologic disease

Last reviewed

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ORPHA:97992
Who is this for?
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1FDA treatments24Specialists8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Orphanet ↗NORD ↗

Treatments

1 available

Omisirge

OMIDUBICEL-ONLV· Gamida Cell Inc.■ Boxed Warning
indicated for the treatment of adults and pediatric patients 12 years and older with hematologic malignancies who are planned for umbilical cord blood transplantation following myeloablative condition

indicated for the treatment of adults and pediatric patients 12 years and older with hematologic malignancies who are planned for umbilical cord blood transplantation following myeloablative conditioning to reduce the time to neutrophil recovery and the incidence of infections

No actively recruiting trials found for Rare hematologic disease at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Rare hematologic disease community →

Specialists

24 foundView all specialists →
FW
Fernando Worner
Specialist
1 Rare hematologic disease publication
EP
Eva Pueo
Specialist
1 Rare hematologic disease publication
IB
Ignacio Barriuso
Specialist
1 Rare hematologic disease publication
DV
Dolors Viles
Specialist
1 Rare hematologic disease publication
DF
Diego Fernández-Rodríguez
Specialist
1 Rare hematologic disease publication
MG
María Isabel Gil
Specialist
1 Rare hematologic disease publication
MP
Marcelo Serra, PhD
Buenos Aires, Buenos Aires
Specialist

Rare Disease Specialist

PI on 1 active trial
MP
Maria Lourdes Posadas Martinez, PhD
Specialist
PI on 1 active trial
TM
Tammuella Chrisentery-Singleton, MD
Phoenix, Arizona
Specialist

Rare Disease Specialist

PI on 2 active trials
MM
Michael Recht, MD, PhD, MBA
CLEVELAND, OH
Specialist
PI on 1 active trial
AT
Amanda M Termuhlen
MINNEAPOLIS, MN
Specialist
PI on 1 active trial1 Rare hematologic disease publication
ND
Nathalie ALADJIDI, Dr
Specialist
PI on 1 active trial
GF
Gian Luca Forni
Specialist
PI on 1 active trial16 Rare hematologic disease publications
DM
Dittus Christopher, DO, MPH
Specialist
PI on 1 active trial
DM
Diane J. Nugent, MD
MONMOUTH, ME
Specialist
PI on 1 active trial
BP
Bernard Maitre, MD, PhD
Specialist
PI on 1 active trial
MM
Michael Heinrich, MD
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Rare hematologic disease.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Rare hematologic diseaseForum →

No community posts yet. Be the first to share your experience with Rare hematologic disease.

Start the conversation →

Latest news about Rare hematologic disease

No recent news articles for Rare hematologic disease.

Follow this condition to be notified when news becomes available.

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Common questions about Rare hematologic disease

Which specialists treat Rare hematologic disease?

24 specialists and care centers treating Rare hematologic disease are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.

What treatment and support options exist for Rare hematologic disease?

1 patient support program are currently tracked on UniteRare for Rare hematologic disease. See the treatments and support programs sections for copay assistance, eligibility, and contact details.