Plasma cell leukemia

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9Active trials53Specialists8Treatment centers

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UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Plasma cell leukemia (PCL) is a rare and aggressive blood cancer in which abnormal plasma cells grow out of control and are found in large numbers in the blood. Plasma cells are a type of white blood cell that normally makes antibodies to help fight infections. In plasma cell leukemia, these cancerous plasma cells flood the bloodstream and can damage the bone marrow, bones, kidneys, and other organs. There are two types of plasma cell leukemia. Primary PCL occurs on its own without any prior blood cancer. Secondary PCL develops in people who already have multiple myeloma, a related but more common plasma cell cancer, when the disease transforms into a more aggressive form. Symptoms often include fatigue, bone pain, frequent infections, unexplained weight loss, bleeding problems, and kidney issues. Some patients also experience enlarged liver or spleen. Plasma cell leukemia is one of the most aggressive blood cancers. Treatment typically involves intensive chemotherapy, often using drug combinations similar to those used in multiple myeloma but given more urgently. Newer targeted therapies and immunotherapies are being studied. Stem cell transplantation may be considered for eligible patients. Despite advances in treatment, PCL remains very difficult to treat, and outcomes are generally poorer than for standard multiple myeloma. Early diagnosis and prompt, aggressive treatment are critical to improving survival.

Also known as:

Key symptoms:

Severe fatigue and weaknessBone pain, especially in the back and ribsFrequent or severe infectionsUnexplained weight lossEasy bruising or unusual bleedingKidney problems or decreased urine outputAnemia (low red blood cell count)Enlarged liver or spleenExcessive thirst and frequent urinationNumbness or tingling in hands and feetConfusion or mental fogginessShortness of breathHigh calcium levels causing nausea and constipation

Inheritance

Sporadic

Usually appears on its own, not inherited from a parent

Age of Onset

Adult

Begins in adulthood (age 18 or older)

Orphanet ↗NORD ↗

FDA & Trial Timeline

10 events
Feb 2026Scaffold-guided Breast Implant Revision Surgery

BellaSeno Pty Ltd — NA

TrialRECRUITING
Feb 2026LTFU of PCL Breast Scaffolds Used in 2021-BRV-004

BellaSeno Pty Ltd

TrialNOT YET RECRUITING
Oct 2025A Clinical Study of BT02 in Patients With Relapsed or Refractory Hematologic Malignancies

Biotroy Therapeutics — PHASE1, PHASE2

TrialNOT YET RECRUITING
May 2025Role of Antibiotic Therapy or Immunoglobulin On iNfections in hAematoLogy Immunoglobulin Stopping or Extension (Stop Ig)

Monash University — PHASE2, PHASE3

TrialRECRUITING
May 2025Clinical Trial on the Efficacy and Safety of Biodegradable 3D-Printed Implants in Chest Wall Reconstruction Surgery

Tang-Du Hospital — NA

TrialNOT YET RECRUITING
Apr 2025OrthoPureXT Multiligament PMCF Study

Tissue Regenix Ltd — NA

TrialRECRUITING
Mar 2025Safety and Effectiveness of ELLANSÉ®-S Dermal Filler in the Treatment of Nasolabial Folds

AQTIS Medical B.V. — NA

TrialRECRUITING
Dec 2024a Study of CT0596 in Relapsed/Refractory Multiple Myeloma and Relapsed/Refractory Plasma Cell Leukemia

Shanghai Changzheng Hospital — EARLY_PHASE1

TrialRECRUITING
Oct 2024Primary Cardiac Lymphoma: Italian Multicenter Experience

Fondazione Italiana Linfomi - ETS

TrialRECRUITING
Oct 2023Study to Evaluate the Safety and Efficacy of Daratumumab and Carfilzomib-based Induction/Consolidation/Maintenance Therapy in Transplant-eligible, Ultra High-risk, Newly Diagnosed Multiple Myeloma

Union Hospital, Tongji Medical College, Huazhong University of Science and Technology — PHASE2

TrialRECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

No FDA-approved treatments are currently listed for Plasma cell leukemia.

9 clinical trialsare actively recruiting — trials can provide access to cutting-edge therapies.

View clinical trials →

Clinical Trials

9 recruitingView all trials with filters →
Phase 22 trials
A Study of Bortezomib, Lenalidomide and Dexamethasone (VRd)-Based Regimen Followed by BCMA CAR-T Therapy in Transplant-Ineligible Patients With Primary Plasma Cell Leukemia
Phase 2
Actively Recruiting
· Sites: Tianjin · Age: 1875 yrs
Study to Evaluate the Safety and Efficacy of Daratumumab and Carfilzomib-based Induction/Consolidation/Maintenance Therapy in Transplant-eligible, Ultra High-risk, Newly Diagnosed Multiple Myeloma
Phase 2
Actively Recruiting
· Sites: Wuhan, Hubei · Age: 1870 yrs
Phase 13 trials
Kappa-CD28 T Lymphocytes, Chronic Lymphocytic Leukemia, B-cell Lymphoma or Multiple Myeloma, CHARKALL
Phase 1
Active
PI: Carlos Ramos, MD (Baylor College of Medicine - Texas Children's Hosp) · Sites: Houston, Texas; Houston, Texas · Age: 1899 yrs
A Study of CAR-GPRC5D in Patients With Relapsed/Refractory Multiple Myeloma or Plasma Cell Leukemia
Phase 1
Actively Recruiting
· Sites: Shanghai · Age: 1875 yrs
Study of CAR-T Cell Therapy in the Treatment of Relapsed/Refractory Hematological Malignancies
Phase 1
Actively Recruiting
PI: Ying Lu (The Affiliated People's Hospital of Ningbo Univers) · Sites: Ningbo, Zhejiang · Age: 1875 yrs

Specialists

Showing 25 of 53View all specialists →
ZM
Zachariah DeFilipp, MD
ATLANTA, GA
Specialist
PI on 5 active trials
YL
Ying Lu
Specialist
PI on 3 active trials409 Plasma cell leukemia publications
PM
Paolo Caimi, MD
CLEVELAND, OH
Specialist
PI on 5 active trials
TM
Thomas G. Martin, MD
Specialist
PI on 4 active trials
RM
Rahul Banerjee, MD
SEATTLE, WA
Specialist
PI on 2 active trials
PM
Paul Martin
Specialist
PI on 3 active trials73 Plasma cell leukemia publications
CP
Claudio G. Brunstein, MD, PhD
MINNEAPOLIS, MN
Specialist
PI on 6 active trials
DM
David Rizzieri, MD
CHARLOTTE, NC
Specialist
PI on 7 active trials
AK
Amrita Krishnan
DUARTE, CA
Specialist
PI on 2 active trials61 Plasma cell leukemia publications
RO
Robert Orlowski
HOUSTON, TX
Specialist
PI on 2 active trials
NM
Natalie Grover, MD
CHAPEL HILL, NC
Specialist
PI on 6 active trials
YN
Yago L Nieto
HOUSTON, TX
Specialist
PI on 4 active trials3 Plasma cell leukemia publications
TM
Trial Manager
Specialist
PI on 3 active trials2 Plasma cell leukemia publications
HM
Hayder Saeed, MD
TAMPA, FL
Specialist
PI on 2 active trials
JP
James L. Rubenstein, MD, PhD
Specialist
PI on 2 active trials
SK
Shaji Kumar
Anchorage, Alaska
Specialist

Rare Disease Specialist

PI on 7 active trials
MM
Margaret L. MacMillan, MD
Specialist
PI on 4 active trials
JM
Jennifer Amengual, MD
NEW YORK, NY
Specialist
PI on 2 active trials
YM
Yi-Bin A Chen, M.D.
BOSTON, MA
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Plasma cell leukemia.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Plasma cell leukemia

Disease timeline:

New recruiting trial: Primary Cardiac Lymphoma: Italian Multicenter Experience

A new clinical trial is recruiting patients for Plasma cell leukemia

New recruiting trial: To Evaluate the Safety and Efficacy of Human BCMA Targeted CAR-NK Cells Injection for Subjects With R/R MM or PCL

A new clinical trial is recruiting patients for Plasma cell leukemia

New recruiting trial: OrthoPureXT Multiligament PMCF Study

A new clinical trial is recruiting patients for Plasma cell leukemia

New recruiting trial: A Study of CAR-GPRC5D in Patients With Relapsed/Refractory Multiple Myeloma or Plasma Cell Leukemia

A new clinical trial is recruiting patients for Plasma cell leukemia

New recruiting trial: Scaffold-guided Breast Implant Revision Surgery

A new clinical trial is recruiting patients for Plasma cell leukemia

New recruiting trial: Safety and Effectiveness of ELLANSÉ®-S Dermal Filler in the Treatment of Nasolabial Folds

A new clinical trial is recruiting patients for Plasma cell leukemia

New recruiting trial: A Phase 1/2 Study of IDP-121 in Patients With Relapsed/Refractory Hematologic Malignancies

A new clinical trial is recruiting patients for Plasma cell leukemia

New recruiting trial: a Study of CT0596 in Relapsed/Refractory Multiple Myeloma and Relapsed/Refractory Plasma Cell Leukemia

A new clinical trial is recruiting patients for Plasma cell leukemia

New recruiting trial: Study of CAR-T Cell Therapy in the Treatment of Relapsed/Refractory Hematological Malignancies

A new clinical trial is recruiting patients for Plasma cell leukemia

New recruiting trial: Study to Evaluate the Safety and Efficacy of Daratumumab and Carfilzomib-based Induction/Consolidation/Maintenance Therapy in Transplant-eligible, Ultra High-risk, Newly Diagnosed Multiple Myeloma

A new clinical trial is recruiting patients for Plasma cell leukemia

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.Is my plasma cell leukemia primary or secondary, and how does that affect my treatment plan?,What genetic or chromosomal abnormalities were found in my cancer cells, and what do they mean for my prognosis?,Am I a candidate for stem cell transplantation, and if so, what type?,What are the specific chemotherapy drugs you recommend, and what side effects should I expect?,Are there any clinical trials available for plasma cell leukemia that I might be eligible for?,What newer therapies like CAR-T cell therapy or bispecific antibodies might be options for me?,What supportive care will I need for my bones, kidneys, and immune system during treatment?

Common questions about Plasma cell leukemia

What is Plasma cell leukemia?

Plasma cell leukemia (PCL) is a rare and aggressive blood cancer in which abnormal plasma cells grow out of control and are found in large numbers in the blood. Plasma cells are a type of white blood cell that normally makes antibodies to help fight infections. In plasma cell leukemia, these cancerous plasma cells flood the bloodstream and can damage the bone marrow, bones, kidneys, and other organs. There are two types of plasma cell leukemia. Primary PCL occurs on its own without any prior blood cancer. Secondary PCL develops in people who already have multiple myeloma, a related but more c

How is Plasma cell leukemia inherited?

Plasma cell leukemia follows a sporadic inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Plasma cell leukemia typically begin?

Typical onset of Plasma cell leukemia is adult. Age of onset can vary across affected individuals.

Are there clinical trials for Plasma cell leukemia?

Yes — 9 recruiting clinical trials are currently listed for Plasma cell leukemia on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.

Which specialists treat Plasma cell leukemia?

25 specialists and care centers treating Plasma cell leukemia are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.