Graft versus host disease

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ORPHA:39812OMIM:614395T86.0
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34Active trials107Specialists8Treatment centers1Financial resources

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UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Graft versus host disease (GvHD) is a serious medical condition that can happen after a stem cell transplant (also called a bone marrow transplant). In a stem cell transplant, a patient receives blood-forming cells from a donor. Sometimes, the donor's immune cells — called T-cells — see the patient's own body as foreign and attack it. This is what causes GvHD. It is sometimes called 'graft-versus-host reaction' or 'GVHD.' GvHD can affect many parts of the body, including the skin, gut, liver, lungs, eyes, and mouth. There are two main types: acute GvHD, which usually happens within the first few months after transplant, and chronic GvHD, which can develop later and may last for years. Symptoms can range from mild skin rashes to severe problems with the digestive system or lungs. Treatment usually starts with steroids like prednisone to calm the immune system. Several newer medications have been approved by the FDA, including ruxolitinib (Jakafi) for steroid-resistant acute GvHD and ibrutinib (Imbruvica) and belumosudil (Rezurock) for chronic GvHD. Managing GvHD often requires a team of specialists and ongoing monitoring. With the right treatment, many people can manage their symptoms and improve their quality of life.

Also known as:

Key symptoms:

Skin rash, redness, or blisteringYellowing of the skin or eyes (jaundice)Nausea, vomiting, or stomach crampsDiarrhea, sometimes severe or bloodyDry or irritated eyesDry mouth or mouth soresDifficulty swallowingShortness of breath or dry coughExtreme tiredness and fatigueJoint stiffness or tightening of the skinWeight lossMuscle weaknessFrequent infections due to a weakened immune systemHair loss or nail changes

Clinical phenotype terms (41)— hover any for plain English
StomatitisHP:0010280Maculopapular exanthemaHP:0040186Chronic hepatitisHP:0200123
Inheritance

Sporadic

Usually appears on its own, not inherited from a parent

Age of Onset

Variable

Can begin at different ages, from infancy through adulthood

Orphanet ↗OMIM ↗NORD ↗

FDA & Trial Timeline

10 events
Jun 2026Vitamin C With Steroids for Gastrointestinal GVHD

Baylor College of Medicine — EARLY_PHASE1

TrialNOT YET RECRUITING
May 2026Ex Vivo-Expanded Regulatory T Cells Plus Low-Dose Interleukin-2 for Steroid-Refractory Chronic GVHD

Leslie Kean — PHASE1

TrialNOT YET RECRUITING
Apr 2026Enteral Nutrition Versus Standard of Care in Allogeneic Hematopoietic Stem Cell Transplantation

University of Nebraska — PHASE2

TrialNOT YET RECRUITING
Nov 2025Electrostimulation Study for Ocular Graft vs. Host Disease

Zhonghui K. Luo, MD, PhD — NA

TrialRECRUITING
Oct 2025BPC2001 for the Prevention of Acute Graft-Versus-Host Disease Following Haploidentical Stem Cell Transplantation

BioPhoenix Co., Ltd. — PHASE2

TrialRECRUITING
Oct 2025HCMV-miRNA Monitoring After Allogeneic Hematopoietic Stem Cell Transplantation Using PSTM-qPCR

Ting YANG

TrialNOT YET RECRUITING
Sep 2025Ruxolitinib Plus Etanercept vs Ruxolitinib for Steroid-Refractory Severe Acute GVHD

First Affiliated Hospital of Zhejiang University — NA

TrialRECRUITING
Sep 2025A PHASE II PROSPECTIVE RANDOMIZED DOUBLE-MASKED CROSSOVER STUDY ASSESSING THE SAFETY & EFFICACY OF RHPRG4 (450 μG/ML RECOMBINANT HUMAN PROTEOGLYCAN 4) COMPARED TO VEHICLE FOR THE TREATMENT OF OCULAR GRAFT-VERSUS-HOST DISEASE (OGVHD)

Lubris Bio Pty Ltd — PHASE2

TrialRECRUITING
Sep 2025Clinical Observation on the Efficacy of Patient-Donor Derived Probiotics in Improving Intestinal Flora Disorder in Patients With Intestinal Acute Graft-Versus-Host Disease (aGVHD)

Institute of Hematology & Blood Diseases Hospital, China — NA

TrialNOT YET RECRUITING
Sep 2025Study of Efficacy and Safety of Ruxolitinib in Chinese Participants With Corticosteroid-refractory Chronic Graft vs. Host Disease

Novartis Pharmaceuticals — PHASE4

TrialRECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

No FDA-approved treatments are currently listed for Graft versus host disease.

20 clinical trialsare actively recruiting — trials can provide access to cutting-edge therapies.

View clinical trials →

Clinical Trials

20 recruitingView all trials with filters →
Phase 34 trials
A Study of Tacrolimus/Methotrexate/Ruxolitinib Versus Post-Transplant Cyclophosphamide/Tacrolimus/Mycophenolate Mofetil in Non-Myeloablative/Reduced Intensity Conditioning Allogeneic Peripheral Blood Stem Cell Transplantation (BMT CTN 2203)
Phase 3
Actively Recruiting
PI: Incyte Medical Monitor (Incyte Corporation) · Sites: Palo Alto, California; San Francisco, California +26 more · Age: 1899 yrs
Effect of Stem Cell Infusion Time on aGVHD in Patients With Hematological Malignancies Post UCBT
Phase 3
Actively Recruiting
PI: Xiaoyu Zhu, Ph.D (The First Affiliated Hospital of USTC) · Sites: Hefei, Anhui
Effect of Stem Cell Infusion Time on aGVHD in Patients With Hematological Malignancies
Phase 3
Active
PI: Xiaoyu Zhu, ph.D (The First Affiliated Hospital of USTC (Anhui Provi) · Sites: Hefei, Anhui; Beijing, Beijing Municipality +4 more · Age: 1260 yrs
MaaT013 As Salvage Therapy in Ruxolitinib Refractory GI-aGVHD Patients
Phase 3
Active
PI: Florent Malard, MD, PhD (APHP) · Sites: Innsbruck; Linz +48 more · Age: 1899 yrs
Phase 41 trial
Study of Efficacy and Safety of Ruxolitinib in Chinese Participants With Corticosteroid-refractory Chronic Graft vs. Host Disease
Phase 4
Actively Recruiting
PI: Novartis Pharmaceuticals (Novartis Pharmaceuticals) · Sites: Hefei, Anhui; Guangzhou, Guangdong +17 more · Age: 12100 yrs
Phase 27 trials
Acalabrutinib for the Treatment of Chronic Graft Versus Host Disease
Phase 2
Active
PI: Stephanie Lee, MD, MPH (Fred Hutch/University of Washington Cancer Consort) · Sites: Tampa, Florida; Buffalo, New York +4 more · Age: 1899 yrs
Optimizing GVHD Prophylaxis After Allogeneic Hematopoietic Cell Transplantation
Phase 2
Actively Recruiting
PI: Moataz Ellithi, MBChB (University of Nebraska) · Sites: Omaha, Nebraska · Age: 6099 yrs
Mesenchymal Stem Cell Infusion as Treatment for Steroid-Resistant Acute Graft Versus Host Disease (GVHD) or Poor Graft Function
Phase 2
Actively Recruiting
PI: Yves Beguin, MD, PhD (CHU-ULg) · Sites: Edegem, Antwerpen; Brussels, Brabant +10 more
Acute GVHD Suppression Using Costimulation Blockade to Expand Non-malignant Transplant
Phase 2
Active
PI: John Horan, MD (Emory University) · Sites: Birmingham, Alabama; Wilmington, Delaware +7 more · Age: 020 yrs
Pediatric GVHD Low Risk Steroid Taper Trial
Phase 2
Active
PI: John E Levine, MD, MS (Icahn School of Medicine at Mount Sinai) · Sites: Los Angeles, California; Washington D.C., District of Columbia +9 more · Age: 021 yrs
BPC2001 for the Prevention of Acute Graft-Versus-Host Disease Following Haploidentical Stem Cell Transplantation
Phase 2
Actively Recruiting
PI: Xiaodong Mo, PhD (Peking University People's Hospital) · Sites: Beijing, Beijing Municipality · Age: 1865 yrs
A PHASE II PROSPECTIVE RANDOMIZED DOUBLE-MASKED CROSSOVER STUDY ASSESSING THE SAFETY & EFFICACY OF RHPRG4 (450 μG/ML RECOMBINANT HUMAN PROTEOGLYCAN 4) COMPARED TO VEHICLE FOR THE TREATMENT OF OCULAR GRAFT-VERSUS-HOST DISEASE (OGVHD)
Phase 2
Actively Recruiting
· Sites: Sydney, New South Wales; Brisbane, Queensland +1 more · Age: 1875 yrs
Other8 trials
FMT in Gut aGVHD Treated
Actively Recruiting
PI: depei wu (first affiliated of Soochow university) · Sites: Suzhou, Jiangsu · Age: 1060 yrs
Chronic Graft-versus-Host Disease in the Oral Cavity of Patients Following Allogeneic Hematopoietic Stem Cell Transplant and Including Healthy Controls
Actively Recruiting
PI: Jacqueline W Mays, D.D.S. (National Institute of Dental and Craniofacial Rese) · Sites: Bethesda, Maryland · Age: 18100 yrs
Metabolome and Microbiome Impact on Acute GVHD in Recipients of Hematopoietic Transplant
Active
PI: Ildefonso Espigado, PhD (Seville University, Dep. of Medicine. Virgen del R) · Sites: Santander, Cantabria; Córdoba, Córdoba +7 more · Age: 1100 yrs
The Skin Microbiome in Graft Versus Host Disease
Active
PI: Simon Mueller, PD Dr. med (Department of Dermatology; University Hospital Bas) · Sites: Basel · Age: 1899 yrs
The Prevalence of Hypoesthesia Related Keratitis in Ocular Graft Vs. Host Disease (GVHD) Patients
Actively Recruiting
· Sites: Indianapolis, Indiana · Age: 1899 yrs
Relationship Between "FODMAPs" and "GVHD"
Actively Recruiting
PI: Depei Wu (SOOCHOW UNIV) · Sites: Suzhou, Jiangsu · Age: 1860 yrs
CXCL9 and EASIX for Prediction of Acute Graft Versus Host Disease
Actively Recruiting
· Sites: Detroit, Michigan · Age: 1880 yrs
Psychiatric Status and Symptom Severity in Graft-versus-Host Disease (GvHD).
Actively Recruiting
PI: Jan Puchowski, MD (Department of Hematology and Transplantology, Facu) · Sites: Gdansk, Pomeranian Voivodeship · Age: 1875 yrs

Specialists

Showing 25 of 107View all specialists →
PM
Pavan Reddy, MD
Specialist
PI on 2 active trials
MM
Mehdi Hamadani, MD
Specialist
PI on 4 active trials
DD
Daihong Liu, Doctor
Specialist
PI on 2 active trials1 Graft versus host disease publication
ZM
Zachariah DeFilipp, MD
ATLANTA, GA
Specialist
PI on 5 active trials
CM
Corey Cutler, MD, MPH
PARK CITY, UT
Specialist
PI on 3 active trials
PM
Philip Imus, MD
BALTIMORE, MD
Specialist
PI on 2 active trials
JM
John Horan, MD
Birmingham, Alabama
Specialist

Rare Disease Specialist

PI on 4 active trials
HM
Hannah Choe, MD
Specialist
PI on 3 active trials
LM
Leland Metheny, MD
CLEVELAND, OH
Specialist
PI on 6 active trials1 Graft versus host disease publication
AK
Anne Kuan
SAN ANTONIO, TX
Specialist
PI on 1 active trial
PM
Paul Martin
Specialist
PI on 3 active trials73 Graft versus host disease publications
DM
David Miklos
CHICAGO, IL
Specialist
PI on 2 active trials
CM
Christopher G Kanakry, M.D.
BALTIMORE, MD
Specialist
PI on 4 active trials
RM
Rachel J Bishop, M.D.
Specialist
PI on 2 active trials
AM
Andre Larochelle, M.D.
Bethesda, Maryland
Specialist

Rare Disease Specialist

PI on 2 active trials
EJ
Erlie Jiang
Specialist
PI on 3 active trials2 Graft versus host disease publications
EM
Everett Meyer
STANFORD, CA
Specialist
PI on 2 active trials15 Graft versus host disease publications
UM
Ulrike Blume-Peytavi, Prof. MD
Specialist
PI on 1 active trial
BM
Betty K Hamilton, MD
Specialist
PI on 1 active trial
CM
Corey Cutler, MD MPH
PARK CITY, UT
Specialist
PI on 1 active trial
NM
Natalia Maximova, MD
Specialist
PI on 2 active trials
DP
Dimitrios Tzachanis, MD PhD
LA JOLLA, CA
Specialist
PI on 1 active trial

Treatment Centers

8 centers
⚗️ Trial Site

Ann & Robert H. Lurie Children's Hospital of Chicago

📍 Chicago, Illinois

⚗️ Trial Site

Dana-Farber Cancer Institute

📍 Boston, Massachusetts

👤 Ann (Annie) W Silk

👤 Matthew Frigault, MD

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

Financial Resources

1 resources

Rezurock

Sanofi

Graft-versus-host disease

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Travel Grants

No travel grants are currently matched to Graft versus host disease.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Graft versus host disease

Disease timeline:

New recruiting trial: Electrostimulation Study for Ocular Graft vs. Host Disease

A new clinical trial is recruiting patients for Graft versus host disease

New recruiting trial: Leflunomide in Combination With Steroids for the Treatment of Acute Graft-versus-Host Disease After Donor Stem Cell Transplant for Hematologic Malignancies

A new clinical trial is recruiting patients for Graft versus host disease

New recruiting trial: Addition of Cord Blood Tissue-Derived Mesenchymal Stromal Cells to Ruxolitinib for the Treatment of Steroid-Refractory Acute Graft Versus Host Disease

A new clinical trial is recruiting patients for Graft versus host disease

New recruiting trial: Comparing the Therapeutic Effects of Using Ruxolitinib and Steroids Concurrently to Steroids Alone as Initial Treatment In Patients Diagnosed With Chronic Graft-versus-host Disease at a Grade of Moderate or Higher Severity

A new clinical trial is recruiting patients for Graft versus host disease

New recruiting trial: Effect of Stem Cell Infusion Time on aGVHD in Patients With Hematological Malignancies Post UCBT

A new clinical trial is recruiting patients for Graft versus host disease

New recruiting trial: Analysis of the Immunobiology of Acute Myeloid Leukemia Relapses After Allogeneic Hematopoietic Stem Cell Transplant (HSCT) for the Generation of Guidelines and Personalized Therapeutic Pathways

A new clinical trial is recruiting patients for Graft versus host disease

New recruiting trial: The Prevalence of Hypoesthesia Related Keratitis in Ocular Graft Vs. Host Disease (GVHD) Patients

A new clinical trial is recruiting patients for Graft versus host disease

New recruiting trial: Dose-Escalation Trial of Mesenchymal Stromal Cells in Patients With Medical Xerostomia

A new clinical trial is recruiting patients for Graft versus host disease

New recruiting trial: Chronic Graft-versus-Host Disease in the Oral Cavity of Patients Following Allogeneic Hematopoietic Stem Cell Transplant and Including Healthy Controls

A new clinical trial is recruiting patients for Graft versus host disease

New recruiting trial: Study of Efficacy and Safety of Ruxolitinib in Chinese Participants With Corticosteroid-refractory Chronic Graft vs. Host Disease

A new clinical trial is recruiting patients for Graft versus host disease

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What type and stage of GvHD do I have, and which organs are affected?,What treatment do you recommend, and what are the main side effects I should watch for?,What signs should prompt me to call you or go to the emergency room right away?,How long will I need to take immune-suppressing medications, and how will we know if they are working?,Are there clinical trials I might be eligible for if my GvHD does not respond to standard treatment?,What can I do to reduce my risk of serious infections while my immune system is suppressed?,How will GvHD affect my ability to return to work, school, or normal activities?

Common questions about Graft versus host disease

What is Graft versus host disease?

Graft versus host disease (GvHD) is a serious medical condition that can happen after a stem cell transplant (also called a bone marrow transplant). In a stem cell transplant, a patient receives blood-forming cells from a donor. Sometimes, the donor's immune cells — called T-cells — see the patient's own body as foreign and attack it. This is what causes GvHD. It is sometimes called 'graft-versus-host reaction' or 'GVHD.' GvHD can affect many parts of the body, including the skin, gut, liver, lungs, eyes, and mouth. There are two main types: acute GvHD, which usually happens within the first

How is Graft versus host disease inherited?

Graft versus host disease follows a sporadic inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

Are there clinical trials for Graft versus host disease?

Yes — 20 recruiting clinical trials are currently listed for Graft versus host disease on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.

Which specialists treat Graft versus host disease?

25 specialists and care centers treating Graft versus host disease are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.

What treatment and support options exist for Graft versus host disease?

1 patient support program are currently tracked on UniteRare for Graft versus host disease. See the treatments and support programs sections for copay assistance, eligibility, and contact details.