Acute graft versus host disease

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Who is this for?
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2FDA treatments1Active trials70Specialists8Treatment centers2Financial resources

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Orphanet ↗NORD ↗

FDA & Trial Timeline

10 events
Aug 2026Prognostic Value of Transcranial Doppler Ultrasound in the Clinical Evolution of Patients With Acute Ischemic Stroke. The TRADE-AIS Study

Jose Ivan Rodriguez de Molina Serrano — NA

TrialNOT YET RECRUITING
Jun 2026Testing the Addition of Venetoclax or Gemtuzumab Ozogamicin (GO) to Usual Treatment Regimen (Cytarabine and Daunorubicin, "7+3") for Core Binding Factor Acute Myeloid Leukemia (CBF-AML) to Improve Response (A MyeloMATCH Treatment Trial)

National Cancer Institute (NCI) — PHASE2

TrialNOT YET RECRUITING
Jun 2026Outcome of Clinical Phenotypes of Pediatric Myocarditis at Assiut University Children Hospital

Assiut University

TrialNOT YET RECRUITING
Apr 2026Buprenorphine for Analgesia in Older Adults With Acute Fractures in the Emergency Department: a Randomized Controlled Study

The Cooper Health System — PHASE1, PHASE2

TrialNOT YET RECRUITING
Mar 2026BREVOC Study: Exhaled VOCs for High-Risk Chest Pain in the ED

Qilu Hospital of Shandong University

TrialNOT YET RECRUITING
Mar 2026Acute Cardiovascular Effects of Transcutaneous Auricular Vagus Nerve Stimulation

Northumbria University — NA

TrialNOT YET RECRUITING
Mar 2026Vitamin D for Acute Intracerebral Hemorrhage

The University of Hong Kong — NA

TrialNOT YET RECRUITING
Feb 2026Bivalirudin Versus Heparin During PCI in High Bleeding Risk Patients With Acute Coronary Syndromes

Shenyang Northern Hospital — PHASE4

TrialNOT YET RECRUITING
Feb 2026Add-on Diuretics in Acute Decompensated Heart Failure

Tanta University — PHASE2

TrialRECRUITING
Jan 2026Comparing the Postoperative Analgesic Efficacy of Anterior Iliac Block and Ilioinguinal-iliohypogastric Block in Inguinal Hernia Surgery

Harran University — NA

TrialNOT YET RECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

2 available

JAKAFI

RUXOLITINIB· Incyte Corporation

treatment of steroid-refractory acute graft-versus-host disease in adult and pediatric patients 12 years and older

Ryoncil

remestemcel-L-rknd· Mesoblast, Inc.Orphan Drug

treatment of steroid refractory acute graft versus host disease (SR-aGvHD) in pediatric patients 2 months of age and older

Clinical Trials

1 recruitingView all trials with filters →
Phase 21 trial
Trial of Efficacy and Safety of MC0518 Versus Best Available Therapy in Participants With Steroid-Refractory Acute Graft Versus Host Disease
Phase 2
Active
· Sites: Bordeaux; La Tronche +34 more · Age: 017 yrs

Specialists

Showing 25 of 70View all specialists →
BW
Benjamin Watkins
Specialist
2 Acute graft versus host disease publications
EH
Ernst Holler
Specialist
2 Acute graft versus host disease publications
AR
Armin Rashidi
SEATTLE, WA
Specialist
2 Acute graft versus host disease publications
FL
Fei Li
Specialist
2 Acute graft versus host disease publications
YC
Yang Cao
Specialist
2 Acute graft versus host disease publications
XH
Xiaoxia Hu
LOS ANGELES, CA
Specialist
2 Acute graft versus host disease publications
FM
Florent Malard
Specialist
2 Acute graft versus host disease publications
CZ
Cong Zeng
Specialist
2 Acute graft versus host disease publications
MQ
Muna Qayed
ATLANTA, GA
Specialist
3 Acute graft versus host disease publications
MM
Mohamad Mohty
Specialist
2 Acute graft versus host disease publications
RZ
Robert Zeiser
Specialist
6 Acute graft versus host disease publications
LH
Liangding Hu
Specialist
2 Acute graft versus host disease publications
DL
Daihong Liu
Specialist
2 Acute graft versus host disease publications
GB
Gautam Borthakur
HOUSTON, TX
Specialist
PI on 3 active trials1 Acute graft versus host disease publication
TM
Tal Hasin, MD
ROCHESTER, MN
Specialist
PI on 2 active trials
SM
Seth E. Karol, MD
MEMPHIS, TN
Specialist
PI on 4 active trials
DM
Dan Douer, MD
NEW YORK, NY
Specialist
PI on 3 active trials
CM
Christopher G Kanakry, M.D.
BALTIMORE, MD
Specialist
PI on 4 active trials
EJ
Erlie Jiang
Specialist
PI on 3 active trials2 Acute graft versus host disease publications

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Financial Resources

2 resources
JAKAFI(RUXOLITINIB)Incyte Corporation

Orencia

Bristol-Myers Squibb Co.

Orencia Patient Support (BMS Access Support)

Patient Assistance
Manufacturer Program
Accepting applications

Travel Grants

No travel grants are currently matched to Acute graft versus host disease.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Acute graft versus host disease

Disease timeline:

New recruiting trial: Intracoronary Administration of OmniMSC-AMI for Acute ST-segment Elevation Myocardial Infarction Patients

A new clinical trial is recruiting patients for Acute graft versus host disease

New recruiting trial: Infusion of Alloreactive nk Cells for Mrd-positive Aml Patients

A new clinical trial is recruiting patients for Acute graft versus host disease

New recruiting trial: Facilitating Neuroplastic Changes of Acute Stroke Survivors

A new clinical trial is recruiting patients for Acute graft versus host disease

New recruiting trial: Early Detection of CTEPH in Patients After APE

A new clinical trial is recruiting patients for Acute graft versus host disease

New recruiting trial: Comprehensive Genomic Profiling and Next Generation Functional Drug Screening for Patients With Aggressive Haematological Malignancies

A new clinical trial is recruiting patients for Acute graft versus host disease

New recruiting trial: Articaine Plus Dexmedetomidine in Supraclavicular Block

A new clinical trial is recruiting patients for Acute graft versus host disease

New recruiting trial: Effect of Glp-1 and Antidiabetic sgLT2 Agents for myoCardial infarcTion and Ultrasensitive Inflammatory Surveillance (GALACTUS Trial)

A new clinical trial is recruiting patients for Acute graft versus host disease

New recruiting trial: A Study of BL-M11D1 in Patients With Relapsed/Refractory Acute Myeloid Leukemia

A new clinical trial is recruiting patients for Acute graft versus host disease

New recruiting trial: Standard Volume vs. High Volume Plasma Exchange in Pediatric Acute Liver Failure

A new clinical trial is recruiting patients for Acute graft versus host disease

New recruiting trial: Comparison of Medical RESCUE Strategies for Patients With Steroid-refractory Acute Severe Ulcerative Colitis

A new clinical trial is recruiting patients for Acute graft versus host disease

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Common questions about Acute graft versus host disease

Are there clinical trials for Acute graft versus host disease?

Yes — 1 recruiting clinical trial is currently listed for Acute graft versus host disease on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.

Which specialists treat Acute graft versus host disease?

25 specialists and care centers treating Acute graft versus host disease are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.

What treatment and support options exist for Acute graft versus host disease?

2 patient support programs are currently tracked on UniteRare for Acute graft versus host disease. See the treatments and support programs sections for copay assistance, eligibility, and contact details.