MT2018-18: Sleeping Beauty Transposon-Engineered Plasmablasts for Hurler Syndrome Post Allo HSCT

Key facts

Sponsor

Masonic Cancer Center, University of Minnesota

Principal Investigator

Paul Orchard, MD

University of Minnesota, Department of Pediatrics

Intervention

Autologous Plasmablasts(drug)

Eligibility

3-8 years · All sexes

Timeline

2022 – 2023

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

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See all trials for Mucopolysaccharidosis type 1 →