A Clinical Study Evaluating the Safety, Tolerability, and Initial Efficacy of JWK008 in Patients With Mucopolysaccharidosis Type I

Key facts

Sponsor

West China Hospital

Principal Investigator

Xingchen Peng, Ph.D

West China Hospital

Intervention

JWK008 Single intravenous infusion administration(genetic)

Enrollment

6 enrolled

Eligibility

18 years · All sexes

Timeline

2024 – 2029

Study locations (1)

• West China Hospital, Sichuan Universit, Chengdu, Sichuan, China

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

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