Active, not recruitingNCT05634512
Evaluation of Intravenous Laronidase Pharmacokinetics Before and After Hematopoietic Cell Transplantation in Patients With Mucopolysaccharidosis Type IH.
Studying Mucopolysaccharidosis type 1
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Masonic Cancer Center, University of Minnesota
- Principal Investigator
- Paul Orchard, MDUniversity of Minnesota Masonic Cancer Center
- Intervention
- Laronidase therapy and a stem cell transplant(drug)
- Enrollment
- 13 enrolled
- Eligibility
- 0-3 years · All sexes
- Timeline
- 2022 – 2026
Study locations (1)
- University of Minnesota Masonic Cancer Center, Minneapolis, Minnesota, United States
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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