Active, not recruitingPHASE1, PHASE2NCT06181136
Study of DNL126 in Pediatric Participants With Mucopolysaccharidosis Type IIIA (Sanfilippo Syndrome Type A)
Studying Mucopolysaccharidosis type 1
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Denali Therapeutics Inc.
- Principal Investigator
- Ana-Claire Meyer, MDDenali Therapeutics
- Intervention
- DNL126(drug)
- Enrollment
- 20 enrolled
- Eligibility
- 0-18 years · All sexes
- Timeline
- 2023 – 2028
Study locations (4)
- UCSF Benioff Children's Hospital Oakland, Oakland, California, United States
- University of Iowa Stead Family Children's Hospital, Iowa City, Iowa, United States
- University of North Carolina at Chapel Hill, Chapel Hill, North Carolina, United States
- Baylor College of Medicine and Texas Children's Hospital, Houston, Texas, United States
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT06181136 on ClinicalTrials.govOther trials for Mucopolysaccharidosis type 1
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