Phase I/II Study of JR-441 in Patients With Mucopolysaccharidosis Type IIIA

Key facts

Sponsor

JCR Pharmaceuticals Co., Ltd.

Intervention

JR-441(drug)

Enrollment

15 enrolled

Eligibility

1-18 years · All sexes

Timeline

2023 – 2029

Study locations (1)

• Universitätsklinikum Hamburg-Eppendorf, Hamburg, Germany

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

Other trials for Mucopolysaccharidosis type 1

Additional recruiting or active studies for the same condition.

• RECRUITINGPHASE1, PHASE2NCT06488924
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• ACTIVE NOT RECRUITINGPHASE1, PHASE2NCT06181136
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• ACTIVE NOT RECRUITINGPHASE1, PHASE2NCT04201405
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• ACTIVE NOT RECRUITINGPHASE2, PHASE3NCT03566043
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• ACTIVE NOT RECRUITINGPHASE1, PHASE2NCT03488394
  Gene Therapy With Modified Autologous Hematopoietic Stem Cells for the Treatment of Patients With Mucopolysaccharidosis Type I, Hurler Variant
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See all trials for Mucopolysaccharidosis type 1 →