Active, not recruitingPHASE2, PHASE3NCT03566043
CAMPSIITE™ RGX-121 Gene Therapy in Subjects With MPS II (Hunter Syndrome)
Studying Mucopolysaccharidosis type 1
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- REGENXBIO Inc.
- Intervention
- RGX-121(genetic)
- Enrollment
- 48 enrolled
- Eligibility
- 5 years · MALE
- Timeline
- 2018 – 2025
Study locations (5)
- University of California San Francisco, Benioff Children's Hospital, Oakland, California, United States
- St. Peter's University Hospital, New Brunswick, New Jersey, United States
- Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
- Children's Hospital of Pittsburgh - UPMC: Program for Neurodevelopment in Rare Disorders, Pittsburgh, Pennsylvania, United States
- Hospital de Clinicas de Porto Alegre, Porto Alegre, Rio Grande do Sul, Brazil
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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