Parental Coping With Challenging Behavior in Mucopolysaccharidosis Type I-III

Key facts

Sponsor

University Hospital Heidelberg

Principal Investigator

Markus Ries, MD PhD MHSc FCP

markus.ries@med.uni-heidelberg.de

Intervention

This is an observational study(other)

Enrollment

34 enrolled

Eligibility

18 years · All sexes

Timeline

2017 – 2017

Study locations (1)

• University of Heidelberg, Heidelberg, Germany

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

Other trials for Mucopolysaccharidosis type 1

Additional recruiting or active studies for the same condition.

• RECRUITINGPHASE1, PHASE2NCT06488924
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• RECRUITINGPHASE1NCT06519552
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• ACTIVE NOT RECRUITINGPHASE1, PHASE2NCT06181136
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• ACTIVE NOT RECRUITINGPHASE1, PHASE2NCT06095388
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• ACTIVE NOT RECRUITINGPHASE1, PHASE2NCT05665166
  Gene Therapy With Modified Autologous Hematopoietic Stem Cells for Patients With Mucopolysaccharidosis Type II
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• ACTIVE NOT RECRUITINGNCT05634512
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• ACTIVE NOT RECRUITINGPHASE1, PHASE2NCT04201405
  Gene Therapy with Modified Autologous Hematopoietic Stem Cells for Patients with Mucopolysaccharidosis Type IIIA
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• ACTIVE NOT RECRUITINGPHASE2, PHASE3NCT03566043
  CAMPSIITE™ RGX-121 Gene Therapy in Subjects With MPS II (Hunter Syndrome)
  REGENXBIO Inc.

See all trials for Mucopolysaccharidosis type 1 →