Laronidase (Aldurazyme TM) Enzyme Replacement Therapy With Hematopoietic Stem Cell Transplant for Hurler Syndrome

Key facts

Sponsor

Masonic Cancer Center, University of Minnesota

Principal Investigator

Paul Orchard, M.D., MD

Masonic Cancer Center, University of Minnesota

Intervention

Laronidase(drug)

Enrollment

20 enrolled

Eligibility

All sexes

Timeline

2012 – 2018

Study locations (1)

• Masonic Cancer Center, University of Minnesota, Minneapolis, Minnesota, United States

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

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