Overview
Systemic Mastocytosis is treated with 2 medications in our database, including Gastrocrom, Cromolyn Sodium Oral Solution (Concentrate). 2 of these have manufacturer assistance programs available to help reduce out-of-pocket costs. Medications are manufactured by Viatris Specialty LLC, Mylan. Patients and caregivers can find copay cards, patient assistance programs, and travel grants for Systemic Mastocytosis treatment below.
Sporadic
Usually appears on its own, not inherited from a parent
Adult
Begins in adulthood (age 18 or older)
FDA & Trial Timeline
1 eventCogent Biosciences, Inc. — PHASE2
Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.
Treatments
4 availableAyvakit
the treatment of adult patients with AdvSM. AdvSM includes patients with aggressive systemic mastocytosis (ASM), systemic mastocytosis with an associated hematological neoplasm (SM-AHN), and mast cell…
the treatment of adult patients with AdvSM. AdvSM includes patients with aggressive systemic mastocytosis (ASM), systemic mastocytosis with an associated hematological neoplasm (SM-AHN), and mast cell leukemia (MCL)
Cimetidine
The treatment of pathological hypersecretory conditions (i.e., Zollinger-Ellison Syndrome, systemic mastocytosis, multiple endocrine adenomas)
Gastrocrom
* Patient Copay Amount: Not Publicly Available * Maximum Annual Benefit Limit: Not Publicly Available * Core Eligibility Restrictions: Not Publicly Available * RxBIN, PCN, and Group numbers: Not Publi
Cromolyn Sodium Oral Solution (Concentrate)
Detailed copay and financial assistance information is not publicly available for this medication at this time. Please consult your pharmacist or the manufacturer's official patient support program fo
Rare Disease Specialist
Treatment Centers
8 centersBaylor College of Medicine Rare Disease Center ↗
Baylor College of Medicine
📍 Houston, TX
🏥 NORDStanford Medicine Rare Disease Center ↗
Stanford Medicine
📍 Stanford, CA
🔬 UDNNIH Clinical Center Undiagnosed Diseases Program ↗
National Institutes of Health
📍 Bethesda, MD
🔬 UDNUCLA UDN Clinical Site ↗
UCLA Health
📍 Los Angeles, CA
🔬 UDNBaylor College of Medicine UDN Clinical Site ↗
Baylor College of Medicine
📍 Houston, TX
🔬 UDNHarvard/MGH UDN Clinical Site ↗
Massachusetts General Hospital
📍 Boston, MA
🏥 NORDMayo Clinic Center for Individualized Medicine ↗
Mayo Clinic
📍 Rochester, MN
👤 Mayo Clinic Center for Individualized Medicine
🏥 NORDUCLA Rare Disease Day Program ↗
UCLA Health
📍 Los Angeles, CA
Financial Resources
2 resourcesHealthWell Foundation — Systemic mastocytosis
HealthWell Foundation
Systemic mastocytosis
Travel Grants
No travel grants are currently matched to Systemic mastocytosis.
Community
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Start the conversation →Latest news about Systemic mastocytosis
1 articlesCaregiver Resources
NORD Caregiver Resources
Support, advocacy, and financial assistance for caregivers of rare disease patients.
Mental Health Support
Rare disease caregiving can be isolating. Connect with counseling and peer support.
Family & Caregiver Grants
Financial assistance programs specifically for caregivers of rare disease patients.
Social Security Disability
Learn how rare disease patients may qualify for SSDI/SSI benefits.
Common questions about Systemic mastocytosis
What is Systemic mastocytosis?
Systemic Mastocytosis is treated with 2 medications in our database, including Gastrocrom, Cromolyn Sodium Oral Solution (Concentrate). 2 of these have manufacturer assistance programs available to help reduce out-of-pocket costs. Medications are manufactured by Viatris Specialty LLC, Mylan. Patients and caregivers can find copay cards, patient assistance programs, and travel grants for Systemic Mastocytosis treatment below.
How is Systemic mastocytosis inherited?
Systemic mastocytosis follows a sporadic inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.
At what age does Systemic mastocytosis typically begin?
Typical onset of Systemic mastocytosis is adult. Age of onset can vary across affected individuals.
Are there clinical trials for Systemic mastocytosis?
Yes — 1 recruiting clinical trial is currently listed for Systemic mastocytosis on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.
Which specialists treat Systemic mastocytosis?
24 specialists and care centers treating Systemic mastocytosis are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.
What treatment and support options exist for Systemic mastocytosis?
2 FDA-approved treatments and 2 patient support programs are currently tracked on UniteRare for Systemic mastocytosis. See the treatments and support programs sections for copay assistance, eligibility, and contact details.