Post-transplant lymphoproliferative disease

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12Active trials67Specialists8Treatment centers

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UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Post-transplant lymphoproliferative disease, often called PTLD, is a serious complication that can happen after an organ or stem cell transplant. When someone receives a transplant, they must take medicines called immunosuppressants to stop their body from rejecting the new organ. These medicines weaken the immune system, which can allow certain white blood cells to grow out of control. In most cases, a common virus called Epstein-Barr virus (EBV) — the same virus that causes mono — plays a key role in triggering this abnormal cell growth. PTLD is considered a type of lymphoma, meaning it is a cancer of the lymph system. PTLD can affect many parts of the body, including the lymph nodes, liver, lungs, gut, and even the brain. Symptoms can vary widely depending on where the disease develops. Common signs include swollen lymph nodes, fever, night sweats, unexplained weight loss, and fatigue. Some people develop stomach pain or problems with the transplanted organ itself. Treatment depends on the type and stage of PTLD. The first step is often reducing the immunosuppressant medicines to let the immune system fight back. Other treatments include a targeted antibody therapy called rituximab, chemotherapy, and sometimes radiation. With early detection and treatment, many patients respond well, though outcomes vary. Close monitoring after transplant is essential for catching PTLD early.

Also known as:

Key symptoms:

Swollen lymph nodes in the neck, armpits, or groinPersistent feverDrenching night sweatsUnexplained weight lossExtreme tiredness or fatigueStomach pain or bloatingNausea, vomiting, or diarrheaDifficulty breathing or chest painHeadaches or confusion (if the brain is involved)Signs that the transplanted organ is not working as well as beforeEnlarged tonsils or throat discomfortLoss of appetite

Clinical phenotype terms (16)— hover any for plain English
SnoringHP:0025267PharyngalgiaHP:0033050MalaiseHP:0033834Pulmonary noduleHP:0033608
Inheritance

Sporadic

Usually appears on its own, not inherited from a parent

Age of Onset

Variable

Can begin at different ages, from infancy through adulthood

Orphanet ↗NORD ↗

FDA & Trial Timeline

10 events
Nov 2026EBV-Tscm Cytotoxic T Cells (CTLs) for EBV- Driven Lymphomas/ Diseases

University Hospital, Basel, Switzerland — PHASE1, PHASE2

TrialNOT YET RECRUITING
Jul 2025Epcoritamab and Lenalidomide in Treating Patients With Refractory or Relapsed Immunodeficiency-Related Large B-Cell Lymphoma

Northwestern University — PHASE2

TrialACTIVE NOT RECRUITING
Jul 2025Elranatamab/Lenalidomide Consolidation and/or Elranatamab Maintenance Versus Standard of Care After D-VRd Induction in Transplant-eligible NDMM Patients

Intergroupe Francophone du Myelome — PHASE3

TrialRECRUITING
Jun 2025Exploratory Study of EBV-TCR-T Cell Injection for EBV DNAemia After Allogeneic Hematopoietic Stem Cell Transplantation

Daihong Liu — PHASE1, PHASE2

TrialRECRUITING
Apr 2025Defining ctDNA Metrics in Posttransplant Lymphoproliferative Disorder (PTLD)

Jennifer Amengual — PHASE2

TrialRECRUITING
Mar 2025EBV-AST Cell Therapy for EBV-Related Diseases After Stem Cell Transplantation

Daihong Liu — PHASE1, PHASE2

TrialRECRUITING
Mar 2025KPD Consolidation After ASCT in NDMM Patients

Peking University People's Hospital — PHASE2, PHASE3

TrialRECRUITING
Mar 2025Effectiveness and Safety of InO±DLI for Relapsed B-ALL/LBL After Allo-HSCT

First Affiliated Hospital of Zhejiang University — PHASE2

TrialNOT YET RECRUITING
Oct 2024PTLD: Multicentric Retrospective Study

Fondazione Italiana Linfomi - ETS

TrialACTIVE NOT RECRUITING
Jul 2024Phase II Study of Post-Transplant Low-Dose Inotuzumab Ozogamicin to Prevent Relapse of Acute Lymphoblastic Leukemia

Institute of Hematology & Blood Diseases Hospital, China — PHASE2

TrialRECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

No FDA-approved treatments are currently listed for Post-transplant lymphoproliferative disease.

12 clinical trialsare actively recruiting — trials can provide access to cutting-edge therapies.

View clinical trials →

Clinical Trials

12 recruitingView all trials with filters →
Phase 41 trial
Evaluation of the Efficacy of a Treatment by One Single Dose of Rituximab (375mg/m2 ) in the Prevention of the Epstein Barr Virus (EBV) Primary Infection and Post-transplant Lymphoproliferative Disorder in Adult EBV Seronegative Patients Who Received an EBV Seropositive Kidney Allograft
Phase 4
Actively Recruiting
· Sites: Strasbourg · Age: 1899 yrs
Phase 24 trials
Tafasitamab and Rituximab for Front-Line Treatment of Post-Transplant Lymphoproliferative Disorder
Phase 2
Actively Recruiting
PI: Timothy J Voorhees, MD, MSCR (Ohio State University Comprehensive Cancer Center) · Sites: New Brunswick, New Jersey; Hillsborough, North Carolina +1 more · Age: 1899 yrs
Defining ctDNA Metrics in Posttransplant Lymphoproliferative Disorder (PTLD)
Phase 2
Actively Recruiting
PI: Jennifer Amengual, MD (Columbia University) · Sites: Stanford, California; New York, New York · Age: 1599 yrs
Loncastuximab Tesirine for the Treatment of Relapsed or Refractory B-Cell Malignancies
Phase 2
Actively Recruiting
PI: Stephen D. Smith (Fred Hutch/University of Washington Cancer Consort) · Sites: Seattle, Washington · Age: 1899 yrs
Epcoritamab and Lenalidomide in Treating Patients With Refractory or Relapsed Immunodeficiency-Related Large B-Cell Lymphoma
Phase 2
Active
PI: Reem Karmali, MD (Northwestern University) · Sites: Chicago, Illinois · Age: 1899 yrs
Phase 11 trial
Administration of T Lymphocytes for Prevention of Relapse of Lymphomas
Phase 1
Active
PI: Natalie Grover, MD (Clinical Director of Cellular Therapy Program) · Sites: Chapel Hill, North Carolina; Winston-Salem, North Carolina · Age: 399 yrs
N/A1 trial
Whole-body Diffusion-weighted Magnetic Resonance Imaging for Staging and Treatment Prediction of Lymphoma
N/A
Active
PI: vincent vandecaveye, MD PhD (Universitaire Ziekenhuizen KU Leuven) · Sites: Leuven, Vlaams-Brabant
Other1 trial
PTLD: Multicentric Retrospective Study
Active
PI: Federica Cavallo, MD (Ematologia Universitaria - A.O.U. Citta della Salu) · Sites: Milan, MI; Aviano +19 more · Age: 1899 yrs

Specialists

Showing 25 of 67View all specialists →
BW
Birte Wistinghausen
NEW YORK, NY
Specialist
PI on 1 active trial
CP
Cyrille TOUZEAU, Prof
Specialist
PI on 1 active trial
AP
Aurore PERROT, Prof
Specialist
PI on 1 active trial
KM
Kurt Gunter, MD
BEVERLY, MA
Specialist
PI on 8 active trials
CM
Corey Cutler, MD, MPH
PARK CITY, UT
Specialist
PI on 3 active trials
CL
Chanaz LOUNI
Specialist
PI on 1 active trial
HP
Hartmut Goldschmidt, Prof.
Specialist
PI on 2 active trials
GM
Gunjan Shah, MD
Specialist
PI on 3 active trials1 Post-transplant lymphoproliferative disease publication
SM
Steven Devine, MD
LA CROSSE, WI
Specialist
PI on 4 active trials
RP
Raija H Silvennoinen, MD, PhD
Specialist
PI on 1 active trial
DM
Deepa Jagadeesh, MD, MPH
WORCESTER, MA
Specialist
PI on 4 active trials
PM
Paul Martin
Specialist
PI on 3 active trials73 Post-transplant lymphoproliferative disease publications
AK
Anne Kuan
SAN ANTONIO, TX
Specialist
PI on 1 active trial
MM
Michael Pulsipher, MD
LOS ANGELES, CA
Specialist
PI on 6 active trials
NM
Natalie Grover, MD
CHAPEL HILL, NC
Specialist
PI on 6 active trials
CP
Claudio G. Brunstein, MD, PhD
MINNEAPOLIS, MN
Specialist
PI on 6 active trials
SK
Shaji Kumar
Anchorage, Alaska
Specialist

Rare Disease Specialist

PI on 7 active trials

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Post-transplant lymphoproliferative disease.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Post-transplant lymphoproliferative diseaseForum →

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Latest news about Post-transplant lymphoproliferative disease

Disease timeline:

New recruiting trial: Defining ctDNA Metrics in Posttransplant Lymphoproliferative Disorder (PTLD)

A new clinical trial is recruiting patients for Post-transplant lymphoproliferative disease

New recruiting trial: Exploratory Study of EBV-TCR-T Cell Injection for EBV DNAemia After Allogeneic Hematopoietic Stem Cell Transplantation

A new clinical trial is recruiting patients for Post-transplant lymphoproliferative disease

New recruiting trial: Evaluation of the Efficacy of a Treatment by One Single Dose of Rituximab (375mg/m2 ) in the Prevention of the Epstein Barr Virus (EBV) Primary Infection and Post-transplant Lymphoproliferative Disorder in Adult EBV Seronegative Patients Who Received an EBV Seropositive Kidney Allograft

A new clinical trial is recruiting patients for Post-transplant lymphoproliferative disease

New recruiting trial: A Confirmatory Trial of Adjunctive NAC to Prevent Post Tuberculosis Lung Disease

A new clinical trial is recruiting patients for Post-transplant lymphoproliferative disease

New recruiting trial: Primary Multiple Myeloma Who Achieved MRD Negativity After Induction Therapy, ASCT or Not

A new clinical trial is recruiting patients for Post-transplant lymphoproliferative disease

New recruiting trial: Bridging Allogeneic Hematopoietic Stem Cell Transplantation or Not After CD19 CAR - T (S1904) Cell Therapy for r/r B-cell Acute Lymphoblastic Leukemia

A new clinical trial is recruiting patients for Post-transplant lymphoproliferative disease

New recruiting trial: Testing the Use of Combination Therapy in Adult Patients With Newly Diagnosed Multiple Myeloma, the EQUATE Trial

A new clinical trial is recruiting patients for Post-transplant lymphoproliferative disease

New recruiting trial: Faecal Microbiota Transplantation After Allogeneic Stem Cell Transplantation

A new clinical trial is recruiting patients for Post-transplant lymphoproliferative disease

New recruiting trial: A Study to Compare Iberdomide Maintenance Versus Lenalidomide Maintenance Therapy Following Autologous Stem Cell Transplant in Participants With Newly Diagnosed Multiple Myeloma

A new clinical trial is recruiting patients for Post-transplant lymphoproliferative disease

New recruiting trial: CD45RA-depleted CD19-CAR T Cell Consolidation After TCRαβ+/CD19 B Cell-depleted Haploidentical Hematopoietic Cell Transplantation for Relapsed/Refractory CD19+ ALL and Lymphoma

A new clinical trial is recruiting patients for Post-transplant lymphoproliferative disease

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What type of PTLD do I have, and how does that affect my treatment options?,How will you balance reducing my immunosuppression with protecting my transplanted organ?,Is rituximab the right first treatment for me, and what happens if it does not work?,How often will I need scans and blood tests to monitor my response to treatment?,What are the signs that my PTLD is coming back, and what should I do if I notice them?,Are there clinical trials available for my type of PTLD?,What long-term effects should I expect from treatment, and how will they affect my quality of life?

Common questions about Post-transplant lymphoproliferative disease

What is Post-transplant lymphoproliferative disease?

Post-transplant lymphoproliferative disease, often called PTLD, is a serious complication that can happen after an organ or stem cell transplant. When someone receives a transplant, they must take medicines called immunosuppressants to stop their body from rejecting the new organ. These medicines weaken the immune system, which can allow certain white blood cells to grow out of control. In most cases, a common virus called Epstein-Barr virus (EBV) — the same virus that causes mono — plays a key role in triggering this abnormal cell growth. PTLD is considered a type of lymphoma, meaning it is a

How is Post-transplant lymphoproliferative disease inherited?

Post-transplant lymphoproliferative disease follows a sporadic inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

Are there clinical trials for Post-transplant lymphoproliferative disease?

Yes — 12 recruiting clinical trials are currently listed for Post-transplant lymphoproliferative disease on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.

Which specialists treat Post-transplant lymphoproliferative disease?

25 specialists and care centers treating Post-transplant lymphoproliferative disease are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.