Overview
Congenital Malformation Syndrome is treated with 2 medications in our database, including VIJOICE, Proteus. 2 of these have manufacturer assistance programs available to help reduce out-of-pocket costs. Medications are manufactured by Novartis. Patients and caregivers can find copay cards, patient assistance programs, and travel grants for Congenital Malformation Syndrome treatment below.
FDA & Trial Timeline
10 eventsAcademisch Medisch Centrum - Universiteit van Amsterdam (AMC-UvA)
Assistance Publique - Hôpitaux de Paris — NA
Bernardino Clavo, MD, PhD
Instituto do Cancer do Estado de São Paulo — NA
University Hospital of Crete — NA
University of Vermont Medical Center — NA
Hartford Hospital — PHASE4
Assiut University
Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.
Treatments
2 availableVIJOICE
* Patient Copay Amount: Not Publicly Available * Maximum Annual Benefit Limit: Not Publicly Available * Core Eligibility Restrictions: Not Publicly Available * RxBIN, PCN, and Group numbers: Not Publi
Proteus
Detailed copay and financial assistance information is not publicly available for this medication at this time. Please consult your pharmacist or the manufacturer's official patient support program fo
Clinical Trials
View all trials with filters →No actively recruiting trials found for Congenital Malformation Syndrome at this time.
New trials open frequently. Follow this disease to get notified.
Rare Disease Specialist
Rare Disease Specialist
Treatment Centers
8 centersBaylor College of Medicine Rare Disease Center ↗
Baylor College of Medicine
📍 Houston, TX
🏥 NORDStanford Medicine Rare Disease Center ↗
Stanford Medicine
📍 Stanford, CA
🔬 UDNNIH Clinical Center Undiagnosed Diseases Program ↗
National Institutes of Health
📍 Bethesda, MD
🔬 UDNUCLA UDN Clinical Site ↗
UCLA Health
📍 Los Angeles, CA
🔬 UDNBaylor College of Medicine UDN Clinical Site ↗
Baylor College of Medicine
📍 Houston, TX
🔬 UDNHarvard/MGH UDN Clinical Site ↗
Massachusetts General Hospital
📍 Boston, MA
🏥 NORDMayo Clinic Center for Individualized Medicine ↗
Mayo Clinic
📍 Rochester, MN
👤 Mayo Clinic Center for Individualized Medicine
🏥 NORDUCLA Rare Disease Day Program ↗
UCLA Health
📍 Los Angeles, CA
Travel Grants
No travel grants are currently matched to Congenital Malformation Syndrome.
Community
No community posts yet. Be the first to share your experience with Congenital Malformation Syndrome.
Start the conversation →Latest news about Congenital Malformation Syndrome
Disease timeline:
New recruiting trial: Gene and Molecular Pathways of Ozone Treatment Response in Gynecological Tumor Patients With Chronic Pelvic Pain Secondary to Cancer Treatment
A new clinical trial is recruiting patients for Congenital Malformation Syndrome
New recruiting trial: Treatment Result of Zirconia Laminate Veneer
A new clinical trial is recruiting patients for Congenital Malformation Syndrome
New recruiting trial: Delineating the Molecular Spectrum and the Clinical, Imaging and Neuronal Phenotype of Chopra-Amiel-Gordon Syndrome
A new clinical trial is recruiting patients for Congenital Malformation Syndrome
New recruiting trial: Solid Tumors in RASopathies
A new clinical trial is recruiting patients for Congenital Malformation Syndrome
New recruiting trial: Effect of Music Therapy on Infants With Neonatal Abstinence Syndrome
A new clinical trial is recruiting patients for Congenital Malformation Syndrome
New recruiting trial: A Randomized Controlled Trial Comparing Fat-free Versus Balanced (WHO) Diet in Gallstone Disease
A new clinical trial is recruiting patients for Congenital Malformation Syndrome
New recruiting trial: Artificial Intelligence-assisted Colonoscopy in the Detection and Characterization of Colorectal Lesions
A new clinical trial is recruiting patients for Congenital Malformation Syndrome
New recruiting trial: Collecting Blood and Stool Samples to Detect Colorectal Cancer or Advanced Neoplasia in Lynch Syndrome Patients
A new clinical trial is recruiting patients for Congenital Malformation Syndrome
New recruiting trial: Klinefelter Syndrome and Testosterone Treatment in Puberty
A new clinical trial is recruiting patients for Congenital Malformation Syndrome
New recruiting trial: Pelvic Vein Quantitative Flow Characterization Using 2D and 4D Flow MRI
A new clinical trial is recruiting patients for Congenital Malformation Syndrome
Caregiver Resources
NORD Caregiver Resources
Support, advocacy, and financial assistance for caregivers of rare disease patients.
Mental Health Support
Rare disease caregiving can be isolating. Connect with counseling and peer support.
Family & Caregiver Grants
Financial assistance programs specifically for caregivers of rare disease patients.
Social Security Disability
Learn how rare disease patients may qualify for SSDI/SSI benefits.
Common questions about Congenital Malformation Syndrome
What is Congenital Malformation Syndrome?
Congenital Malformation Syndrome is treated with 2 medications in our database, including VIJOICE, Proteus. 2 of these have manufacturer assistance programs available to help reduce out-of-pocket costs. Medications are manufactured by Novartis. Patients and caregivers can find copay cards, patient assistance programs, and travel grants for Congenital Malformation Syndrome treatment below.
Which specialists treat Congenital Malformation Syndrome?
25 specialists and care centers treating Congenital Malformation Syndrome are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.
What treatment and support options exist for Congenital Malformation Syndrome?
2 FDA-approved treatments are currently tracked on UniteRare for Congenital Malformation Syndrome. See the treatments and support programs sections for copay assistance, eligibility, and contact details.