Neuroectodermal-endocrine syndrome

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ORPHA:2676
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18Specialists8Treatment centers

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Overview

Neuroectodermal-endocrine syndrome is a very rare condition that affects two major body systems at the same time: the nervous system (which controls how the brain and nerves work) and the endocrine system (which controls hormones). Because it is so rare, it is sometimes also referred to by its Orphanet code 2676. The syndrome causes a mix of problems related to how nerve cells develop and how the body produces and regulates hormones. This combination of features is what makes it unique and sometimes difficult to diagnose quickly. People with this condition may experience a range of symptoms including skin changes, problems with hormone-producing glands, and neurological difficulties. The exact features can vary from person to person, which means the condition can look different in different individuals. Because so few cases have been reported in the medical literature, doctors are still learning about the full range of symptoms and how the disease progresses over time. Treatment is currently focused on managing individual symptoms rather than curing the underlying cause. A team of specialists is usually needed to address the different body systems involved. Research into this condition is ongoing, but the rarity of the syndrome means that large clinical trials are not yet available.

Also known as:

Key symptoms:

Skin changes or unusual skin markingsProblems with hormone levels (endocrine dysfunction)Neurological symptoms such as seizures or developmental delaysAbnormalities in glands that produce hormonesPossible intellectual or learning difficultiesGrowth problems or short staturePossible vision or eye abnormalities

Inheritance

Variable

Can be inherited in different ways depending on the underlying gene

Age of Onset

Variable

Can begin at different ages, from infancy through adulthood

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Neuroectodermal-endocrine syndrome.

View clinical trials →

No actively recruiting trials found for Neuroectodermal-endocrine syndrome at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Neuroectodermal-endocrine syndrome community →

Specialists

18 foundView all specialists →
ND
Nageshwara V Dasari
HOUSTON, TX
Specialist
PI on 2 active trials
AP
Annamaria Colao, MD, PhD
Specialist
PI on 3 active trials
TH
Timothy Hobday
ROCHESTER, MN
Specialist
PI on 2 active trials1 Neuroectodermal-endocrine syndrome publication
AS
Ann (Annie) W Silk
Los Angeles, California
Specialist

Rare Disease Specialist

PI on 1 active trial
SA
Srivandana Akshintala
WASHINGTON, DC
Specialist
PI on 1 active trial
PM
Paul Martin
Specialist
PI on 3 active trials73 Neuroectodermal-endocrine syndrome publications
SM
Susan K. Parsons, MD, MRP
Specialist
PI on 1 active trial
AM
Antonio T Fojo, M.D.
BALTIMORE, MD
Specialist
PI on 2 active trials
CM
Chris DeRenzo, MD
MEMPHIS, TN
Specialist
PI on 1 active trial
AM
Anna Pawlowska, MD
DUARTE, CA
Specialist
PI on 3 active trials
NM
Nina Merchant
Specialist
PI on 1 active trial
MM
Michael Heinrich, MD
Specialist
PI on 1 active trial
KP
Kyueun Lee, Ph.D
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Neuroectodermal-endocrine syndrome.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Neuroectodermal-endocrine syndrome

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What tests do you recommend to confirm the diagnosis and understand which body systems are affected?,Should I have genetic testing, and if so, what type is most appropriate for my situation?,Which specialists should be part of my care team, and how often should I see each one?,Are there any clinical trials or research studies I could participate in?,What symptoms should prompt me to go to the emergency room right away?,How will this condition affect my daily life, and what support services are available?,Are there any patient registries or advocacy groups that could connect me with others who have this condition?

Common questions about Neuroectodermal-endocrine syndrome

What is Neuroectodermal-endocrine syndrome?

Neuroectodermal-endocrine syndrome is a very rare condition that affects two major body systems at the same time: the nervous system (which controls how the brain and nerves work) and the endocrine system (which controls hormones). Because it is so rare, it is sometimes also referred to by its Orphanet code 2676. The syndrome causes a mix of problems related to how nerve cells develop and how the body produces and regulates hormones. This combination of features is what makes it unique and sometimes difficult to diagnose quickly. People with this condition may experience a range of symptoms i

Which specialists treat Neuroectodermal-endocrine syndrome?

18 specialists and care centers treating Neuroectodermal-endocrine syndrome are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.