Epithelial tumor of the appendix

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11Active trials19Specialists8Treatment centers

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Overview

Epithelial tumors of the appendix are a group of rare growths that start in the lining cells of the appendix — a small, finger-shaped pouch attached to the large intestine in the lower right side of the belly. These tumors are sometimes called appendiceal neoplasms or appendix cancers. They include several types, such as low-grade and high-grade mucinous neoplasms (also called LAMN and HAMN), mucinous adenocarcinoma, and non-mucinous adenocarcinoma. Some types produce a jelly-like substance called mucin, which can build up inside the belly if the tumor ruptures — a serious condition known as pseudomyxoma peritonei (PMP). Many people with an epithelial tumor of the appendix have no symptoms at first. The tumor is often found by accident during surgery for appendicitis or during imaging done for another reason. When symptoms do appear, they can include belly pain, bloating, or a change in bowel habits. Because the appendix is small and symptoms are vague, diagnosis is often delayed. Treatment depends on the type and stage of the tumor. Surgery is the main treatment and may range from simple removal of the appendix to more extensive operations. For tumors that have spread into the belly, a specialized procedure called cytoreductive surgery combined with heated chemotherapy washed directly into the abdomen (HIPEC) may be recommended. Early-stage tumors often have a very good outlook, while more advanced cases require more aggressive treatment.

Also known as:

Key symptoms:

Dull or crampy pain in the lower right bellyBloating or a feeling of fullness in the abdomenIncreasing waist size without weight gainChange in bowel habits such as constipation or diarrheaNausea or vomitingNew hernia in the groin or belly button areaFeeling of pressure or heaviness in the pelvisUnexplained weight lossSymptoms that look like appendicitis (sudden sharp right-sided belly pain)Ovarian mass found on imaging in women

Inheritance

Sporadic

Usually appears on its own, not inherited from a parent

Age of Onset

Adult

Begins in adulthood (age 18 or older)

Orphanet ↗NORD ↗

FDA & Trial Timeline

10 events
Feb 2026Proactive Temperature Management in CRS-HIPEC for Prevention of Delirium

Aerospace Center Hospital — NA

TrialNOT YET RECRUITING
Dec 2024Study to Evaluate the Non-inferiority of Low-dose HIPEC Versus High-dose HIPEC in the Treatment of PMP (HIPEC-PMP)

University of Southampton — PHASE3

TrialRECRUITING
Nov 2024Metronomic Neoadjuvant Capecitabine and Cyclophosphamide in HUGE Pseudomyxoma Peritonei Patients

Fondazione IRCCS Istituto Nazionale dei Tumori, Milano — PHASE2

TrialRECRUITING
Jan 2024A Phase I/II Study of Intraperitoneal Paclitaxel in Patients With Metastatic Appendiceal Adenocarcinoma

M.D. Anderson Cancer Center — PHASE1, PHASE2

TrialRECRUITING
Dec 2023A Prospective Feasibility Study Using ctDNA to Tailor Neoadjuvant Chemotherapy for Patients With Colorectal or Appendiceal Adenocarcinoma

M.D. Anderson Cancer Center — NA

TrialRECRUITING
Nov 2022Genetics of Appendix Cancer Study

Andreana Holowatyj, PhD, MSCI

TrialRECRUITING
Sep 2022Diagnostic Value of Diffusion-weighted Magnetic Resonance in High-risk Colorectal and Appendiceal Neoplasms

Laval University — NA

TrialACTIVE NOT RECRUITING
Sep 2021Impact of Cardiac Coherence on Anxiety in Patients Operated on for a Peritoneal Carcinosis

Institut du Cancer de Montpellier - Val d'Aurelle — NA

TrialRECRUITING
May 2021Study of CBX-12 in Subjects With Advanced or Metastatic Refractory Solid Tumors

Cybrexa Therapeutics — PHASE1, PHASE2

TrialACTIVE NOT RECRUITING
Mar 2017Atezolizumab and Bevacizumab in Treating Patients With Rare Solid Tumors

M.D. Anderson Cancer Center — PHASE2

TrialACTIVE NOT RECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

No FDA-approved treatments are currently listed for Epithelial tumor of the appendix.

11 clinical trialsare actively recruiting — trials can provide access to cutting-edge therapies.

View clinical trials →

Clinical Trials

11 recruitingView all trials with filters →
Phase 31 trial
Study to Evaluate the Non-inferiority of Low-dose HIPEC Versus High-dose HIPEC in the Treatment of PMP (HIPEC-PMP)
Phase 3
Actively Recruiting
PI: Faheez Mohamed, MBChB, MD, FRCS (Peritoneal Malignancy Unit Hampshire Hospitals NHS) · Sites: Basingstoke, Hampshire · Age: 1699 yrs
Phase 24 trials
Metronomic Neoadjuvant Capecitabine and Cyclophosphamide in HUGE Pseudomyxoma Peritonei Patients
Phase 2
Actively Recruiting
PI: Alessandra Raimondi, MD (Fondazione IRCCS Istituto Nazionale dei Tumori, Mi) · Sites: Milan · Age: 1876 yrs
Antibiotic Treatment and Long-term Outcomes of Patients With Pseudomyxoma Peritonei of Appendiceal Origin
Phase 2
Active
PI: Armando Sardi, M.D. (Mercy Medical Center) · Sites: Baltimore, Maryland · Age: 2199 yrs
Atezolizumab and Bevacizumab in Treating Patients With Rare Solid Tumors
Phase 2
Active
PI: Kanwal P Raghav, MD (M.D. Anderson Cancer Center) · Sites: Houston, Texas · Age: 1899 yrs
ICARuS Post-operative Intraperitoneal Chemotherapy (EPIC) and Hyperthermic Intraperitoneal Chemotherapy (HIPEC) After Optimal Cytoreductive Surgery (CRS) for Neoplasms of the Appendix, Colon or Rectum With Isolated Peritoneal Metastasis
Phase 2
Active
PI: Garrett Nash, MD, MPH (Memorial Sloan Kettering Cancer Center) · Sites: Miami, Florida; St Louis, Missouri +7 more · Age: 1899 yrs
Phase 11 trial
Biweekly Intraperitoneal Oxaliplatin With Systemic Capecitabine and Bevacizumab for Patients With Peritoneal Carcinomatosis From Appendiceal or Colorectal Cancer
Phase 1
Active
PI: Benjamin Tan, M.D. (Washington University School of Medicine) · Sites: St Louis, Missouri · Age: 1899 yrs
N/A2 trials
Impact of Cardiac Coherence on Anxiety in Patients Operated on for a Peritoneal Carcinosis
N/A
Actively Recruiting
PI: Estelle Guerdoux-Ninot, MD (Institut régional du cancer de Montpellier) · Sites: Montpellier, Hérault · Age: 1899 yrs
Diagnostic Value of Diffusion-weighted Magnetic Resonance in High-risk Colorectal and Appendiceal Neoplasms
N/A
Active
PI: Alexandre Brind'Amour, MD (Laval University) · Sites: Montreal, Quebec; Québec, Quebec · Age: 1899 yrs
Other2 trials
Register With Patients in Which Hyperthermic Intra-Peritoneal Chemotherapy (HIPEC) Was Performed
Actively Recruiting
PI: André JL D'Hoore, PhD (University Clinics Gasthuisberg Department of Abdo) · Sites: Leuven, Flemish Brabant
Genetics of Appendix Cancer Study
Actively Recruiting
PI: Andreana N Holowatyj, PhD, MSCI (Vanderbilt-Ingram Cancer Center) · Sites: Nashville, Tennessee · Age: 1899 yrs

Specialists

19 foundView all specialists →
AM
Alexandre Brind'Amour, MD
Specialist
PI on 1 active trial1 Epithelial tumor of the appendix publication
AM
Andreana N Holowatyj, PhD, MSCI
Specialist
PI on 1 active trial
FF
Faheez Mohamed, MBChB, MD, FRCS
Specialist
PI on 1 active trial
RM
Richard McQuellon
WINSTON SALEM, NC
Specialist
PI on 1 active trial
SM
Scot C. Remick, MD
SCARBOROUGH, ME
Specialist
PI on 9 active trials
BM
Brennan Spiegel, MD, MSHS
LOS ANGELES, CA
Specialist
PI on 1 active trial
MP
Marie A Bakitas, PhD
LEBANON, NH
Specialist
PI on 1 active trial
KR
Kanwal P Raghav
HOUSTON, TX
Specialist
PI on 2 active trials6 Epithelial tumor of the appendix publications
PM
Prakash Pandalai, MD
LEXINGTON, KY
Specialist
PI on 1 active trial
WP
Wim P Ceelen, MD, PhD, Prof
Specialist
PI on 2 active trials
JC
Juan P Cata
EL SEGUNDO, CA
Specialist
PI on 2 active trials

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Epithelial tumor of the appendix.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Epithelial tumor of the appendix

Disease timeline:

New recruiting trial: A Phase I/II Study of Intraperitoneal Paclitaxel in Patients With Metastatic Appendiceal Adenocarcinoma

A new clinical trial is recruiting patients for Epithelial tumor of the appendix

New recruiting trial: A Prospective Feasibility Study Using ctDNA to Tailor Neoadjuvant Chemotherapy for Patients With Colorectal or Appendiceal Adenocarcinoma

A new clinical trial is recruiting patients for Epithelial tumor of the appendix

New recruiting trial: Study to Evaluate the Non-inferiority of Low-dose HIPEC Versus High-dose HIPEC in the Treatment of PMP (HIPEC-PMP)

A new clinical trial is recruiting patients for Epithelial tumor of the appendix

New recruiting trial: Locally ablatIVe thErapy for oLigo-progressive gastrOintestiNal maliGnancies (LIVELONG)

A new clinical trial is recruiting patients for Epithelial tumor of the appendix

New recruiting trial: Genetics of Appendix Cancer Study

A new clinical trial is recruiting patients for Epithelial tumor of the appendix

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What exact type of epithelial tumor do I have, and what does the grade mean for my treatment and outlook?,Has the tumor spread beyond the appendix, and do I need additional surgery or chemotherapy?,Should I be referred to a center that specializes in cytoreductive surgery and HIPEC?,Should my tumor tissue be tested for specific genetic mutations that might affect my treatment options?,Are there any clinical trials I might be eligible for?,How often do I need follow-up scans and blood tests, and what are we watching for?,Should my family members be tested for hereditary cancer syndromes given my diagnosis?

Common questions about Epithelial tumor of the appendix

What is Epithelial tumor of the appendix?

Epithelial tumors of the appendix are a group of rare growths that start in the lining cells of the appendix — a small, finger-shaped pouch attached to the large intestine in the lower right side of the belly. These tumors are sometimes called appendiceal neoplasms or appendix cancers. They include several types, such as low-grade and high-grade mucinous neoplasms (also called LAMN and HAMN), mucinous adenocarcinoma, and non-mucinous adenocarcinoma. Some types produce a jelly-like substance called mucin, which can build up inside the belly if the tumor ruptures — a serious condition known as p

How is Epithelial tumor of the appendix inherited?

Epithelial tumor of the appendix follows a sporadic inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Epithelial tumor of the appendix typically begin?

Typical onset of Epithelial tumor of the appendix is adult. Age of onset can vary across affected individuals.

Are there clinical trials for Epithelial tumor of the appendix?

Yes — 11 recruiting clinical trials are currently listed for Epithelial tumor of the appendix on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.

Which specialists treat Epithelial tumor of the appendix?

19 specialists and care centers treating Epithelial tumor of the appendix are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.