Vascular Ehlers-Danlos syndrome

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ORPHA:286OMIM:130050Q79.6
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2Active trials22Specialists8Treatment centers

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UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Vascular Ehlers-Danlos syndrome (vEDS), also known as Ehlers-Danlos syndrome type IV, is a rare and severe inherited connective tissue disorder caused by pathogenic variants in the COL3A1 gene, which encodes type III procollagen. Type III collagen is a major structural component of blood vessel walls, the gastrointestinal tract, and the uterus, making these organ systems particularly vulnerable. The condition is considered the most life-threatening subtype of Ehlers-Danlos syndrome due to the risk of spontaneous arterial dissection or rupture, bowel perforation (most commonly of the sigmoid colon), and uterine rupture during pregnancy. Characteristic physical features include thin, translucent skin through which underlying veins are easily visible, particularly over the chest and abdomen. Patients often have a distinctive facial appearance with thin lips, a narrow nose, small chin, and prominent eyes. Easy bruising is common, and wound healing may be delayed. Joint hypermobility, when present, tends to be limited to the small joints of the hands. Arterial, intestinal, and uterine complications typically present in adolescence or early adulthood, with a median life expectancy historically reported around 50 years, though this varies considerably. Diagnosis is confirmed through molecular genetic testing of the COL3A1 gene. Management focuses on surveillance, prevention of complications, and prompt treatment of vascular or gastrointestinal emergencies. Patients are advised to avoid contact sports, heavy lifting, and invasive vascular procedures when possible. The medication celiprolol, a beta-blocker with vasodilatory properties, has shown some evidence of reducing the risk of arterial events in clinical trials and is used in some centers as a preventive therapy. Surgical interventions carry significant risk due to tissue fragility and are generally reserved for life-threatening emergencies. Genetic counseling is strongly recommended for affected individuals and their families.

Also known as:

Clinical phenotype terms— hover any for plain English:

Bladder diverticulumHP:0000015Abnormal oral frenulum morphologyHP:0000190
Inheritance

Autosomal dominant

Passed on from just one parent; each child has about a 50% chance of inheriting it

Age of Onset

Variable

Can begin at different ages, from infancy through adulthood

Orphanet ↗OMIM ↗NORD ↗

FDA & Trial Timeline

2 events
Apr 2024Heart Coherence Training on Vascular Ehlers-Danlos Syndrome Patients

Baylor College of Medicine — NA

TrialRECRUITING
Nov 2022Clinical Trial to Compare the Efficacy of Celiprolol to Placebo in Patients With Vascular Ehlers-Danlos Syndrome

Acer Therapeutics Inc. — PHASE3

TrialRECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

No FDA-approved treatments are currently listed for Vascular Ehlers-Danlos syndrome.

2 clinical trialsare actively recruiting — trials can provide access to cutting-edge therapies.

View clinical trials →

Clinical Trials

2 recruitingView all trials with filters →
Phase 31 trial
Clinical Trial to Compare the Efficacy of Celiprolol to Placebo in Patients With Vascular Ehlers-Danlos Syndrome
Phase 3
Actively Recruiting
PI: Sheila Woodhouse, MD; Ph.D. · Sites: Culver City, California · Age: 1564 yrs
N/A1 trial
Heart Coherence Training on Vascular Ehlers-Danlos Syndrome Patients
N/A
Actively Recruiting
PI: Shaine A Morris, MD, MPH (Baylor College of Medicine) · Sites: Houston, Texas · Age: 1245 yrs

Specialists

22 foundView all specialists →
CD
Cyrille BERGOIN, Dr.
Specialist
PI on 1 active trial
PP
Patrick MUCCI, Prof.
Specialist
PI on 1 active trial
SP
Sheila Woodhouse, MD; Ph.D.
Culver City, California
Specialist

Rare Disease Specialist

SM
Shaine A Morris, MD, MPH
Houston, Texas
Specialist

Rare Disease Specialist

PI on 2 active trials
MM
Michael Frank, MD
Specialist
PI on 1 active trial
MP
Mari Lundberg, Professor
MINNEAPOLIS, MN
Specialist
PI on 1 active trial1 Vascular Ehlers-Danlos syndrome publication
LM
Luca Sangiorgi, MD, PhD, MS
Specialist
PI on 3 active trials
XM
Xavier JEUNEMAITRE, MD,PHD
Specialist
PI on 1 active trial
RA
Raja Sivamani, MD MS AP
Sacramento, California
Specialist

Rare Disease Specialist

PI on 4 active trials
PD
Philip Noto, DO
OLD WESTBURY, NY
Specialist
PI on 1 active trial3 Vascular Ehlers-Danlos syndrome publications
MM
Malcolm Kohler, Prof. MD
Specialist
PI on 2 active trials
RO
Richard A Driscoll, O.D.
Specialist
PI on 1 active trial
AP
Amanda J Miller, Ph.D.
Specialist
PI on 1 active trial
CM
Carlos Rafael Ramirez Paesano, MD
Specialist
PI on 1 active trial
KP
Kathryn C Chatfield, MD, PhD
COLORADO SPRINGS, CO
Specialist
PI on 1 active trial
EM
Emmanuel Messas, MD
Specialist
PI on 3 active trials
MP
Megan L Fitzgerald, PhD
Delafield, Wisconsin
Specialist

Rare Disease Specialist

PI on 1 active trial
TB
Thomas Van Den Bossche
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Vascular Ehlers-Danlos syndrome.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Vascular Ehlers-Danlos syndrome

Disease timeline:

New trial: Clinical Trial to Compare the Efficacy of Celiprolol to Placebo in Patients With Vascular Ehlers-Dan

Phase PHASE3 trial recruiting. ACER-002 (celiprolol) 200 mg BID

New trial: Heart Coherence Training on Vascular Ehlers-Danlos Syndrome Patients

Phase NA trial recruiting. Heartmath Intervention

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Common questions about Vascular Ehlers-Danlos syndrome

What is Vascular Ehlers-Danlos syndrome?

Vascular Ehlers-Danlos syndrome (vEDS), also known as Ehlers-Danlos syndrome type IV, is a rare and severe inherited connective tissue disorder caused by pathogenic variants in the COL3A1 gene, which encodes type III procollagen. Type III collagen is a major structural component of blood vessel walls, the gastrointestinal tract, and the uterus, making these organ systems particularly vulnerable. The condition is considered the most life-threatening subtype of Ehlers-Danlos syndrome due to the risk of spontaneous arterial dissection or rupture, bowel perforation (most commonly of the sigmoid co

How is Vascular Ehlers-Danlos syndrome inherited?

Vascular Ehlers-Danlos syndrome follows a autosomal dominant inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

Are there clinical trials for Vascular Ehlers-Danlos syndrome?

Yes — 2 recruiting clinical trials are currently listed for Vascular Ehlers-Danlos syndrome on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.

Which specialists treat Vascular Ehlers-Danlos syndrome?

22 specialists and care centers treating Vascular Ehlers-Danlos syndrome are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.