Overview
Other Congenital Malformation Syndromes is treated with 1 medication in our database, including VIJOICE. 1 of these has manufacturer assistance programs available to help reduce out-of-pocket costs. Medications are manufactured by Novartis. Patients and caregivers can find copay cards, patient assistance programs, and travel grants for Other Congenital Malformation Syndromes treatment below.
FDA & Trial Timeline
5 eventsNational Institute of Allergy and Infectious Diseases (NIAID)
Merck Sharp & Dohme LLC — PHASE2
Erasca, Inc. — PHASE1
Celgene — PHASE3
National Institute of Allergy and Infectious Diseases (NIAID)
Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.
Treatments
No FDA-approved treatments are currently listed for Other Congenital Malformation Syndromes.
View clinical trials →Clinical Trials
View all trials with filters →No actively recruiting trials found for Other Congenital Malformation Syndromes at this time.
New trials open frequently. Follow this disease to get notified.
Rare Disease Specialist
Rare Disease Specialist
Rare Disease Specialist
Treatment Centers
8 centersBaylor College of Medicine Rare Disease Center ↗
Baylor College of Medicine
📍 Houston, TX
🏥 NORDStanford Medicine Rare Disease Center ↗
Stanford Medicine
📍 Stanford, CA
🔬 UDNNIH Clinical Center Undiagnosed Diseases Program ↗
National Institutes of Health
📍 Bethesda, MD
🔬 UDNUCLA UDN Clinical Site ↗
UCLA Health
📍 Los Angeles, CA
🔬 UDNBaylor College of Medicine UDN Clinical Site ↗
Baylor College of Medicine
📍 Houston, TX
🔬 UDNHarvard/MGH UDN Clinical Site ↗
Massachusetts General Hospital
📍 Boston, MA
🏥 NORDMayo Clinic Center for Individualized Medicine ↗
Mayo Clinic
📍 Rochester, MN
👤 Mayo Clinic Center for Individualized Medicine
🏥 NORDUCLA Rare Disease Day Program ↗
UCLA Health
📍 Los Angeles, CA
Travel Grants
No travel grants are currently matched to Other Congenital Malformation Syndromes.
Community
No community posts yet. Be the first to share your experience with Other Congenital Malformation Syndromes.
Start the conversation →Latest news about Other Congenital Malformation Syndromes
1 articlesCaregiver Resources
NORD Caregiver Resources
Support, advocacy, and financial assistance for caregivers of rare disease patients.
Mental Health Support
Rare disease caregiving can be isolating. Connect with counseling and peer support.
Family & Caregiver Grants
Financial assistance programs specifically for caregivers of rare disease patients.
Social Security Disability
Learn how rare disease patients may qualify for SSDI/SSI benefits.
Common questions about Other Congenital Malformation Syndromes
What is Other Congenital Malformation Syndromes?
Other Congenital Malformation Syndromes is treated with 1 medication in our database, including VIJOICE. 1 of these has manufacturer assistance programs available to help reduce out-of-pocket costs. Medications are manufactured by Novartis. Patients and caregivers can find copay cards, patient assistance programs, and travel grants for Other Congenital Malformation Syndromes treatment below.
Which specialists treat Other Congenital Malformation Syndromes?
6 specialists and care centers treating Other Congenital Malformation Syndromes are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.