Other Congenital Malformation Syndromes Advocacy Hub | UniteRare

At a Glance

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Regulatory Watchboard

5 events

May 2023Evaluating the Genetics and Immunology of Periodic Fever, Aphthous Stomatitis, Pharyngitis, and Cervical Adenitis (PFAPA) Syndrome and Other Tonsil Disorders

National Institute of Allergy and Infectious Diseases (NIAID)

TrialRECRUITING

Nov 2021A Study of the Safety and Tolerability in Participants With PIK3CA-related Overgrowth Spectrum or Proteus Syndrome Who Are Being Treated With Miransertib (MK-7075) in Other Studies (MK-7075-006)

Merck Sharp & Dohme LLC — PHASE2

TrialACTIVE NOT RECRUITING

Dec 2020A Dose Escalation/Expansion Study of ERAS-601 in Patients With Advanced or Metastatic Solid Tumors

Erasca, Inc. — PHASE1

TrialACTIVE NOT RECRUITING

Aug 2019A Study to Evaluate Long-term Safety in Participants Who Have Participated in Other Luspatercept (ACE-536) Clinical Trials

Celgene — PHASE3

TrialRECRUITING

Dec 2016Natural History, Pathogenesis, and Outcome of Autoinflammatory Diseases (NOMID/CAPS, DIRA, CANDLE, SAVI, NLRC4-MAS, Still'S-like Diseases, and Other Undifferentiated Autoinflammatory Diseases)

National Institute of Allergy and Infectious Diseases (NIAID)

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

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FINANCIAL LANDSCAPE SUMMARY

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Clinical Trial Landscape

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Specialist Network

Top 6 by expertise

Hanny Al-Samkari, MD

Massachusetts General Hospital

📍 Miami, Florida

Score 83 trials

Ann (Annie) W Silk

Dana-Farber - Harvard Cancer Center LAO

📍 Los Angeles, California

Score 81 trial

Michael Ortiz, MD

Memorial Sloan Kettering Cancer Center

Score 42 trials

Cheryl L. Willman, MD, MD

University of New Mexico Cancer Center

📍 ALBUQUERQUE, TX

Score 42 trials

Yuankai Shi, MD

Cancer Institute and Hospital, Chinese Academy of Medical Sciences

Score 313 trials

John Matthews, MBBS, MCRP, PhD

The University of Alabama at Birmingham

📍 Birmingham, Alabama

Score 04 trials

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