Neonatal scleroderma

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ORPHA:398127P83.8
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11Specialists8Treatment centers

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UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Neonatal scleroderma is an extremely rare skin condition that appears in newborns, characterized by hardening and thickening of the skin shortly after birth. The term 'scleroderma' means 'hard skin,' and when it occurs in the neonatal period (the first 28 days of life), it is classified separately from the more common forms of scleroderma seen in older children and adults. Affected babies may develop firm, tight patches of skin that can limit movement and cause discomfort. The skin may appear shiny, waxy, or discolored in the affected areas. In some cases, the hardening can extend to deeper tissues beneath the skin. Because this condition is so rare, the exact cause is not fully understood. It may overlap with or be confused with other neonatal skin conditions such as sclerema neonatorum or neonatal morphea. The treatment approach is mainly supportive, focusing on skin care, physical therapy to maintain movement, and monitoring for any complications that may affect internal organs. Early recognition and management by a team of specialists is important to give the baby the best possible outcome. The long-term course can vary widely depending on the severity and extent of skin involvement.

Key symptoms:

Hardening or thickening of the skinTight, shiny, or waxy-looking skinSkin discoloration (darker or lighter patches)Reduced movement of affected limbs or jointsStiff joints or difficulty bending arms and legsSkin that feels firm or woody to the touchPoor feeding due to tightened skin around the mouthRestricted chest wall movement affecting breathingSwelling of affected areasFailure to thrive or poor weight gain

Inheritance

Sporadic

Usually appears on its own, not inherited from a parent

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Neonatal scleroderma.

View clinical trials →

No actively recruiting trials found for Neonatal scleroderma at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Neonatal scleroderma community →

Specialists

11 foundView all specialists →
SM
Sarah L Lonowski, MD
OMAHA, NE
Specialist
PI on 1 active trial
NM
Nihan Cuzdan, MD
Specialist
PI on 1 active trial
ZL
Zhanguo Li
Specialist
PI on 7 active trials819 Neonatal scleroderma publications
MM
Monique Hinchcliff, MD
NORTH HAVEN, CT
Specialist
PI on 2 active trials
AM
Adela Cardones, MD
DURHAM, NC
Specialist
PI on 2 active trials
JM
John S Nelson, M.D,Ph.D
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Neonatal scleroderma.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Neonatal sclerodermaForum →

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Latest news about Neonatal scleroderma

No recent news articles for Neonatal scleroderma.

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

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Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.How much of my baby's body is affected, and is there any internal organ involvement?,What is the expected course of this condition for my child specifically?,What treatments do you recommend, and what are the potential side effects?,How often should my baby have follow-up appointments and with which specialists?,Are there any physical therapy or skin care routines I should start at home?,Should we consider genetic testing to rule out other conditions?,Are there any clinical trials or research studies we could participate in?

Common questions about Neonatal scleroderma

What is Neonatal scleroderma?

Neonatal scleroderma is an extremely rare skin condition that appears in newborns, characterized by hardening and thickening of the skin shortly after birth. The term 'scleroderma' means 'hard skin,' and when it occurs in the neonatal period (the first 28 days of life), it is classified separately from the more common forms of scleroderma seen in older children and adults. Affected babies may develop firm, tight patches of skin that can limit movement and cause discomfort. The skin may appear shiny, waxy, or discolored in the affected areas. In some cases, the hardening can extend to deeper ti

How is Neonatal scleroderma inherited?

Neonatal scleroderma follows a sporadic inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Neonatal scleroderma typically begin?

Typical onset of Neonatal scleroderma is neonatal. Age of onset can vary across affected individuals.

Which specialists treat Neonatal scleroderma?

11 specialists and care centers treating Neonatal scleroderma are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.