Hemolytic uremic syndrome

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ORPHA:544458
Who is this for?
Show terms as
2Active trials35Specialists8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Also known as:

Orphanet ↗NORD ↗

FDA & Trial Timeline

4 events
Oct 2025Prevalence of Hemolytic Uremic Syndrome (HUS) in Pediatrics

Assiut University

TrialNOT YET RECRUITING
Oct 2024Efficacy of INM004 in Children With STEC-HUS

Inmunova S.A. — PHASE3

TrialRECRUITING
Sep 2022Hyperhydration in Children With Shiga Toxin-Producing E. Coli Infection

University of Calgary — NA

TrialRECRUITING
Apr 2021Therapeutic Orientation Test in Thrombotic Microangiopathy

University Hospital, Montpellier — NA

TrialRECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

No FDA-approved treatments are currently listed for Hemolytic uremic syndrome.

2 clinical trialsare actively recruiting — trials can provide access to cutting-edge therapies.

View clinical trials →

Clinical Trials

2 recruitingView all trials with filters →
Phase 31 trial
Efficacy of INM004 in Children With STEC-HUS
Phase 3
Actively Recruiting
PI: Santiago Sanguineti, Ph.D (Inmunova S.A.) · Sites: Bahía Blanca, Buenos Aires; Bahía Blanca, Buenos Aires +50 more · Age: 017 yrs
N/A1 trial
Hyperhydration in Children With Shiga Toxin-Producing E. Coli Infection
N/A
Actively Recruiting
PI: Stephen Freedman, MDCM (University of Calgary) · Sites: Birmingham, Alabama; Little Rock, Arkansas +24 more · Age: 021 yrs

Specialists

Showing 25 of 35View all specialists →
DM
David Askenazi, MD
BIRMINGHAM, AL
Specialist
PI on 1 active trial
PT
Phillip I Tarr
SAINT LOUIS, MO
Specialist
1 Hemolytic uremic syndrome publication
OB
Olivia Boyer
READING, PA
Specialist
4 Hemolytic uremic syndrome publications
VF
Véronique Frémeaux-Bacchi
Specialist
4 Hemolytic uremic syndrome publications
CL
Christoph Licht
Specialist
3 Hemolytic uremic syndrome publications
NK
Nicole C A J van de Kar
Specialist
2 Hemolytic uremic syndrome publications
NS
Nora Schwotzer
Specialist
2 Hemolytic uremic syndrome publications
BG
Bora Gülhan
Specialist
2 Hemolytic uremic syndrome publications
F&
Fatih Özaltın
Specialist
2 Hemolytic uremic syndrome publications
PW
Patrick R Walsh
Specialist
2 Hemolytic uremic syndrome publications
AS
Anne-Laure Sellier-Leclerc
Specialist
2 Hemolytic uremic syndrome publications
SS
Sidharth Kumar Sethi
Specialist
2 Hemolytic uremic syndrome publications
PN
Patrick Niaudet
Specialist
1 Hemolytic uremic syndrome publication
SF
Stephen B Freedman
Specialist
1 Hemolytic uremic syndrome publication
AJ
Anuja Java
SAINT LOUIS, MO
Specialist
1 Hemolytic uremic syndrome publication
RR
Rupesh Raina
AKRON, OH
Specialist
3 Hemolytic uremic syndrome publications
SP
Santiago Sanguineti, Ph.D
Specialist
PI on 1 active trial
AM
Arnaud Garnier, MD
Specialist
PI on 1 active trial1 Hemolytic uremic syndrome publication
RM
Robert J Kreitman, M.D.
OLNEY, MD
Specialist
PI on 12 active trials
FP
Fernando Goldbaum, PhD
Specialist
PI on 1 active trial
UD
Urielle Desalbres
Specialist
PI on 21 active trials1 Hemolytic uremic syndrome publication
KB
Karine Brochard
Specialist
PI on 1 active trial
NS
Nuria Saval
Specialist
PI on 1 active trial
SW
Sydney Williams
Specialist
PI on 1 active trial94 Hemolytic uremic syndrome publications
PP
Pieter van Paassen, MD, PhD
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Hemolytic uremic syndrome.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Hemolytic uremic syndrome

Disease timeline:

New recruiting trial: Therapeutic Orientation Test in Thrombotic Microangiopathy

A new clinical trial is recruiting patients for Hemolytic uremic syndrome

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Common questions about Hemolytic uremic syndrome

Are there clinical trials for Hemolytic uremic syndrome?

Yes — 2 recruiting clinical trials are currently listed for Hemolytic uremic syndrome on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.

Which specialists treat Hemolytic uremic syndrome?

25 specialists and care centers treating Hemolytic uremic syndrome are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.