Neuromyelitis optica spectrum disorder

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3FDA treatments5Active trials77Specialists8Treatment centers2Financial resources

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Overview

Neuromyelitis optica spectrum disorder (NMOSD), also known as Devic's disease or Devic syndrome, is a rare but serious autoimmune disease that mainly attacks the optic nerves (which connect your eyes to your brain) and the spinal cord. In autoimmune diseases, the body's immune system mistakenly attacks its own healthy tissue. In NMOSD, the immune system produces proteins called antibodies — most often against a protein called AQP4 (aquaporin-4) — that damage the protective covering of nerve fibers, causing inflammation and injury. The most common symptoms are sudden vision loss or pain in one or both eyes, and weakness, numbness, or paralysis in the arms and legs. Many people also experience problems with bladder and bowel control. NMOSD tends to cause attacks, or relapses, that can leave lasting disability if not treated quickly. Unlike multiple sclerosis (MS), which it is sometimes confused with, NMOSD attacks are often more severe and recovery between attacks may be incomplete. Treatment has improved greatly in recent years. During an attack, high-dose steroids and plasma exchange (a process that filters harmful antibodies from the blood) are used to reduce damage. To prevent future attacks, doctors use long-term immunosuppressive medications. Several FDA-approved therapies now exist specifically for NMOSD, including eculizumab (Soliris), inebilizumab (Uplizna), and satralizumab (Enspryng). Early diagnosis and consistent treatment are key to protecting long-term function and quality of life.

Also known as:

Key symptoms:

Sudden vision loss or blurred vision in one or both eyesEye pain, especially when moving the eyesWeakness or paralysis in the arms or legsNumbness or tingling in the limbs or trunkPainful muscle spasmsLoss of bladder or bowel controlDifficulty walking or loss of balanceNausea, vomiting, or hiccups that won't stop (from brainstem involvement)Extreme fatigueSensitivity to heat worsening symptomsNeck or back painDifficulty breathing in severe cases

Clinical phenotype terms (17)— hover any for plain English
Functional abnormality of the bladderHP:0000009Neuronal loss in central nervous systemHP:0002529ParaplegiaHP:0010550Peripheral demyelinationHP:0011096MyelitisHP:0012486Optic neuritisHP:0100653Anti-aquaporin 4 antibody positivityHP:0033342CSF pleocytosisHP:0012229Anti-myelin oligodendrocyte glycoprotein antibody positivityHP:0032492Recurrent singultusHP:0100247
Inheritance

Sporadic

Usually appears on its own, not inherited from a parent

Age of Onset

Variable

Can begin at different ages, from infancy through adulthood

Orphanet ↗NORD ↗

FDA & Trial Timeline

7 events
Dec 2025Efficacy and Safety of Transcranial Temporal Interference Stimulation (tTIS) for Neuropathic Pain in Neuromyelitis Optica Spectrum Disorder (NMOSD)

Tang-Du Hospital — NA

TrialRECRUITING
Jul 2024Inebilizumab in Acute Neuromyelitis Optica Spectrum Disorders

Xuanwu Hospital, Beijing

TrialRECRUITING
Jul 2024FcRn Antagonists (Efgartigimod) for Acute NMOSD Attack

Tianjin Medical University General Hospital — PHASE2

TrialNOT YET RECRUITING
Jul 2021Biorepository and Registry for Plasma Exchange Patients

Charles M Knudson

TrialRECRUITING
Jun 2020Uplizna: FDA approved

Uplizna is indicated for for the treatment of neuromyelitis optica spectrum disorder (NMOSD) in adult patients who are anti-aquaporin-4 (AQP4) antibody positive.

FDAcompleted
Jan 2019Clinical and Imaging Cohort of Neuroinflammation Diseases in China (CLUE)

Beijing Tiantan Hospital

TrialRECRUITING
Jun 2012The Longitudinal CONQUER Study of Rare Neuroimmunologic Disorders

University of Texas Southwestern Medical Center

TrialACTIVE NOT RECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

3 available

Enspryng

SATRALIZUMAB· Genentech, Inc.

ENSPRYNG is indicated for the treatment of neuromyelitis optica spectrum disorder (NMOSD) in adult patients who are anti-aquaporin-4 (AQP4) antibody positive

Ultomiris

RAVULIZUMAB· Alexion Pharmaceuticals Inc.■ Boxed Warning

the treatment of adult patients with neuromyelitis optica spectrum disorder (NMOSD) who are anti-aquaporin-4 (AQP4) antibody-positive

Uplizna

INEBILIZUMAB· Horizon Therapeutics USA, Inc.Orphan Drug

Uplizna is indicated for for the treatment of neuromyelitis optica spectrum disorder (NMOSD) in adult patients who are anti-aquaporin-4 (AQP4) antibody positive.

Clinical Trials

5 recruitingView all trials with filters →
N/A1 trial
Efficacy and Safety of Transcranial Temporal Interference Stimulation (tTIS) for Neuropathic Pain in Neuromyelitis Optica Spectrum Disorder (NMOSD)
N/A
Actively Recruiting
· Sites: Xi'an, Shaanxi · Age: 1875 yrs
Other4 trials
The Longitudinal CONQUER Study of Rare Neuroimmunologic Disorders
Active
PI: Benjamin M Greenberg, MD (University of Texas Southwestern Medical Center) · Sites: Dallas, Texas · Age: 699 yrs
Biorepository and Registry for Plasma Exchange Patients
Actively Recruiting
· Sites: Iowa City, Iowa · Age: 1299 yrs
Clinical and Imaging Cohort of Neuroinflammation Diseases in China (CLUE)
Actively Recruiting
PI: Yaou Liu, PhD (Beijing Tiantan Hospital) · Sites: Beijing, Beijing Municipality · Age: 1675 yrs
Inebilizumab in Acute Neuromyelitis Optica Spectrum Disorders
Actively Recruiting
PI: Junwei Hao, MD (Xuanwu Hospital, Beijing) · Sites: Beijing, Beijing Municipality · Age: 1899 yrs

Specialists

Showing 25 of 77View all specialists →
DM
Darin T. Okuda, MD
DALLAS, TX
Specialist
PI on 1 active trial
XC
Xiangjun Chen
Specialist
PI on 1 active trial996 Neuromyelitis optica spectrum disorder publications
JZ
Jing Zhang
Specialist
PI on 1 active trial1393 Neuromyelitis optica spectrum disorder publications
MP
Michael Levy, MD, PhD
Boston, Massachusetts
Specialist

Rare Disease Specialist

PI on 9 active trials
PL
Pablo Lopez
Specialist
PI on 1 active trial21 Neuromyelitis optica spectrum disorder publications
LD
Li Guo, Doctor
LAS VEGAS, NV
Specialist
PI on 1 active trial1 Neuromyelitis optica spectrum disorder publication
WD
Wei Qiu, Doctor
RICHLAND, WA
Specialist
PI on 1 active trial
ZD
Zhanhua Liang, Doctor
Specialist
PI on 1 active trial
WD
Wei Lu, Doctor
Specialist
PI on 1 active trial
MD
Meini Zhang, Doctor
Specialist
PI on 1 active trial
FD
Feng Gao, Doctor
Specialist
PI on 1 active trial
HD
Huiyu Feng, Doctor
Specialist
PI on 1 active trial
YD
Yiqi Wang, Doctor
Specialist
PI on 1 active trial
XD
Xinfeng Liu, Doctor
Specialist
PI on 1 active trial
XD
Xiangyang Zhu, Doctor
Specialist
PI on 1 active trial
YD
Yanbing Han, Doctor
Specialist
PI on 1 active trial
CD
Chunming Xie, Doctor
Specialist
PI on 1 active trial
YD
Yuying Zhao, Doctor
Specialist
PI on 1 active trial
ZD
Zunbo Li, Doctor
Specialist
PI on 1 active trial
DD
Daishi Tian, Doctor
Specialist
PI on 1 active trial1 Neuromyelitis optica spectrum disorder publication
JD
Jianglong Tu, Doctor
Specialist
PI on 1 active trial
XD
Xiaoling Luo, Doctor
Specialist
PI on 1 active trial
FD
Feng Wang, Doctor
Specialist
PI on 4 active trials

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Financial Resources

2 resources

HealthWell Foundation — Neuromyelitis optica spectrum disorder

HealthWell Foundation

Neuromyelitis optica spectrum disorder

Verified 4d ago
Foundation Grant
foundation grant
Accepting applications

SOLIRIS

Alexion Pharmaceuticals Inc.

SOLIRIS Patient Support (Alexion OneSource)

Patient Assistance
Manufacturer Program
Accepting applications

Travel Grants

No travel grants are currently matched to Neuromyelitis optica spectrum disorder.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Neuromyelitis optica spectrum disorder

1 articles
NewsRSSApr 22, 2026
My First Symptom of NMOSD
A patient shares their experience with neuromyelitis optica spectrum disorder (NMOSD), a rare disease that affects the nerves in the spinal cord and eyes. They
See all news about Neuromyelitis optica spectrum disorder

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.Which antibody type do I have (AQP4 or MOG), and how does that affect my treatment options?,Which long-term preventive therapy do you recommend for me, and why?,What should I do if I think I am having a new attack — who do I call and where should I go?,How often will I need MRI scans and blood tests to monitor my disease?,Are there clinical trials I might be eligible for?,What rehabilitation services do you recommend to help me recover from my last attack?,How can I manage fatigue, pain, and bladder problems alongside my main treatment?

Common questions about Neuromyelitis optica spectrum disorder

What is Neuromyelitis optica spectrum disorder?

Neuromyelitis optica spectrum disorder (NMOSD), also known as Devic's disease or Devic syndrome, is a rare but serious autoimmune disease that mainly attacks the optic nerves (which connect your eyes to your brain) and the spinal cord. In autoimmune diseases, the body's immune system mistakenly attacks its own healthy tissue. In NMOSD, the immune system produces proteins called antibodies — most often against a protein called AQP4 (aquaporin-4) — that damage the protective covering of nerve fibers, causing inflammation and injury. The most common symptoms are sudden vision loss or pain in one

How is Neuromyelitis optica spectrum disorder inherited?

Neuromyelitis optica spectrum disorder follows a sporadic inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

Are there clinical trials for Neuromyelitis optica spectrum disorder?

Yes — 5 recruiting clinical trials are currently listed for Neuromyelitis optica spectrum disorder on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.

Which specialists treat Neuromyelitis optica spectrum disorder?

25 specialists and care centers treating Neuromyelitis optica spectrum disorder are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.

What treatment and support options exist for Neuromyelitis optica spectrum disorder?

2 patient support programs are currently tracked on UniteRare for Neuromyelitis optica spectrum disorder. See the treatments and support programs sections for copay assistance, eligibility, and contact details.