Clinical trials for Duchenne muscular dystrophy
73 recruiting or active trials synced from ClinicalTrials.gov.
ℹ
Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing data- RECRUITINGN/ANCT07332013Urinary Titin Biomarker in DMDChildren's Hospital of Philadelphia · PI: Sabrina Yum, MD
- RECRUITINGNCT07092540The Baby Duchenne Study: Characterizing Developmental and Clinical Outcomes in the First Three Years in Children With Duchenne Muscular DystrophyUniversity of Rochester
- ENROLLING BY INVITATIONN/ANCT06887491The Effect of Dual-tasking Program on Cognitive and Physical Functions and Independence in Activities of Daily Living in Children With Duchenne Muscular Dystrophy: A Single-blind Randomized Controlled TrialLokman Hekim University
- ACTIVE NOT RECRUITINGPhase 1NCT07347548A Trial to Investigate the Safety and Pharmacokinetics of GRT6019 in Healthy Male ParticipantsGrünenthal GmbH
- ENROLLING BY INVITATIONPhase 2NCT07209332Open-Label Extension Study of WVE-N531 in Patients With Duchenne Muscular DystrophyWave Life Sciences Ltd. · PI: Medical Director, MD
- ACTIVE NOT RECRUITINGEarly Phase 1NCT07282652A Study to Evaluate the Safety and Tolerability of RAG-18 in Pediatric Patients With Duchenne Muscular DystrophyPeking Union Medical College Hospital
- RECRUITINGPhase 2NCT07287189Phase 2 Study of SAT-3247 in Pediatric Ambulatory PatientsSatellos Bioscience, Inc. · PI: Satellos Chief Medical Officer
- ENROLLING BY INVITATIONNCT07435116Duchenne Muscular Dystrophy and the Viscoelastic Properties of Upper Limb MusclesSanko University
- RECRUITINGN/ANCT07127978A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular DystrophyITF Therapeutics LLC
- RECRUITINGPhase 3NCT07160634A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)Solid Biosciences Inc.
- RECRUITINGPhase 1NCT07038824A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 45 Skipping to Evaluate the Safety and Efficacy of ENTR-601-45Entrada Therapeutics, Inc. · PI: Entrada Therapeutics Clinical Trials
- ENROLLING BY INVITATIONPhase 2NCT06867107A Long-term Follow-up Study for Participants That Completed the SAT-3247-CL-101 StudySatellos Bioscience, Inc.
- RECRUITINGEarly Phase 1NCT07188012Safety and Dystrophin Expression of SPOT-mRNA03 in Duchenne Muscular Dystrophy (DMD) PatientsShanghai Siponuoyin Biotechnology Co Ltd · PI: Wang Jiwen
- RECRUITINGPhase 1NCT06817382A Study to Investigate the Safety and Biodistribution of a Single Intrathecal (IT) Injection of INS1201 in Ambulatory Males With Duchenne Muscular Dystrophy (DMD)Insmed Gene Therapy LLC · PI: Insmed Medical Information
- RECRUITINGN/ANCT07129954Fear of Falling in Muscular DystrophyUniversita di Verona · PI: Valentina Varalta, Doctor
- RECRUITINGPhase 1NCT07037862A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 44 Skipping to Evaluate the Safety and Efficacy of ENTR-601-44Entrada Therapeutics, Inc. · PI: Entrada Therapeutics Clinical Trials
- RECRUITINGN/ANCT06402942Gamified Occupational Therapy for Adolescents With Duchenne Muscular DystrophyBaşak Çağla Arslan
- ACTIVE NOT RECRUITINGPhase 2NCT06450639A Study to Assess the Efficacy and Safety of Satralizumab in Duchenne Muscular Dystrophy (DMD)Hoffmann-La Roche · PI: Clinical Trials
- RECRUITINGNCT06925269DMD Voice: Qualitative Interviews With Patients and CaregiversRed Nucleus Enterprise Solutions, LLC · PI: Mindy Leffler, M.Ed.
- RECRUITINGPhase 1NCT06692426Trial of Cell Based Therapy for DMDMasonic Cancer Center, University of Minnesota · PI: Peter Kang, MD
- ENROLLING BY INVITATIONN/ANCT06868784Investigation of the Relationship Between Executive Functions and Occupational Performance of Children With Duchenne Muscular DystrophyLokman Hekim University
- ENROLLING BY INVITATIONN/ANCT06363526Effectiveness of 5-week Digital Respiratory Practice in Children With Duchenne and Becker Muscular Dystrophies.University of Malaga · PI: Rocío Martín-Valero, PhD
- RECRUITINGPhase 2NCT06769633Pharmacokinetics and Safety of Givinostat in DMD Patients Ages From at Least 2 Years to Less Then 6 Years OldItalfarmaco
- RECRUITINGN/ANCT06755138Research on the Relationship Between Scoliosis, Pain, Quality of Life, and Trunk Muscle Compensation Patterns Among Patients with Duchenne Muscular Dystrophy.Seoul National University Hospital · PI: Sungbae Jo Research professor, Ph. D
- RECRUITINGNCT06773988Follow-up of NIV At Home in Patients with Duchenne Muscular DystrophyUniversitaire Ziekenhuizen KU Leuven
- ACTIVE NOT RECRUITINGPhase 4NCT06713135A Study on Safety and Effectiveness of Long-term Treatment With Vamorolone in Boys With Duchenne Muscular DystrophySanthera Pharmaceuticals · PI: A Child, MD
- RECRUITINGEarly Phase 1NCT06900049Evaluation of the Safety, Tolerability, and Efficacy of LE051 in Patients With Duchenne Muscular DystrophyShanghai Jiao Tong University School of Medicine
- RECRUITINGNCT06564974Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMITCatalyst Pharmaceuticals, Inc. · PI: William Andrews, MD
- ACTIVE NOT RECRUITINGPHASE1, PHASE2NCT06053814NS-050/NCNP-03 in Boys With DMD (Meteor50)NS Pharma, Inc.
- RECRUITINGNCT06574919Clinical and Functional Assessment of Patients With Inherited Non-Duchenne Myopathies in Sohag University HospitalSohag University
- RECRUITINGEarly Phase 1NCT06641895Evaluation of the Safety and Efficacy of BBM-D101 to Treat Patients with Duchenne Muscular DystrophyShanghai Jiao Tong University School of Medicine · PI: Jiwen Wang
- RECRUITINGNCT06093100Wearable Technology to Evaluate Hyperglycemia and HRV in DMD - Longitudinal AimVanderbilt University Medical Center · PI: Jaclyn Tamaroff, MD
- ACTIVE NOT RECRUITINGEarly Phase 1NCT06392724A Study to Evaluate the Safety and Tolerability of GEN6050X in Duchenne Muscular Dystrophy.Peking Union Medical College Hospital
- RECRUITINGN/ANCT06861270Estimation of Non-Reimbursable Costs for Patients With Duchenne Muscular Dystrophy in FranceAssistance Publique - Hôpitaux de Paris · PI: Isabelle Durand-Zaleski, Professor
- ENROLLING BY INVITATIONN/ANCT06491927Long Term Follow-up for RGX-202REGENXBIO Inc.
- RECRUITINGPHASE1, PHASE2NCT06138639A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)Solid Biosciences Inc. · PI: Solid Bio Clinical Trials
- ACTIVE NOT RECRUITINGPhase 2NCT06100887Phase 2 Study of EDG-5506 in Children and Adolescents With Duchenne Muscular Dystrophy Previously Treated With Gene TherapyEdgewise Therapeutics, Inc.
- RECRUITINGNCT06124196Wearable Technology to Evaluate Hyperglycemia and HRV in DMDVanderbilt University Medical Center · PI: Jaclyn Tamaroff, MD
- RECRUITINGPhase 2NCT05996003NS-089/NCNP-02-201 in Boys With Duchenne Muscular Dystrophy (DMD)NS Pharma, Inc. · PI: Trial info
- RECRUITINGPhase 3NCT05933057Efficacy, Safety and Tolerability of Givinostat in Non-ambulant Patients With Duchenne Muscular DystrophyItalfarmaco
- ENROLLING BY INVITATIONN/ANCT06270719An Observational Study Comparing Delandistrogene Moxeparvovec With Standard of Care in Participants With Duchenne Muscular DystrophySarepta Therapeutics, Inc.
- ACTIVE NOT RECRUITINGPhase 1NCT06114056A Clinical Study Evaluating the Safety, Tolerability, and Initial Efficacy of Single Intravenous Infusion of JWK007 in Patients With Duchenne Muscular Dystrophy (DMD)West China Hospital · PI: Xingchen Xingchen, Ph.D
- ACTIVE NOT RECRUITINGPhase 2NCT06244082Ph2 Open-label Study of AOC 1044 in Duchenne Muscular Dystrophy Participants With Mutations Amenable to Exon44 SkippingAvidity Biosciences, Inc. · PI: Carmen Castrillo, MD
- RECRUITINGPhase 1NCT06280209A Phase 1/2 Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of BMN 351 in Participants With Duchenne Muscular DystrophyBioMarin Pharmaceutical
- ACTIVE NOT RECRUITINGPhase 2NCT06128564A Gene Delivery Study to Evaluate the Safety and Expression of Delandistrogene Moxeparvovec in Participants Under the Age of Four With Duchenne Muscular Dystrophy (DMD)Hoffmann-La Roche · PI: Clinical Trials
- ENROLLING BY INVITATIONPhase 3NCT05967351A Long-term Follow-up Study of Participants Who Received Delandistrogene Moxeparvovec (SRP-9001) in a Previous Clinical StudySarepta Therapeutics, Inc.
- ENROLLING BY INVITATIONN/ANCT06412328Psychoeducation Program for Parents of Children with Duchenne Muscular DystrophyLokman Hekim University
- ACTIVE NOT RECRUITINGPhase 3NCT05881408A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Non-Ambulatory and Ambulatory Participants With Duchenne Muscular Dystrophy (DMD)Sarepta Therapeutics, Inc. · PI: Medical Director
- RECRUITINGPHASE2, PHASE3NCT05693142AFFINITY DUCHENNE: RGX-202 Gene Therapy in Participants With Duchenne Muscular Dystrophy (DMD)REGENXBIO Inc.
- RECRUITINGNCT05683379AFFINITY BEYOND: Anti-AAV8 Antibody Assessment Study of Males With DMDREGENXBIO Inc.
- ACTIVE NOT RECRUITINGN/ANCT06445985Hydrotherapy in Duchenne Muscular Dystrophy (DMD)Lancashire Teaching Hospitals NHS Foundation Trust · PI: Christian De Goede
- ACTIVE NOT RECRUITINGPhase 2NCT05540860A Study of EDG-5506 in Children With Duchenne Muscular Dystrophy (LYNX)Edgewise Therapeutics, Inc.
- RECRUITINGN/ANCT06366815phenotypeS in Non Ambulant Duchenne Muscular DystrophyFondazione Policlinico Universitario Agostino Gemelli IRCCS · PI: Marika Pane
- ACTIVE NOT RECRUITINGPHASE1, PHASE2NCT05524883Safety, Tolerability, Pharmacodynamic, Efficacy, and Pharmacokinetic Study of DYNE-251 in Participants With Duchenne Muscular Dystrophy Amenable to Exon 51 SkippingDyne Therapeutics
- ACTIVE NOT RECRUITINGPhase 2NCT05195775Tadalafil as Adjuvant Therapy for DMDUniversity of Florida · PI: Tanja Taivassalo
- RECRUITINGPhase 1NCT04906460Open-label Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy (FORWARD-53)Wave Life Sciences Ltd. · PI: Medical Director, MD
- RECRUITINGN/ANCT04972604CureDuchenne Link®: A Resource for ResearchCureDuchenne · PI: Debra Miller
- ACTIVE NOT RECRUITINGPhase 2NCT05135663Extension Study of NS-089/NCNP-02 in DMDNippon Shinyaku Co., Ltd.
- ACTIVE NOT RECRUITINGPhase 4NCT04687020Long-term Use of Viltolarsen in Boys With Duchenne Muscular Dystrophy in Clinical Practice (VILT-502)NS Pharma, Inc.
- RECRUITINGPhase 4NCT05412394Once Weekly Infant Corticosteroid Trial for DMDAnne M. Connolly · PI: Anne Connolly, MD
- ACTIVE NOT RECRUITINGPhase 3NCT04281485Study to Evaluate the Safety and Efficacy of PF-06939926 for the Treatment of Duchenne Muscular DystrophyPfizer · PI: Pfizer CT.gov Call Center
- ACTIVE NOT RECRUITINGPhase 3NCT04587908A Phase 3 Study of TAS-205 in Patients With Duchenne Muscular Dystrophy（REACH-DMD）Taiho Pharmaceutical Co., Ltd. · PI: Taiho Pharmaceutical Co., Ltd.
- RECRUITINGN/ANCT01484678Magnetic Resonance Imaging and Biomarkers for Muscular DystrophyUniversity of Florida · PI: William Rooney, PhD
- ACTIVE NOT RECRUITINGPhase 2NCT04428476Open-label Extension of the HOPE-2 TrialCapricor Inc. · PI: Craig McDonald, MD
- RECRUITINGN/ANCT05982119Assessments in Patients With Muscular Pathology and in Control Subjects : The ActiLiège Next StudyCentre Hospitalier Universitaire de Liege
- ACTIVE NOT RECRUITINGPhase 2NCT04433234Long-term, Extension Study of DS-5141b in Patients With Duchenne Muscular DystrophyDaiichi Sankyo Co., Ltd. · PI: Clinical Study Leader
- RECRUITINGN/ANCT03882827Natural History of Duchenne Muscular DystrophyGenethon · PI: Francesco MUNTONI, Pr
- RECRUITINGNCT05016908Extracellular RNA Biomarkers of Duchenne Muscular DystrophyMassachusetts General Hospital · PI: Thurman M. Wheeler, MD
- RECRUITINGNCT04012671A Registered Cohort Study on Duchenne Muscular DystrophyNing Wang, MD., PhD.
- ENROLLING BY INVITATIONN/ANCT06606340A Long-term Observational Study Evaluating Eteplirsen, Golodirsen, or Casimersen in Routine Clinical PracticeSarepta Therapeutics, Inc.
- ACTIVE NOT RECRUITINGPhase 1NCT03368742Microdystrophin Gene Transfer Study in Adolescents and Children With DMDSolid Biosciences Inc. · PI: Solid Bio Clinical Trials
- RECRUITINGPHASE2, PHASE3NCT03373968Givinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability StudyItalfarmaco
- ACTIVE NOT RECRUITINGNCT01633866Pediatric Radio Frequency Coils GenericChildren's Hospital Medical Center, Cincinnati · PI: Charles Dumoulin, PhD