Active, not recruitingPhase 3NCT05881408
A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Non-Ambulatory and Ambulatory Participants With Duchenne Muscular Dystrophy (DMD)
Studying Duchenne muscular dystrophy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Sarepta Therapeutics, Inc.
- Principal Investigator
- Medical DirectorSarepta Therapeutics, Inc.
- Intervention
- delandistrogene moxeparvovec(genetic)
- Enrollment
- 148 enrolled
- Eligibility
- MALE
- Timeline
- 2023 – 2027
Study locations (20)
- Arkansas Children's Hospital, Little Rock, Arkansas, United States
- Lucile Packard Children's Hospital Stanford, Palo Alto, California, United States
- University of California at Davis Medical Center, Sacramento, California, United States
- Rady Children's Hospital-San Diego, San Diego, California, United States
- University of Florida, UF Health Center for Pediatric Neuromuscular and Rare Diseases, Gainesville, Florida, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States
- The Johns Hopkins Hospital, Charlotte R. Bloomberg Children's Center, Pediatric Clinical Research Unit, Baltimore, Maryland, United States
- Boston Children's Hospital, Boston, Massachusetts, United States
- Washington University of St. Louis, St. Louis Children's Hospital, St Louis, Missouri, United States
- University of Rochester, Department of Neurology, Rochester, New York, United States
- Lenox Baker Children's Hospital (Duke University), Durham, North Carolina, United States
- Nationwide Children's Hospital, Columbus, Ohio, United States
- Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
- Children's Hospital of the King's Daughters, Norfolk, Virginia, United States
- The Children's Hospital at Westmead, Westmead, New South Wales, Australia
- +5 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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