Active, not recruitingPHASE1, PHASE2NCT05524883
Safety, Tolerability, Pharmacodynamic, Efficacy, and Pharmacokinetic Study of DYNE-251 in Participants With Duchenne Muscular Dystrophy Amenable to Exon 51 Skipping
Studying Duchenne muscular dystrophy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Dyne Therapeutics
- Intervention
- DYNE-251(drug)
- Enrollment
- 86 enrolled
- Eligibility
- 4-16 years · MALE
- Timeline
- 2022 – 2029
Study locations (30)
- University of California San Diego, La Jolla, California, United States
- UCLA University California of Los Angeles, Los Angeles, California, United States
- Children's Hospital Colorado, Aurora, Colorado, United States
- Rare Disease Research, LLC, Atlanta, Georgia, United States
- UMass Memorial Medical Center, Worcester, Massachusetts, United States
- Nationwide Children's Hospital, Columbus, Ohio, United States
- Shriners Hospitals for Children Portland, Portland, Oregon, United States
- Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
- UPMC Children's Hospital of Pittsburgh, Pittsburgh, Pennsylvania, United States
- University of Utah - PPDS, Salt Lake City, Utah, United States
- Virginia Commonwealth University, Richmond, Virginia, United States
- Children's Hospital at Westmead, Westmead, New South Wales, Australia
- Murdoch Children's Research Institute, Parkville, Victoria, Australia
- UZ Gent, Ghent, Belgium
- UZ Leuven, Leuven, Belgium
- +15 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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