Active, not recruitingPhase 2NCT06128564
A Gene Delivery Study to Evaluate the Safety and Expression of Delandistrogene Moxeparvovec in Participants Under the Age of Four With Duchenne Muscular Dystrophy (DMD)
Studying Duchenne muscular dystrophy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Hoffmann-La Roche
- Principal Investigator
- Clinical TrialsHoffmann-La Roche
- Intervention
- delandistrogene moxeparvovec(genetic)
- Enrollment
- 13 enrolled
- Eligibility
- 2-3 years · MALE
- Timeline
- 2023 – 2030
Study locations (7)
- Chr de La Citadelle, Liège, Belgium
- Hôpital Necker-Enfants Malades, Paris, France
- Universitätsklinikum Essen, Essen, Germany
- PU A. Gemelli, Università Cattolica del Sacro Cuore, Rome, Lazio, Italy
- Hospital Sant Joan De Deu, Esplugues de Llobregas, Barcelona, Spain
- Great Ormond Street Hospital for Children, London, United Kingdom
- John Radcliffe Hospital, Oxford, United Kingdom
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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