Specialists for Duchenne muscular dystrophy
56 physicians and care centers identified from ClinicalTrials.gov trial PIs, PubMed publications, and the NPPES NPI registry.
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Specialists are identified from ClinicalTrials.gov principal investigators, PubMed publications, and the NPI registry, then ranked through an automated scoring pipeline.
Report missing data- Francesco Muntoni, ProfessorRare Disease SpecialistUCL GOS Institute of Child HealthLondonQC-verified
- Tanja TaivassaloRare Disease SpecialistUniversity of FloridaGainesville, FloridaQC-verified
- Rocío Martín-Valero, PhDRare Disease SpecialistRocío Martín-ValeroMálagaQC-verified
- Debra MillerRare Disease SpecialistArkansas Children's HospitalLittle Rock, ArkansasQC-verified 108
- William Rooney, PhDRare Disease SpecialistUniversity of FloridaGainesville, FloridaQC-verified
- Sungbae Jo Research professor, Ph. DRare Disease SpecialistSeoul National University HospitalSeoulQC-verified 5
- Isabelle Durand-Zaleski, ProfessorRare Disease SpecialistAP-HP Hôtel DieuParisQC-verified PI×2
- Christian De GoedeRare Disease SpecialistLancashire Teaching Hospitals NHS Foundation TrustPreston, LancashireQC-verified 5
- Valentina Varalta, DoctorRare Disease SpecialistAzienda Ospedaliera Universitaria Integrata Verona - UOC di NeuroriabilitazioneVerona, veronaQC-verified
- Francesco MUNTONI, PrRare Disease SpecialistCentre Hospitalier Universitaire BrugmannBrusselsQC-verified
- Insmed Medical InformationRare Disease SpecialistUSA012Little Rock, ArkansasQC-verified
- Jiwen WangRare Disease SpecialistShanghai Children's Medical Center Affiliated to Shanghai Jiao Tong University School of MedicineShanghai, Shanghai Municipality1862
- Marika PaneRare Disease SpecialistIRCCS Eugenio Medea - Ass. "La Nostra Famiglia"Bosisio Parini, LcPI×2 28
- Craig McDonald, MDRare Disease SpecialistPhoenix Children's HospitalPhoenix, ArizonaPI×4
- Giuseppe Vita, MD, LCSWRare Disease / Clinical ResearchDepartment of Neuroscience, University of MessinaNORTH BRANFORD, CTPI×1
- Ronald G Victor, MDRare Disease / Clinical ResearchCedars-Sinai Medical CenterPI×5
- Satellos Chief Medical OfficerRare Disease SpecialistSatellos Bioscience, Inc.Los Angeles, CaliforniaPI×1 1
- Anne Connolly, MDRare Disease / Clinical ResearchNationwide Children's HospitalPI×1
- Vinay PenematsaRare Disease / Clinical ResearchPTC Therapeutics, Inc.PI×1
- Brenda Wong, MDRare Disease / Clinical ResearchChildren's Hospital Medical Center, CincinnatiPI×2
- Francesco Bibbiani, MDRare Disease / Clinical ResearchPTC Therapeutics, Inc.PI×4
- Mark AwadallaRare Disease / Clinical ResearchCapricor Inc.PI×2
- Laurent Servais, MD, PhDRare Disease SpecialistUniversity of LiegeLiègePI×2
- Tamara Dangouloff, PhDRare Disease / Clinical ResearchUniversity of LiegePI×1
- Peter Kang, MDRare Disease SpecialistUniversity of MinnesotaMinneapolis, MinnesotaPI×2
- A Child, MDRare Disease / Clinical ResearchLeeds Teaching HospitalPI×1
- Seward Rutkove, MD, MDBeth Israel Deaconess Medical CenterPI×3
- Susan Sparks, M.D., Ph.D.Rare Disease / Clinical ResearchLevine Children's HospitalPI×1
- Caroline Hugeron, MDRare Disease / Clinical ResearchHôpital Raymond PoincaréPI×1
- Carolina Tesi-Rocha, M.D.Rare Disease / Clinical ResearchCooperative International Neuromuscular Research GroupPI×1
- Marielle Contesse, PhDRare Disease / Clinical ResearchEmmes Endpoint SolutionsPI×1
- Magnhild Rasmussen, Dr.med.Rare Disease / Clinical ResearchOslo University HospitalPI×1
- Basil Darras, MD, M.DRare Disease / Clinical ResearchBoston Children's HospitalBOSTON, MAPI×1
- Serenay ZorluRare Disease / Clinical ResearchMedipol UniversityPI×1
- Anne Connolly, M.D.Rare Disease / Clinical ResearchWashington University School of MedicinePI×1
- Subha V Raman, MD, MSEE, M.DRare Disease / Clinical ResearchOhio State UniversitySARASOTA, FLPI×1
- Carmen Castrillo, MDRare Disease SpecialistArkansas Children's HospitalLittle Rock, ArkansasPI×2
- Trial infoRare Disease SpecialistChildren's Hospital ColoradoAurora, Colorado3
- Xingchen Xingchen, Ph.DRare Disease SpecialistWest China Hospital, Sichuan UniversityChengdu, Sichuan
- JungHyun Kim, profRare Disease SpecialistSeoul National University HospitalSeoul, Jongno
- kristina m casteels, MDRare Disease / Clinical ResearchUniversitaire Ziekenhuizen KU LeuvenPI×1
- Yi DaiRare Disease / Clinical ResearchPeking Union Medical College HospitalPI×1
- Nathalie GoemansRare Disease / Clinical ResearchUniversity Hospitals LeuvenQC-verified 2
- Craig M Zaidman, MDRare Disease / Clinical ResearchWashington University School of MedicineSAINT LOUIS, MO2
- Jonathan H Soslow, MDRare Disease / Clinical ResearchVanderbilt University Medical CenterNASHVILLE, TN2
- Eleonora S D'AmbrosioRare Disease / Clinical ResearchAbigail Wexner Research InstituteOH2
- Toshifumi YokotaRare Disease / Clinical ResearchUniversity of Alberta2
- Güllü Aydın, R.ARare Disease / Clinical ResearchHacettepe UniversityPI×2
- Ajay Kaul, M.DRare Disease / Clinical ResearchChildren's Hospital Medical CenterCINCINNATI, OHPI×1
- Daniel J BerlauRare Disease / Clinical ResearchRegis University2
- Alexander P MurphyRare Disease / Clinical ResearchRoche Products Ltd2
- Michela GuglieriRare Disease / Clinical ResearchJohn Walton Muscular Dystrophy Research CentrePI×1 2
- Kevin Flanigan, MDPediatric Neurology / DMD Gene TherapyNationwide Children's HospitalColumbus, OHQC-verified
- Thomas Voit, MD, PhDPediatric Neurology / Neuromuscular DiseaseUCL Great Ormond Street Institute of Child HealthLondonQC-verified
- Paula R Clemens, M.D.Neurology / Duchenne Muscular DystrophyUniversity of PittsburghPittsburgh, PAQC-verified
- Gunnar Buyse, MD, PhD.Pediatric Neurology / Duchenne Muscular DystrophyUniversity Hospitals Leuven (UZ Leuven)LeuvenQC-verified