Diffuse large B-cell lymphoma of the central nervous system

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2Active trials27Specialists8Treatment centers

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UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Diffuse large B-cell lymphoma of the central nervous system (also called primary CNS lymphoma or PCNSL) is a rare and aggressive type of cancer that starts in the brain, spinal cord, eyes, or the membranes surrounding the brain (meninges). It develops from a type of white blood cell called B-lymphocytes, which are part of the immune system. Unlike lymphomas that start elsewhere in the body and later spread to the brain, this cancer begins directly in the central nervous system. Common symptoms include headaches, confusion, memory problems, personality changes, weakness on one side of the body, seizures, and vision changes. Some patients experience difficulty speaking or problems with balance and coordination. Symptoms often develop over weeks to months and can be mistaken for other brain conditions like stroke or dementia. This disease is more common in people with weakened immune systems, such as those with HIV/AIDS or organ transplant recipients on immunosuppressive drugs, but it also occurs in people with normal immune systems, typically in older adults. Treatment usually involves high-dose methotrexate-based chemotherapy, sometimes combined with other drugs and occasionally followed by radiation therapy or stem cell transplant. While the disease is serious, advances in treatment have improved outcomes significantly over the past two decades. Early diagnosis and prompt treatment are important for the best possible results.

Also known as:

Key symptoms:

Persistent headachesConfusion or difficulty thinking clearlyMemory problemsPersonality or behavior changesWeakness on one side of the bodySeizuresBlurred or double visionDifficulty speaking or finding wordsProblems with balance or coordinationNausea and vomitingFatigue and drowsinessEye floaters or vision lossNumbness or tingling in limbsDifficulty walking

Inheritance

Sporadic

Usually appears on its own, not inherited from a parent

Age of Onset

Adult

Begins in adulthood (age 18 or older)

Orphanet ↗NORD ↗

FDA & Trial Timeline

4 events
Mar 2025Cord Blood-derived CAR-NK Cells Targeting CD19 for Refractory/Relapsed Central Nervous System Lymphoma

Second Affiliated Hospital, School of Medicine, Zhejiang University — PHASE1

TrialENROLLING BY INVITATION
Jan 2025High-dose Methotrexate Combined with Thiotepa and Zanubrutinib in the Treatment of Newly Diagnosed PCNSL (MTZ)

Sun Yat-sen University — PHASE2

TrialNOT YET RECRUITING
May 2021DALY II USA/ MB-CART2019.1 for DLBCL

Miltenyi Biomedicine GmbH — PHASE2

TrialRECRUITING
Dec 2017A Phase I/II Study to Evaluate the Safety of Cellular Immunotherapy Using Autologous T Cells Engineered to Express a CD20-Specific Chimeric Antigen Receptor for Patients With Relapsed or Refractory B Cell Non-Hodgkin Lymphomas

Fred Hutchinson Cancer Center — PHASE1, PHASE2

TrialACTIVE NOT RECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

No FDA-approved treatments are currently listed for Diffuse large B-cell lymphoma of the central nervous system.

2 clinical trialsare actively recruiting — trials can provide access to cutting-edge therapies.

View clinical trials →

Clinical Trials

2 recruitingView all trials with filters →
Phase 21 trial
DALY II USA/ MB-CART2019.1 for DLBCL
Phase 2
Actively Recruiting
PI: Johanna Theruvath, MD (Miltenyi Biomedicine GmbH) · Sites: Gilbert, Arizona; Phoenix, Arizona +23 more · Age: 1899 yrs

Specialists

Showing 25 of 27View all specialists →
JM
Johanna Theruvath, MD
Specialist
PI on 1 active trial
AA
Alvaro J Alencar
MIAMI, FL
Specialist
PI on 1 active trial3 Diffuse large B-cell lymphoma of the central nervous system publications
MR
Mark Ratain
CHICAGO, IL
Specialist
PI on 1 active trial2 Diffuse large B-cell lymphoma of the central nervous system publications
SA
Stephen M Ansell
ROCHESTER, MN
Specialist
PI on 1 active trial5 Diffuse large B-cell lymphoma of the central nervous system publications
TM
Tae Min Kim, PhD., M.D.
Specialist
PI on 1 active trial
SM
Shivaani Kummar, MD
PORTLAND, OR
Specialist
PI on 5 active trials
CM
Caspian Oliai, MD
LOS ANGELES, CA
Specialist
PI on 1 active trial
SM
Scot C. Remick, MD
SCARBOROUGH, ME
Specialist
PI on 9 active trials
SK
Shaji Kumar
Anchorage, Alaska
Specialist

Rare Disease Specialist

PI on 7 active trials
JM
Jeffrey J. Raizer, MD
CHICAGO, IL
Specialist
PI on 7 active trials
PM
Paul Rubinstein, MD
PALO ALTO, CA
Specialist
PI on 1 active trial
GM
Gary Schiller, MD
LOS ANGELES, CA
Specialist
PI on 1 active trial1 Diffuse large B-cell lymphoma of the central nervous system publication
SM
Stefano Tarantolo, MD
OMAHA, NE
Specialist
PI on 1 active trial
EM
Elizabeth Budde, MD
CHICAGO, IL
Specialist
PI on 1 active trial
LM
Lasika Seneviratne, MD
LOS ANGELES, CA
Specialist
PI on 1 active trial
SM
Salil Goorha, MD
MEMPHIS, TN
Specialist
PI on 1 active trial
TM
Tamra Slone, MD
WILMINGTON, OH
Specialist
PI on 1 active trial
RP
Robert Z. Orlowski, MD, PhD
HOUSTON, TX
Specialist
PI on 1 active trial
EM
Elizabeth C. Dees, MD
CHAPEL HILL, NC
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Diffuse large B-cell lymphoma of the central nervous system.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Diffuse large B-cell lymphoma of the central nervous system

Disease timeline:

New recruiting trial: DALY II USA/ MB-CART2019.1 for DLBCL

A new clinical trial is recruiting patients for Diffuse large B-cell lymphoma of the central nervous system

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What is the exact location and extent of the lymphoma in my brain, and has it spread to my eyes or spinal fluid?,What chemotherapy regimen do you recommend for me, and what are the expected side effects?,Am I a candidate for autologous stem cell transplant as consolidation therapy?,What is the risk of cognitive decline from the proposed treatment, and how can it be minimized?,How will you monitor whether the treatment is working, and how often will I need MRI scans?,What happens if the lymphoma comes back after treatment — what are my options at that point?,Are there any clinical trials available that I should consider?

Common questions about Diffuse large B-cell lymphoma of the central nervous system

What is Diffuse large B-cell lymphoma of the central nervous system?

Diffuse large B-cell lymphoma of the central nervous system (also called primary CNS lymphoma or PCNSL) is a rare and aggressive type of cancer that starts in the brain, spinal cord, eyes, or the membranes surrounding the brain (meninges). It develops from a type of white blood cell called B-lymphocytes, which are part of the immune system. Unlike lymphomas that start elsewhere in the body and later spread to the brain, this cancer begins directly in the central nervous system. Common symptoms include headaches, confusion, memory problems, personality changes, weakness on one side of the body

How is Diffuse large B-cell lymphoma of the central nervous system inherited?

Diffuse large B-cell lymphoma of the central nervous system follows a sporadic inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Diffuse large B-cell lymphoma of the central nervous system typically begin?

Typical onset of Diffuse large B-cell lymphoma of the central nervous system is adult. Age of onset can vary across affected individuals.

Are there clinical trials for Diffuse large B-cell lymphoma of the central nervous system?

Yes — 2 recruiting clinical trials are currently listed for Diffuse large B-cell lymphoma of the central nervous system on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.

Which specialists treat Diffuse large B-cell lymphoma of the central nervous system?

25 specialists and care centers treating Diffuse large B-cell lymphoma of the central nervous system are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.