Cancer-associated retinopathy

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1FDA treatments2Active trials27Specialists8Treatment centers

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UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Cancer-associated retinopathy (CAR) is a rare condition where the immune system accidentally attacks the light-sensing cells in the back of the eye (the retina) in people who have cancer elsewhere in the body. It is also sometimes called paraneoplastic retinopathy or paraneoplastic visual syndrome. The body produces antibodies to fight the cancer, but these same antibodies mistakenly target proteins in the retina, causing damage to the cells that allow you to see. The most common cancers linked to CAR are small cell lung cancer, breast cancer, gynecological cancers (such as ovarian and cervical cancer), and colon cancer. Symptoms often appear before the cancer is even diagnosed, which makes CAR an important warning sign that something else may be going on in the body. The main symptoms include progressive vision loss, difficulty seeing in dim light (night blindness), sensitivity to light, and seeing flashing lights or shimmering effects. Treatment focuses on managing the immune response and treating the underlying cancer. There is no cure, but immunosuppressive therapies — medicines that calm the immune system — can sometimes slow vision loss. Early detection is very important because the damage to the retina can become permanent if not addressed quickly.

Also known as:

Key symptoms:

Gradual or sudden loss of vision in one or both eyesDifficulty seeing in low light or at night (night blindness)Sensitivity to bright light (photophobia)Seeing flashing lights, shimmering, or flickering (photopsias)Loss of color visionBlind spots or missing areas in the field of visionBlurry or hazy visionNarrowing of the visual field (tunnel vision)Difficulty adjusting from bright to dark environmentsEye fatigue or discomfort

Clinical phenotype terms (36)— hover any for plain English
Malignant genitourinary tract tumorHP:0006758Adult-onset night blindnessHP:0007830ERG: Reduced dark-adapted b-wave amplitudeHP:0007984Progressive visual field defectsHP:0007987Small cell lung carcinomaHP:0030357PhotopsiaHP:0030786Female reproductive system neoplasmHP:0033020Neoplasm of the breastHP:0100013Anti-recoverin antibody positivityHP:6000882Central scotomaHP:0000603Retinal atrophyHP:0001105Constriction of peripheral visual fieldHP:0001133Hematological neoplasmHP:0004377DyschromatopsiaHP:0007641Retinal pigment epithelial atrophyHP:0007722
Inheritance

Sporadic

Usually appears on its own, not inherited from a parent

Age of Onset

Adult

Begins in adulthood (age 18 or older)

Orphanet ↗NORD ↗

FDA & Trial Timeline

10 events
Mar 2026A Long-term Follow-up Study of Patients With ARD103 CAR-T Cell Therapies

ARCE Therapeutics, Inc.

TrialNOT YET RECRUITING
Nov 2025A Study to Investigate the Safety and Preliminary Efficacy of ALLO-329, an Allogeneic CAR T-cell Therapy, in Adults With Autoimmune Disease

Allogene Therapeutics — PHASE1

TrialRECRUITING
Sep 2025Non-Pharmacological Interventions for Neurotoxicity in Hematologic Patients Receiving CAR-T Therapy

Instituto de Investigacion Sanitaria INCLIVA — NA

TrialRECRUITING
Sep 2025Clinical Study of BCMA/CD70-targeted CAR-T Therapy for Refractory Pediatric Rheumatic Diseases

Chongqing Precision Biotech Co., Ltd — PHASE1

TrialRECRUITING
Aug 2025Anti CD19/BCMA CAR Gene Therapy for Autoimmune Diseases

Anhui Provincial Hospital — NA

TrialRECRUITING
Jul 2025Temporal Characterization of Extracellular Vesicles During Cellular Therapy Using CAR-T Cells and During the Occurrence of Immune Effector Cell-Associated Neurotoxicity Syndrome

Centre Hospitalier Universitaire de Saint Etienne — PHASE4

TrialRECRUITING
Jun 2025Adjunctive Methylene Blue for Immunotherapy-related CRS and ICANS: Phase I Study

Institute of Hematology & Blood Diseases Hospital, China — PHASE1

TrialRECRUITING
Jun 2025Intrathecal Cytarabine, Methotrexate, and Hydrocortisone for the Prevention of High-Grade Chimeric Antigen Receptor T-Cell-Associated Neurotoxicity Syndrome

OHSU Knight Cancer Institute — PHASE2

TrialRECRUITING
May 2025Clinical Study of ARD103 CAR-T Therapy for Patients With R/R AML or MDS

ARCE Therapeutics, Inc. — PHASE1, PHASE2

TrialRECRUITING
May 2025Study of Therapeutic Efficacy of Anti-CD19 CAR-T Cell Therapy in Patients With MDR-SRNS

The Children's Hospital of Zhejiang University School of Medicine — PHASE1

TrialRECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

1 available

GAVRETO�

pralsetinib· Rigel Pharmaceuticals, Inc.■ Boxed WarningAccelerated Approval
GAVRETO is indicated for the treatment of adult and pediatric patients 12 years of age and older with advanced or metastatic RET fusion-positive thyroid cancer who require systemic therapy and who are

GAVRETO is indicated for the treatment of adult and pediatric patients 12 years of age and older with advanced or metastatic RET fusion-positive thyroid cancer who require systemic therapy and who are radioactive iodine-refractory (if radioactive iodine is appropriate).

Clinical Trials

2 recruitingView all trials with filters →
Phase 12 trials
ALaCART-B: Acute Leukemia and Chimeric Antigen Receptor-T Cell Therapy for B-lymphoblastic Leukemia.
Phase 1
Actively Recruiting
PI: Allen Yeoh, M.D (National University Hospital, Singapore) · Sites: Singapore · Age: 080 yrs
GPC3-CAR-T Cells for Immunotherapy of Cancer With GPC3 Expression
Phase 1
Actively Recruiting
PI: Zhenfeng Zhang, MD,PhD (Second Affiliated Hospital of Guangzhou Medical Un) · Sites: Guangzhou, Guangdong; Guangzhou, Guangdong · Age: 1875 yrs

Specialists

Showing 25 of 27View all specialists →
HG
Hashem Ghoraba
CLEVELAND, OH
Specialist
1 Cancer-associated retinopathy publication
IC
Irini Chatziralli
Specialist
2 Cancer-associated retinopathy publications
CO
Christopher Or
Specialist
1 Cancer-associated retinopathy publication
KM
Kapil Mishra
IRVINE, CA
Specialist
1 Cancer-associated retinopathy publication
AA
Amir Akhavanrezayat
Specialist
1 Cancer-associated retinopathy publication
SP
Sungwho Park
Specialist
1 Cancer-associated retinopathy publication
NT
Ngoc Than
Specialist
1 Cancer-associated retinopathy publication
LL
Loh-Shan Leung
STANFORD, CA
Specialist
1 Cancer-associated retinopathy publication
SS
Steven Sanislo
STANFORD, CA
Specialist
1 Cancer-associated retinopathy publication
QN
Quan Dong Nguyen
Specialist
1 Cancer-associated retinopathy publication
KG
Karel Goyvaerts
Specialist
1 Cancer-associated retinopathy publication
TC
Tanja Coeckelbergh
Specialist
1 Cancer-associated retinopathy publication
PS
Pieter-Paul Schauwvlieghe
Specialist
1 Cancer-associated retinopathy publication
IK
Irmak Karaca
NEW YORK, NY
Specialist
2 Cancer-associated retinopathy publications
PT
Panagiotis Theodossiadis
Specialist
2 Cancer-associated retinopathy publications
HM
He Huang, MD
Hanzhou, Zhejiang
Specialist

Rare Disease Specialist

PI on 11 active trials
JP
Jianhua Mao, PhD
Shanghai, Shanghai Municipality
Specialist

Rare Disease Specialist

PI on 3 active trials
PM
Pablo Tebas, MD
PHILADELPHIA, PA
Specialist
PI on 5 active trials
MM
Miles Prince, MD
Specialist
PI on 2 active trials
KJ
Kwangsic Joo
Specialist
2 Cancer-associated retinopathy publications
FZ
Flora Zagouri
Specialist
2 Cancer-associated retinopathy publications
AM
Allen Yeoh, M.D
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Cancer-associated retinopathy.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Cancer-associated retinopathy

Disease timeline:

New recruiting trial: Adjunctive Methylene Blue for Immunotherapy-related CRS and ICANS: Phase I Study

A new clinical trial is recruiting patients for Cancer-associated retinopathy

New recruiting trial: Clinical Study of ARD103 CAR-T Therapy for Patients With R/R AML or MDS

A new clinical trial is recruiting patients for Cancer-associated retinopathy

New recruiting trial: CD7 CAR-T Cell Sequential Allo-HSCT for Non-malignant Blood and Immune System Diseases

A new clinical trial is recruiting patients for Cancer-associated retinopathy

New recruiting trial: Chimeric Antigen Receptor Natural Killer Cell Therapy for High-risk Lymphoma Patients With Primary Sjogren's Syndrome

A new clinical trial is recruiting patients for Cancer-associated retinopathy

New recruiting trial: Anti CD19/BCMA CAR Gene Therapy for Autoimmune Diseases

A new clinical trial is recruiting patients for Cancer-associated retinopathy

New recruiting trial: A Study of OL-CD19-GDT in Relapsed/ Refractory Autoimmune Diseases

A new clinical trial is recruiting patients for Cancer-associated retinopathy

New recruiting trial: Phase 2 Study of Rapcabtagene Autoleucel in Myositis

A new clinical trial is recruiting patients for Cancer-associated retinopathy

New recruiting trial: Temporal Characterization of Extracellular Vesicles During Cellular Therapy Using CAR-T Cells and During the Occurrence of Immune Effector Cell-Associated Neurotoxicity Syndrome

A new clinical trial is recruiting patients for Cancer-associated retinopathy

New recruiting trial: The Effect of Chimeric Antigen Receptor (CAR)-T Cell Therapy on the Reconstitution of HIV-specific Immune Function

A new clinical trial is recruiting patients for Cancer-associated retinopathy

New recruiting trial: ALaCART-B: Acute Leukemia and Chimeric Antigen Receptor-T Cell Therapy for B-lymphoblastic Leukemia.

A new clinical trial is recruiting patients for Cancer-associated retinopathy

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.Which specific anti-retinal antibodies were found in my blood, and what do they mean for my prognosis?,Has a thorough search been done to find the cancer that may be causing my eye symptoms?,What treatment options are available to slow my vision loss, and what are the risks of each?,How quickly could my vision change, and what signs should prompt me to seek emergency care?,Are there any clinical trials for CAR that I might be eligible for?,What low vision rehabilitation services are available to help me adapt to my vision changes?,How will treating my cancer affect my eye condition?

Common questions about Cancer-associated retinopathy

What is Cancer-associated retinopathy?

Cancer-associated retinopathy (CAR) is a rare condition where the immune system accidentally attacks the light-sensing cells in the back of the eye (the retina) in people who have cancer elsewhere in the body. It is also sometimes called paraneoplastic retinopathy or paraneoplastic visual syndrome. The body produces antibodies to fight the cancer, but these same antibodies mistakenly target proteins in the retina, causing damage to the cells that allow you to see. The most common cancers linked to CAR are small cell lung cancer, breast cancer, gynecological cancers (such as ovarian and cervic

How is Cancer-associated retinopathy inherited?

Cancer-associated retinopathy follows a sporadic inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Cancer-associated retinopathy typically begin?

Typical onset of Cancer-associated retinopathy is adult. Age of onset can vary across affected individuals.

Are there clinical trials for Cancer-associated retinopathy?

Yes — 2 recruiting clinical trials are currently listed for Cancer-associated retinopathy on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.

Which specialists treat Cancer-associated retinopathy?

25 specialists and care centers treating Cancer-associated retinopathy are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.