RecruitingPhase 1NCT07354724
A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease
Studying Glycogen storage disease due to acid maltase deficiency
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Denali Therapeutics Inc.
- Principal Investigator
- Medical MonitorDenali Therapeutics Inc.
- Intervention
- DNL952(drug)
- Enrollment
- 32 enrolled
- Eligibility
- 18-75 years · All sexes
- Timeline
- 2026 – 2028
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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