RecruitingNCT06121011
A Global Prospective Observational Registry of Patients With Pompe Disease
Studying Glycogen storage disease due to acid maltase deficiency
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Amicus Therapeutics
- Intervention
- Cipaglucosidase alfa(biological)
- Enrollment
- 500 enrolled
- Eligibility
- All sexes
- Timeline
- 2024 – 2034
Study locations (30)
- University of Arkansas Medical Science, Little Rock, Arkansas, United States
- University of California Irvine, Irvine, California, United States
- Wolfson Children's Hospital, Jacksonville, Florida, United States
- Emory University, Atlanta, Georgia, United States
- Indiana University, IU Health Physicians Neurology, Indianapolis, Indiana, United States
- Washington University School of Medicine, St Louis, Missouri, United States
- NYU Neurogenetics, NYU Langone Medical Center, New York, New York, United States
- Duke University Medical Center, Durham, North Carolina, United States
- University of Cincinnati Medical Center, Cincinnati, Ohio, United States
- Cincinnati Children's Hospital, Cincinnati, Ohio, United States
- University of Pennsylvania Perelman Center for Advanced Medicine, Philadelphia, Pennsylvania, United States
- University of Pittsburgh, Pittsburgh, Pennsylvania, United States
- UPMC Children's Hospital of Pittsburgh, Pittsburgh, Pennsylvania, United States
- University of Utah, Salt Lake City, Utah, United States
- Lysosomal and Rare Disorders Research and Treatment Center, Inc., Fairfax, Virginia, United States
- +15 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT06121011 on ClinicalTrials.govOther trials for Glycogen storage disease due to acid maltase deficiency
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