Rare Glycogen Storage Diseases Natural History Study

Key facts

Sponsor

Duke University

Principal Investigator

Priya Kishnani, M.D.

Duke

Intervention

No intervention(other)

Enrollment

200 enrolled

Eligibility

0-90 years · All sexes

Timeline

2024 – 2034

Study locations (1)

• Duke University, Durham, North Carolina, United States

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

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