RecruitingPhase 2NCT07123155
Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
Studying Glycogen storage disease due to acid maltase deficiency
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Shionogi
- Intervention
- S-606001(drug)
- Enrollment
- 45 enrolled
- Eligibility
- 18 years · All sexes
- Timeline
- 2025 – 2027
Study locations (28)
- University of California - Irvine Medical Center, Irvine, California, United States
- University of Florida (UF) - Gainesville, Gainesville, Florida, United States
- Emory University Hospital, Atlanta, Georgia, United States
- Washington University in St. Louis, St Louis, Missouri, United States
- Duke University Medical Center, Durham, North Carolina, United States
- Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States
- University of Pennsylvania, Philadelphia, Pennsylvania, United States
- University of Pittsburgh School of Medicine, Pittsburgh, Pennsylvania, United States
- Lysosomal and Rare Disorders Research and Treatment Center (LDRTC), Fairfax, Virginia, United States
- UZ Leuven, Leuven, Belgium
- Aarhus University Hospital, Aarhus, Denmark
- HCL Hopital Pierre Wertheimer, Bron, France
- AP-HP Hopital Raymond Poincare, Garches, France
- Centre de Reference des Maladies Neuromusculaires et de la SLA - AP-HM Hopital de La Timone, Marseille, France
- CHU de Nice - Hopital Pasteur 2 - Centre de reference des Maladies Neuromusculaires, Nice, France
- +13 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT07123155 on ClinicalTrials.govOther trials for Glycogen storage disease due to acid maltase deficiency
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