Not yet recruitingPhase 4NCT06575829
Treatment Frequency Reduction in Pompe Disease
Studying Glycogen storage disease due to acid maltase deficiency
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Erasmus Medical Center
- Principal Investigator
- Pieter A. van Doorn, Prof. dr.Erasmus Medical Center
- Intervention
- Algucosidase alfa 20 mg/kg once every 4 weeks instead of once every 2 weeks(drug)
- Enrollment
- 10 enrolled
- Eligibility
- 50 years · All sexes
- Timeline
- 2024 – 2027
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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