Enrolling by invitationPHASE2, PHASE3NCT06075537
An Extension Study of the Long-Term Safety, Tolerability, and Efficacy of Tividenofusp Alfa (DNL310) in Participants With Mucopolysaccharidosis Type II (MPS II) From Study DNLI-E-0002 or Study DNLI-E-0007
Studying Mucopolysaccharidosis
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Denali Therapeutics Inc.
- Principal Investigator
- Medical MonitorDenali Therapeutics
- Intervention
- tividenofusp alfa(drug)
- Enrollment
- 99 enrolled
- Eligibility
- 18 years · All sexes
- Timeline
- 2023 – 2027
Study locations (25)
- UCSF Benioff Children's Hospital Oakland, Oakland, California, United States
- UNC Children's Research Institute, Chapel Hill, North Carolina, United States
- Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States
- Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
- The University of Texas Medical School at Houston, Houston, Texas, United States
- Huntsman Cancer Hospital, Salt Lake City, Utah, United States
- Sanatorio Mater Dei, Buenos Aires, Argentina
- Universitair Ziekenhuis Antwerpen, Edegem, Antwerpen, Belgium
- UZ Brussel, Jette, Belgium
- University of Alberta - Faculty of Medicine & Dentistry, Edmonton, Alberta, Canada
- Hospital for Sick Children, Toronto, Ontario, Canada
- McGill University Health Center, Montreal, Quebec, Canada
- Vseobecna Fakultni Nemocnice V Praze, Prague, Czechia
- Hopital Jeanne De Flandre - Metabolic Diseases Unit, Lille, France
- Universitätsklinikum Hamburg-Eppendorf, Hamburg, Germany
- +10 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT06075537 on ClinicalTrials.govOther trials for Mucopolysaccharidosis
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