RecruitingPHASE2, PHASE3NCT05371613
A Study to Determine the Efficacy and Safety of Tividenofusp Alfa (DNL310) vs Idursulfase in Pediatric and Young Adult Participants With Neuronopathic (nMPS II) or Non-Neuronopathic Mucopolysaccharidosis Type II (nnMPS II)
Studying Mucopolysaccharidosis
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Denali Therapeutics Inc.
- Principal Investigator
- Jose Alcantara Rodriguez, PharmDDenali Therapeutics Inc.
- Intervention
- tividenofusp alfa(drug)
- Enrollment
- 63 enrolled
- Eligibility
- 2-25 years · All sexes
- Timeline
- 2022 – 2027
Study locations (30)
- UCSF Benioff Children's Hospital Oakland, Oakland, California, United States
- Ann and Robert H Lurie Children's Hospital of Chicago, Chicago, Illinois, United States
- Hackensack University Medical Center, Hackensack, New Jersey, United States
- UNC Children's Research Institute, Chapel Hill, North Carolina, United States
- Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States
- Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
- The University of Texas Medical School at Houston, Houston, Texas, United States
- University of Utah, PPDS, Salt Lake City, Utah, United States
- Sanatorio Mater Dei, Buenos Aires, Argentina
- Women's and Children's Hospital, North Adelaide, Australia
- UZ Antwerpen, Antwerp, Antwerpen, Belgium
- Universitair Ziekenhuis Brussel, Jette, Brussels Capital, Belgium
- Hospital de Clínicas de Porto Alegre (HCPA) - PPDS, Porto Alegre, Brazil
- Instituto Fernandes Figueira, Rio de Janeiro, Brazil
- University of Alberta - Faculty of Medicine & Dentistry, Edmonton, Alberta, Canada
- +15 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT05371613 on ClinicalTrials.govOther trials for Mucopolysaccharidosis
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