RecruitingPHASE2, PHASE3NCT05208281
A Multi-cohort Study of Safety, Efficacy, PK and PD of GNR-055 in Patients With Mucopolysaccharidosis Type II
Studying Mucopolysaccharidosis
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- AO GENERIUM
- Principal Investigator
- Oksana A. Markova, MD, MScAO GENERIUM
- Intervention
- GNR-055 1.0-2.0-3.0 mg/kg(drug)
- Enrollment
- 32 enrolled
- Eligibility
- MALE
- Timeline
- 2021 – 2028
Study locations (5)
- Federal State-Funded Healthcare Institution Central Clinical Hospital of the Russian Academy of Sciences (Research Institute of Pediatrics and Child Health Protection of the Central Clinical Hospital of the Russian Academy of Sciences), Moscow, Russia
- Federal State Budgetary Educational Institution of Higher Education "St. Petersburg State Pediatric Medical University" of the Ministry of Health of the Russian Federation, Saint Petersburg, Russia
- V.I. Vernadsky Crimean Federal University, Simferopol, Russia
- State Budgetary Healthcare Institution Republican Medical Genetic Center, Ufa, Russia
- State Autonomous Healthcare Institution of the Sverdlovsk Region Regional Children's Clinical Hospital, Yekaterinburg, Russia
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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