Enrolling by invitationPhase 3NCT05594992
An Extension Study of JR-141 to Evaluate the Long-term Safety and Efficacy in MPS II (Hunter Syndrome) Subjects
Studying Mucopolysaccharidosis
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- JCR Pharmaceuticals Co., Ltd.
- Intervention
- JR-141(drug)
- Enrollment
- 80 enrolled
- Eligibility
- All sexes
- Timeline
- 2023 – 2028
Study locations (10)
- UCSF Benioff Children's Hospital Oakland, Oakland, California, United States
- Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
- Hospital Universitario Austral, Buenos Aires, Argentina
- Hospital de Clínicas de Porto Alegre, Porto Alegre, Brazil
- Instituto de Genética e Erros Inatos do Metabolismo, São Paulo, Brazil
- Hôpital Femme Mère Enfant, Bron, France
- Universitätsklinikum Hamburg-Eppendorf, Hamburg, Germany
- Osp. Pediatrico Bambino Gesù, IRCCS, Rome, Italy
- Uniwersytecki Szpital Dziecięcy, Krakow, Poland
- Hospital Sant Joan de Déu, Barcelona, Spain
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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