Active, not recruitingPHASE1, PHASE2NCT05793307
Evaluation of the Safety and Efficacy of Infantile-onset Pompe Disease Gene Therapy Drug
Studying Glycogen storage disease due to acid maltase deficiency
Last synced from ClinicalTrials.gov
ℹ
Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- GeneCradle Inc
- Intervention
- GC301(genetic)
- Enrollment
- 16 enrolled
- Eligibility
- All sexes
- Timeline
- 2023 – 2026
Study locations (5)
- Peking Union Medical College, Beijing, China
- 301 Chinese PLA General Hospital, Beijing, China
- Central South University, Xiangya Hospital, Changsha, China
- Zhejiang University, School of Medicine, The Children's Hospital, Hangzhou, China
- The First Affiliated Hospital of Zhengzhou University, Zhengzhou, China
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT05793307 on ClinicalTrials.govOther trials for Glycogen storage disease due to acid maltase deficiency
Additional recruiting or active studies for the same condition.
- RECRUITINGNANCT07478172Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular DiseaseUniversity of Missouri-Columbia
- RECRUITINGPHASE1, PHASE2NCT07282847A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late Onset Pompe Disease (PROGRESS-GT LOPD)AskBio Inc
- RECRUITINGPHASE2NCT07123155Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)Shionogi
- RECRUITINGPHASE4NCT06666413China Post-approval Commitment (PAC) Study of Avalglucosidase Alfa in Participants With IOPDGenzyme, a Sanofi Company
- RECRUITINGNCT06795152Rare Glycogen Storage Diseases Natural History StudyDuke University
- RECRUITINGPHASE1, PHASE2NCT06391736Evaluation of the Safety and Efficacy of Late-onset Pompe Disease Gene Therapy DrugGeneCradle Inc
- RECRUITINGNCT06121011A Global Prospective Observational Registry of Patients With Pompe DiseaseAmicus Therapeutics
- ACTIVE NOT RECRUITINGEARLY PHASE1NCT06109948Study to Assess the Safety, Tolerability, PK and PD of ABX1100Aro Biotherapeutics
See all trials for Glycogen storage disease due to acid maltase deficiency →