CompletedPHASE1, PHASE2NCT05174039
An Open-label Safety, Pharmacokinetic, and Efficacy Study of Miglustat for the Treatment of Subjects With Batten Ceroid Lipofuscinosis, Neuronal 3 (CLN3) Disease
Studying Batten Disease
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Beyond Batten Disease Foundation
- Principal Investigator
- Gary D. Clark, MD, MDTexas Children Hospital
- Intervention
- Miglustat 100 milligrams (mg) Oral Capsule(drug)
- Enrollment
- 6 enrolled
- Eligibility
- 17 years · All sexes
- Timeline
- 2022 – 2024
Study locations (1)
- Texas Children Hospital, Houston, Texas, United States
Collaborators
Theranexus
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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