Clinical trials for Batten Disease
6 recruiting or active trials synced from ClinicalTrials.gov.
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing data- ACTIVE NOT RECRUITINGPHASE1, PHASE2NCT05228145Gene Therapy Study for Children With CLN5 Batten DiseaseNeurogene Inc. · PI: Effie Albanis, MD
- ACTIVE NOT RECRUITINGNCT04273243Long-Term Follow Up of CLN6 Batten Disease Subjects Following Gene TransferEmily de los Reyes · PI: Emily de los Reyes, MD
- ENROLLING BY INVITATIONNCT03862274Examining Developmental Outcomes of Children Diagnosed With CLN2 DiseaseJessica Scherr · PI: Jessica Scherr, PhD
- ACTIVE NOT RECRUITINGPHASE1, PHASE2NCT03770572Gene Therapy for Children With CLN3 Batten DiseaseAlcyone Therapeutics, Inc · PI: Kathrin C Meyer, PhD
- ACTIVE NOT RECRUITINGNCT03285425Natural History of Neuronal Ceroid Lipofuscinosis, Batten's CLN6 DiseaeEmily de los Reyes · PI: Emily de los Reyes, MD
- RECRUITINGNCT01873924Clinical and Neuropsychological Investigations in Batten DiseaseUniversity of Rochester · PI: Jonathan W Mink, MD PhD