Active, not recruitingPHASE1, PHASE2NCT05095727
A Study of mRNA-3745 in Adult and Pediatric Participants With Glycogen Storage Disease Type 1a (GSD1a)
Studying Glycogen storage disease due to acid maltase deficiency
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- ModernaTX, Inc.
- Intervention
- mRNA-3745(drug)
- Enrollment
- 15 enrolled
- Eligibility
- 6 years · All sexes
- Timeline
- 2022 – 2026
Study locations (16)
- University of Connecticut Health Center, Farmington, Connecticut, United States
- Boston Children's Hospital, Boston, Massachusetts, United States
- Duke University Medical Center, Durham, North Carolina, United States
- Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States
- Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
- The University of Texas Health Science Center at Houston, Houston, Texas, United States
- Baylor College of Medicine, Houston, Texas, United States
- University of Utah, Salt Lake City, Utah, United States
- Stollery Children's Hospital University of Alberta, Edmonton, Alberta, Canada
- The Hospital for Sick Children, Toronto, Ontario, Canada
- AP-HP - Hôpital Antoine Béclère, Clamart, France
- CHRU Tours - Hopital Clocheville, Tours, France
- Universitair Medisch Centrum Groningen, Groningen, Netherlands
- Instytut Pomnik Centrum Zdrowia Dziecka, Warsaw, Poland
- Hospital Universitario 12 de Octubre, Madrid, Spain
- +1 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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